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Onasemnogene abeparvovec gene therapy for symptomatic infantile-onset spinal muscular atrophy type 1 (STR1VE-EU): an open-label, single-arm, multicentre, phase 3 trial |
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| Titel: |
Onasemnogene abeparvovec gene therapy for symptomatic infantile-onset spinal muscular atrophy type 1 (STR1VE-EU): an open-label, single-arm, multicentre, phase 3 trial |
| Auteur: |
Mercuri, Eugenio Muntoni, Francesco Baranello, Giovanni Masson, Riccardo Boespflug-Tanguy, Odile Bruno, Claudio Corti, Stefania Daron, Aurore Deconinck, Nicolas Servais, Laurent Straub, Volker Ouyang, Haojun Chand, Deepa Tauscher-Wisniewski, Sitra Mendonca, Nuno Lavrov, Arseniy |
| Verschenen in: |
The lancet neurology |
| Paginering: |
Jaargang 20 () nr. 10 pagina's 832-841 |
| Jaar: |
2021 |
| Inhoud: |
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| Uitgever: |
Elsevier Ltd |
| Bronbestand: |
Elektronische Wetenschappelijke Tijdschriften |
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