| nr |
titel |
auteur |
tijdschrift |
jaar |
jaarg. |
afl. |
pagina('s) |
type |
| 1 |
An Immune-Competent Murine Model to Study Elimination of AAV-Transduced Hepatocytes by Capsid-Specific CD8+ T Cells
|
Palaschak, Brett
|
|
2017
|
5 |
C |
p. 142-152
11 p.
|
artikel
|
| 2 |
A One-Step PCR-Based Assay to Evaluate the Efficiency and Precision of Genomic DNA-Editing Tools
|
Germini, Diego
|
|
2017
|
5 |
C |
p. 43-50
8 p.
|
artikel
|
| 3 |
Cell Therapy in Myology: Dynamics of Muscle Precursor Cell Death after Intramuscular Administration in Non-human Primates
|
Skuk, Daniel
|
|
2017
|
5 |
C |
p. 232-240
9 p.
|
artikel
|
| 4 |
Dendritic Cell Therapies for Hematologic Malignancies
|
Weinstock, Matthew
|
|
2017
|
5 |
C |
p. 66-75
10 p.
|
artikel
|
| 5 |
Development of a Novel AAV Gene Therapy Cassette with Improved Safety Features and Efficacy in a Mouse Model of Rett Syndrome
|
Gadalla, Kamal K.E.
|
|
2017
|
5 |
C |
p. 180-190
11 p.
|
artikel
|
| 6 |
Effect of a Fusion Peptide by Covalent Conjugation of a Mitochondrial Cell-Penetrating Peptide and a Glutathione Analog Peptide
|
Cerrato, Carmine Pasquale
|
|
2017
|
5 |
C |
p. 221-231
11 p.
|
artikel
|
| 7 |
Efficacy of Gene Therapy Is Dependent on Disease Progression in Dystrophic Mice with Mutations in the FKRP Gene
|
Vannoy, Charles Harvey
|
|
2017
|
5 |
C |
p. 31-42
12 p.
|
artikel
|
| 8 |
Efficient Production of Papillomavirus Gene Delivery Vectors in Defined In Vitro Reactions
|
Cerqueira, Carla
|
|
2017
|
5 |
C |
p. 165-179
15 p.
|
artikel
|
| 9 |
Engineering of GlcNAc-1-Phosphotransferase for Production of Highly Phosphorylated Lysosomal Enzymes for Enzyme Replacement Therapy
|
Liu, Lin
|
|
2017
|
5 |
C |
p. 59-65
7 p.
|
artikel
|
| 10 |
Genetic Engineering and Manufacturing of Hematopoietic Stem Cells
|
Wang, Xiuyan
|
|
2017
|
5 |
C |
p. 96-105
10 p.
|
artikel
|
| 11 |
Immune Modulatory Cell Therapy for Hemophilia B Based on CD20-Targeted Lentiviral Gene Transfer to Primary B Cells
|
Wang, Xiaomei
|
|
2017
|
5 |
C |
p. 76-82
7 p.
|
artikel
|
| 12 |
Improved MECP2 Gene Therapy Extends the Survival of MeCP2-Null Mice without Apparent Toxicity after Intracisternal Delivery
|
Sinnett, Sarah E.
|
|
2017
|
5 |
C |
p. 106-115
10 p.
|
artikel
|
| 13 |
Integrase-Deficient Lentiviral Vector as an All-in-One Platform for Highly Efficient CRISPR/Cas9-Mediated Gene Editing
|
Ortinski, Pavel I.
|
|
2017
|
5 |
C |
p. 153-164
12 p.
|
artikel
|
| 14 |
Lentivector Iterations and Pre-Clinical Scale-Up/Toxicity Testing: Targeting Mobilized CD34+ Cells for Correction of Fabry Disease
|
Huang, Ju
|
|
2017
|
5 |
C |
p. 241-258
18 p.
|
artikel
|
| 15 |
Neuroglobin Can Prevent or Reverse Glaucomatous Progression in DBA/2J Mice
|
Cwerman-Thibault, Hélène
|
|
2017
|
5 |
C |
p. 200-220
21 p.
|
artikel
|
| 16 |
Preclinical Evaluation of a Lentiviral Vector for Huntingtin Silencing
|
Cambon, Karine
|
|
2017
|
5 |
C |
p. 259-276
18 p.
|
artikel
|
| 17 |
Spatially and Temporally Regulated NRF2 Gene Therapy Using Mcp-1 Promoter in Retinal Ganglion Cell Injury
|
Fujita, Kosuke
|
|
2017
|
5 |
C |
p. 130-141
12 p.
|
artikel
|
| 18 |
STRIP2 Is Indispensable for the Onset of Embryonic Stem Cell Differentiation
|
Sabour, Davood
|
|
2017
|
5 |
C |
p. 116-129
14 p.
|
artikel
|
| 19 |
Targeting Wnt/β-Catenin Activated Cells with Dominant-Negative N-cadherin to Reduce Neointima Formation
|
Hulin-Curtis, Sarah
|
|
2017
|
5 |
C |
p. 191-199
9 p.
|
artikel
|
| 20 |
The Clonal Fate of Live Cells
|
Wang, Wei
|
|
2017
|
5 |
C |
p. 93-95
3 p.
|
artikel
|
| 21 |
The 2.8 Å Electron Microscopy Structure of Adeno-Associated Virus-DJ Bound by a Heparinoid Pentasaccharide
|
Xie, Qing
|
|
2017
|
5 |
C |
p. 1-12
12 p.
|
artikel
|
| 22 |
Toward a Rapid Production of Multivirus-Specific T Cells Targeting BKV, Adenovirus, CMV, and EBV from Umbilical Cord Blood
|
Dave, Hema
|
|
2017
|
5 |
C |
p. 13-21
9 p.
|
artikel
|
| 23 |
Toward Personalized Gene Therapy: Characterizing the Host Genetic Control of Lentiviral-Vector-Mediated Hepatic Gene Delivery
|
Suwanmanee, Thipparat
|
|
2017
|
5 |
C |
p. 83-92
10 p.
|
artikel
|
| 24 |
Vectofusin-1 Promotes RD114-TR-Pseudotyped Lentiviral Vector Transduction of Human HSPCs and T Lymphocytes
|
Piovan, Claudia
|
|
2017
|
5 |
C |
p. 22-30
9 p.
|
artikel
|
| 25 |
Viral Vector-Based Innovative Approaches to Directly Abolishing Tumorigenic Pluripotent Stem Cells for Safer Regenerative Medicine
|
Mitsui, Kaoru
|
|
2017
|
5 |
C |
p. 51-58
8 p.
|
artikel
|
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