Evidence for Long-term Efficacy and Safety of Gene Therapy for Wiskott–Aldrich Syndrome in Preclinical Models
Titel:
Evidence for Long-term Efficacy and Safety of Gene Therapy for Wiskott–Aldrich Syndrome in Preclinical Models
Auteur:
Marangoni, Francesco Bosticardo, Marita Charrier, Sabine Draghici, Elena Locci, Michela Scaramuzza, Samantha Panaroni, Cristina Ponzoni, Maurilio Sanvito, Francesca Doglioni, Claudio Liabeuf, Marie Gjata, Bernard Montus, Marie Siminovitch, Katherine Aiuti, Alessandro Naldini, Luigi Dupré, Loïc Roncarolo, Maria Grazia Galy, Anne Villa, Anna