Glycoengineered Acid α-Glucosidase With Improved Efficacy at Correcting the Metabolic Aberrations and Motor Function Deficits in a Mouse Model of Pompe Disease
Titel:
Glycoengineered Acid α-Glucosidase With Improved Efficacy at Correcting the Metabolic Aberrations and Motor Function Deficits in a Mouse Model of Pompe Disease
Auteur:
Zhu, Yunxiang Jiang, Ji-Lei Gumlaw, Nathan K Zhang, Jinhua Bercury, Scott D Ziegler, Robin J Lee, Karen Kudo, Mariko Canfield, William M Edmunds, Timothy Jiang, Canwen Mattaliano, Robert J Cheng, Seng H