| nr |
titel |
auteur |
tijdschrift |
jaar |
jaarg. |
afl. |
pagina('s) |
type |
| 1 |
A Randomized, Double-Blind, Placebo-Controlled, Global Phase 3 Study of Edasalonexent in Pediatric Patients with Duchenne Muscular Dystrophy: Results of the PolarisDMD Trial
|
Finkel, Richard S.
|
|
|
8 |
5 |
p. 769-784
|
artikel
|
| 2 |
Association of HLA Class II Alleles with Disease Severity and Treatment Response in Iranian Patients with Myasthenia Gravis
|
Sinaei, Farnaz
|
|
|
8 |
5 |
p. 827-829
|
artikel
|
| 3 |
Author’s Response to: Rebuttal to: Simvastatin Treatment Does Not Ameliorate Muscle Pathophysiology in a Mouse Model for Duchenne Muscular Dystrophy, Verhaart et al. 2020
|
Aartsma-Rus, Annemieke
|
|
|
8 |
5 |
p. 867-868
|
artikel
|
| 4 |
Electrostatic Coating of Viral Particles for Gene Delivery Applications in Muscular Dystrophies: Influence of Size on Stability and Antibody Protection
|
Guerra-Rebollo, Marta
|
|
|
8 |
5 |
p. 815-825
|
artikel
|
| 5 |
Minimal Consequences of CMAH and DBA/2 Backgrounds on a FKRP Deficient Model
|
Vaubourg, Camille
|
|
|
8 |
5 |
p. 785-793
|
artikel
|
| 6 |
Plasma Creatinine Level Does Not Predict Respiratory Function in Amyotrophic Lateral Sclerosis
|
Morgadinho, João
|
|
|
8 |
5 |
p. 795-799
|
artikel
|
| 7 |
Profiling Serum Antibodies Against Muscle Antigens in Facioscapulohumeral Muscular Dystrophy Finds No Disease-Specific Autoantibodies
|
Greco, Anna
|
|
|
8 |
5 |
p. 801-814
|
artikel
|
| 8 |
Rebuttal to: Simvastatin Treatment Does Not Ameliorate Muscle Pathophysiology in a Mouse Model for Duchenne Muscular Dystrophy, Verhaart et al. 2020
|
Whitehead, N.P.
|
|
|
8 |
5 |
p. 865-866
|
artikel
|
| 9 |
Sharing “Negative” Results in Neuromuscular Research: A Positive Experience
|
Arechavala-Gomeza, Virginia
|
|
|
8 |
5 |
p. 765-767
|
artikel
|
| 10 |
Simvastatin Treatment Does Not Ameliorate Muscle Pathophysiology in a Mouse Model for Duchenne Muscular Dystrophy
|
Verhaart, Ingrid E.C.
|
|
|
8 |
5 |
p. 845-863
|
artikel
|
| 11 |
The Safety Factor for Neuromuscular Transmission: Effects of Dimethylsulphoxide, Cannabinoids and Synaptic Homeostasis
|
Odierna, Gianmaria Lorenzo
|
|
|
8 |
5 |
p. 831-844
|
artikel
|
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