Long-term impact of early initiation of enzyme replacement therapy in 34 MPS VI patients: A resurvey study
Title:
Long-term impact of early initiation of enzyme replacement therapy in 34 MPS VI patients: A resurvey study
Author:
Horovitz, Dafne D.G. Leão, Emília K.E.A. Ribeiro, Erlane M. Martins, Ana M. Barth, Anneliese L. Neri, João I.C.F. Kerstenetzky, Marcelo Siqueira, Ana C.M. Ribeiro, Bethania F.R. Kim, Chong A. Santos, Francisca C. Franco, José F.S. Lichtvan, Leniza C.L. Giuliani, Liane R. Rodrigues, Maria Do C.S. Bonatti, Renata C.F. Teixeira, Thaís B. Gonçalves, Alexandra Lourenço, Charles M. Pereira, Ane S.S. Acosta, Angelina X.