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Onasemnogene abeparvovec gene therapy for symptomatic infantile-onset spinal muscular atrophy type 1 (STR1VE-EU): an open-label, single-arm, multicentre, phase 3 trial |
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Title: |
Onasemnogene abeparvovec gene therapy for symptomatic infantile-onset spinal muscular atrophy type 1 (STR1VE-EU): an open-label, single-arm, multicentre, phase 3 trial |
Author: |
Mercuri, Eugenio Muntoni, Francesco Baranello, Giovanni Masson, Riccardo Boespflug-Tanguy, Odile Bruno, Claudio Corti, Stefania Daron, Aurore Deconinck, Nicolas Servais, Laurent Straub, Volker Ouyang, Haojun Chand, Deepa Tauscher-Wisniewski, Sitra Mendonca, Nuno Lavrov, Arseniy |
Appeared in: |
The lancet neurology |
Paging: |
Volume 20 () nr. 10 pages 832-841 |
Year: |
2021 |
Contents: |
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Publisher: |
Elsevier Ltd |
Source file: |
Elektronische Wetenschappelijke Tijdschriften |
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