Long-term impact of early initiation of enzyme replacement therapy in 34 MPS VI patients: A resurvey study
Titel:
Long-term impact of early initiation of enzyme replacement therapy in 34 MPS VI patients: A resurvey study
Auteur:
Horovitz, Dafne D.G. Leão, Emília K.E.A. Ribeiro, Erlane M. Martins, Ana M. Barth, Anneliese L. Neri, João I.C.F. Kerstenetzky, Marcelo Siqueira, Ana C.M. Ribeiro, Bethania F.R. Kim, Chong A. Santos, Francisca C. Franco, José F.S. Lichtvan, Leniza C.L. Giuliani, Liane R. Rodrigues, Maria Do C.S. Bonatti, Renata C.F. Teixeira, Thaís B. Gonçalves, Alexandra Lourenço, Charles M. Pereira, Ane S.S. Acosta, Angelina X.