nr |
titel |
auteur |
tijdschrift |
jaar |
jaarg. |
afl. |
pagina('s) |
type |
1 |
AAV capsid CD8+ T-cell epitopes are highly conserved across AAV serotypes
|
Hui, Daniel J |
|
2015 |
2 |
C |
p. - 1 p. |
artikel |
2 |
AAV-mediated RLBP1 gene therapy improves the rate of dark adaptation in Rlbp1 knockout mice
|
Choi, Vivian W |
|
2015 |
2 |
C |
p. - 1 p. |
artikel |
3 |
AAV9 supports wide-scale transduction of the CNS and TDP-43 disease modeling in adult rats
|
Jackson, Kasey L |
|
2015 |
2 |
C |
p. - 1 p. |
artikel |
4 |
A comparison of AAV strategies distinguishes overlapping vectors for efficient systemic delivery of the 6.2 kb Dysferlin coding sequence
|
Pryadkina, Marina |
|
2015 |
2 |
C |
p. - 1 p. |
artikel |
5 |
A marker-free system for highly efficient construction of vaccinia virus vectors using CRISPR Cas9
|
Yuan, Ming |
|
2015 |
2 |
C |
p. - 1 p. |
artikel |
6 |
Amelioration of murine sickle cell disease by nonablative conditioning and γ-globin gene-corrected bone marrow cells
|
Pestina, Tamara I |
|
2015 |
2 |
C |
p. - 1 p. |
artikel |
7 |
An assessment of the effects of ectopic gp91phox expression in XCGD iPSC-derived neutrophils
|
Lin, Huan-Ting |
|
2015 |
2 |
C |
p. - 1 p. |
artikel |
8 |
A novel, long-lived, and highly engraftable immunodeficient mouse model of mucopolysaccharidosis type I
|
Mendez, Daniel C |
|
2015 |
2 |
C |
p. - 1 p. |
artikel |
9 |
A phase 1 study of a heterologous prime-boost vaccination involving a truncated HER2 sequence in patients with HER2-expressing breast cancer
|
Kim, Sung-Bae |
|
2015 |
2 |
C |
p. - 1 p. |
artikel |
10 |
Bilateral single-site intracerebral injection of a nonpathogenic herpes simplex virus-1 vector decreases anxiogenic behavior in MPS VII mice
|
Liu, Wenpei |
|
2015 |
2 |
C |
p. - 1 p. |
artikel |
11 |
Clinical testing of a dendritic cell targeted therapeutic vaccine in patients with chronic hepatitis C virus infection
|
Zabaleta, Aintzane |
|
2015 |
2 |
C |
p. - 1 p. |
artikel |
12 |
Coherence analysis discriminates between retroviral integration patterns in CD34+ cells transduced under differing clinical trial conditions
|
Hallwirth, Claus V |
|
2015 |
2 |
C |
p. - 1 p. |
artikel |
13 |
Comparative impact of AAV and enzyme replacement therapy on respiratory and cardiac function in adult Pompe mice
|
Falk, Darin J |
|
2015 |
2 |
C |
p. - 1 p. |
artikel |
14 |
Conditionally replicating adenovirus prevents pluripotent stem cell–derived teratoma by specifically eliminating undifferentiated cells
|
Mitsui, Kaoru |
|
2015 |
2 |
C |
p. - 1 p. |
artikel |
15 |
Corrigendum to “Assessment of toxicity and biodistribution of recombinant AAV8 vector–mediated immunomodulatory gene therapy in mice with Pompe disease”
|
Wang, Gensheng |
|
2015 |
2 |
C |
p. - 1 p. |
artikel |
16 |
Design of a regulated lentiviral vector for hematopoietic stem cell gene therapy of globoid cell leukodystrophy
|
Ungari, Silvia |
|
2015 |
2 |
C |
p. - 1 p. |
artikel |
17 |
Development of a replication-competent lentivirus assay for dendritic cell-targeting lentiviral vectors
|
Farley, Daniel C |
|
2015 |
2 |
C |
p. - 1 p. |
artikel |
18 |
Disease modeling and lentiviral gene transfer in patient-specific induced pluripotent stem cells from late-onset Pompe disease patient
|
Sato, Yohei |
|
2015 |
2 |
C |
p. - 1 p. |
artikel |
19 |
Effectiveness of gene delivery systems for pluripotent and differentiated cells
|
Rapti, Kleopatra |
|
2015 |
2 |
C |
p. - 1 p. |
artikel |
20 |
Efficacy of irreversible electroporation in human pancreatic adenocarcinoma: advanced murine model
|
Philips, Prejesh |
|
2015 |
2 |
C |
p. - 1 p. |
artikel |
21 |
Efficient gene delivery to photoreceptors using AAV2/rh10 and rescue of the Rho−/− mouse
|
Palfi, Arpad |
|
2015 |
2 |
C |
p. - 1 p. |
artikel |
22 |
Efficient genome editing in hematopoietic stem cells with helper-dependent Ad5/35 vectors expressing site-specific endonucleases under microRNA regulation
|
Saydaminova, Kamola |
|
2015 |
2 |
C |
p. - 1 p. |
artikel |
23 |
Efficient inhibition of tumor angiogenesis and growth by a synthetic peptide blocking S100A4-methionine aminopeptidase 2 interaction
|
Ochiya, Takahiro |
|
2015 |
2 |
C |
p. - 1 p. |
artikel |
24 |
Engineered dendritic cells from cord blood and adult blood accelerate effector T cell immune reconstitution against HCMV
|
Daenthanasanmak, Anusara |
|
2015 |
2 |
C |
p. - 1 p. |
artikel |
25 |
Generation of a lentiviral vector producer cell clone for human Wiskott-Aldrich syndrome gene therapy
|
Wielgosz, Matthew M |
|
2015 |
2 |
C |
p. - 1 p. |
artikel |
26 |
Generation of a stable packaging cell line producing high-titer PPT-deleted integration-deficient lentiviral vectors
|
Hu, Peirong |
|
2015 |
2 |
C |
p. - 1 p. |
artikel |
27 |
Generation of new peptide-Fc fusion proteins that mediate antibody-dependent cellular cytotoxicity against different types of cancer cells
|
Sioud, Mouldy |
|
2015 |
2 |
C |
p. - 1 p. |
artikel |
28 |
Gene therapy to treat inherited and complex retinal degenerative diseases
|
Rex, Tonia S |
|
2015 |
2 |
C |
p. - 1 p. |
artikel |
29 |
Hepatic insulin gene therapy prevents diabetic enteropathy in STZ-treated CD-1 mice
|
You, Shuo |
|
2015 |
2 |
C |
p. - 1 p. |
artikel |
30 |
High-accuracy biodistribution analysis of adeno-associated virus variants by double barcode sequencing
|
Marsic, Damien |
|
2015 |
2 |
C |
p. - 1 p. |
artikel |
31 |
High-level production of replication-defective human immunodeficiency type 1 virus vector particles using helper-dependent adenovirus vectors
|
Hu, Yani |
|
2015 |
2 |
C |
p. - 1 p. |
artikel |
32 |
Highly efficient in vitro and in vivo delivery of functional RNAs using new versatile MS2-chimeric retrovirus-like particles
|
Prel, Anne |
|
2015 |
2 |
C |
p. - 1 p. |
artikel |
33 |
High-throughput monitoring of integration site clonality in preclinical and clinical gene therapy studies
|
Giordano, Frank A |
|
2015 |
2 |
C |
p. - 1 p. |
artikel |
34 |
Identification of an adeno-associated virus binding epitope for AVB sepharose affinity resin
|
Wang, Qiang |
|
2015 |
2 |
C |
p. - 1 p. |
artikel |
35 |
Increasing the minicircle DNA purity using an enhanced triplex DNA technology to eliminate DNA contaminants
|
Hou, Xiaohu H |
|
2015 |
2 |
C |
p. - 1 p. |
artikel |
36 |
Inhalable delivery of AAV-based MRP4/ABCC4 silencing RNA prevents monocrotaline-induced pulmonary hypertension
|
Claude, Caroline |
|
2015 |
2 |
C |
p. - 1 p. |
artikel |
37 |
Large-scale production of lentiviral vector in a closed system hollow fiber bioreactor
|
Sheu, Jonathan |
|
2015 |
2 |
C |
p. - 1 p. |
artikel |
38 |
Lysophosphatidic acid induces YAP-promoted proliferation of human corneal endothelial cells via PI3K and ROCK pathways
|
Hsueh, Yi-Jen |
|
2015 |
2 |
C |
p. - 1 p. |
artikel |
39 |
MD11-mediated delivery of recombinant eIF3f induces melanoma and colorectal carcinoma cell death
|
Marchione, Roberta |
|
2015 |
2 |
C |
p. - 1 p. |
artikel |
40 |
Membrane-stabilizing copolymers confer marked protection to dystrophic skeletal muscle in vivo
|
Houang, Evelyne M |
|
2015 |
2 |
C |
p. - 1 p. |
artikel |
41 |
Mucosal delivery of a vectored RSV vaccine is safe and elicits protective immunity in rodents and nonhuman primates
|
Pierantoni, Angiolo |
|
2015 |
2 |
C |
p. - 1 p. |
artikel |
42 |
Multigenic lentiviral vectors for combined and tissue-specific expression of miRNA- and protein-based antiangiogenic factors
|
Askou, Anne Louise |
|
2015 |
2 |
C |
p. - 1 p. |
artikel |
43 |
Nuclear expression of mitochondrial ND4 leads to the protein assembling in complex I and prevents optic atrophy and visual loss
|
Cwerman-Thibault, Hélène |
|
2015 |
2 |
C |
p. - 1 p. |
artikel |
44 |
Ototoxicity-induced loss of hearing and inner hair cells is attenuated by HSP70 gene transfer
|
Takada, Yohei |
|
2015 |
2 |
C |
p. - 1 p. |
artikel |
45 |
Preclinical safety and efficacy studies with an affinity-enhanced epithelial junction opener and PEGylated liposomal doxorubicin
|
Richter, Maximilian |
|
2015 |
2 |
C |
p. - 1 p. |
artikel |
46 |
Quantitative high-throughput gene expression profiling of human striatal development to screen stem cell–derived medium spiny neurons
|
Straccia, Marco |
|
2015 |
2 |
C |
p. - 1 p. |
artikel |
47 |
Re-examination of regulatory opinions in Europe: possible contribution for the approval of the first gene therapy product Glybera
|
Watanabe, Natsumi |
|
2015 |
2 |
C |
p. - 1 p. |
artikel |
48 |
Reversal of diabetes following transplantation of an insulin-secreting human liver cell line: Melligen cells
|
Lawandi, Janet |
|
2015 |
2 |
C |
p. - 1 p. |
artikel |
49 |
Short-lived recombinant adeno-associated virus transgene expression in dystrophic muscle is associated with oxidative damage to transgene mRNA
|
Dupont, Jean-Baptiste |
|
2015 |
2 |
C |
p. - 1 p. |
artikel |
50 |
Silencing p75NTR prevents proNGF-induced endothelial cell death and development of acellular capillaries in rat retina
|
Shanab, Ahmed Y |
|
2015 |
2 |
C |
p. - 1 p. |
artikel |
51 |
Simple downstream process based on detergent treatment improves yield and in vivo transduction efficacy of adeno-associated virus vectors
|
Dias Florencio, Gabriella |
|
2015 |
2 |
C |
p. - 1 p. |
artikel |
52 |
Structure-based redesign of lysostaphin yields potent antistaphylococcal enzymes that evade immune cell surveillance
|
Blazanovic, Kristina |
|
2015 |
2 |
C |
p. - 1 p. |
artikel |
53 |
Super-resolution imaging of nuclear import of adeno-associated virus in live cells
|
Kelich, Joseph M |
|
2015 |
2 |
C |
p. - 1 p. |
artikel |
54 |
Testing gene therapy vectors in human primary nasal epithelial cultures
|
Cao, Huibi |
|
2015 |
2 |
C |
p. - 1 p. |
artikel |
55 |
The human ankyrin 1 promoter insulator sustains gene expression in a β-globin lentiviral vector in hematopoietic stem cells
|
Romero, Zulema |
|
2015 |
2 |
C |
p. - 1 p. |
artikel |
56 |
Towards the safer clinical translation of human induced pluripotent stem cell–derived cells to regenerative medicine
|
Tani, Kenzaburo |
|
2015 |
2 |
C |
p. - 1 p. |
artikel |
57 |
Transcytosis in the blood–cerebrospinal fluid barrier of the mouse brain with an engineered receptor/ligand system
|
Méndez-Gómez, Héctor R |
|
2015 |
2 |
C |
p. - 1 p. |
artikel |
58 |
Transgene-host cell interactions mediate significant influences on the production, stability, and function of recombinant canine FVIII
|
Crawford, Bredon |
|
2015 |
2 |
C |
p. - 1 p. |
artikel |
59 |
Using MRI to evaluate and predict therapeutic success from depot-based cancer vaccines
|
DeBay, Drew R |
|
2015 |
2 |
C |
p. - 1 p. |
artikel |
60 |
Vaccinia virus as a subhelper for AAV replication and packaging
|
Moore, Andrea R |
|
2015 |
2 |
C |
p. - 1 p. |
artikel |