| nr |
titel |
auteur |
tijdschrift |
jaar |
jaarg. |
afl. |
pagina('s) |
type |
| 1 |
AAV-based gene replacement: The promise of gene therapy for deafness
|
Qi, Jieyu
|
|
|
35 |
2 |
p.
|
artikel
|
| 2 |
Aberrant spliceosome activity via elevated intron retention and upregulation and phosphorylation of SF3B1 in chronic lymphocytic leukemia
|
Kashyap, Manoj Kumar
|
|
|
35 |
2 |
p.
|
artikel
|
| 3 |
ac4C-AFL: A high-precision identification of human mRNA N4-acetylcytidine sites based on adaptive feature representation learning
|
Pham, Nhat Truong
|
|
|
35 |
2 |
p.
|
artikel
|
| 4 |
Accessory oligos for neuronal delivery of therapeutic siRNAs for ALS
|
Rossi, John J.
|
|
|
35 |
2 |
p.
|
artikel
|
| 5 |
A cystic fibrosis gene editing approach that is on target
|
Porter, Joseph J.
|
|
|
35 |
2 |
p.
|
artikel
|
| 6 |
Adeno-associated virus-based gene therapy delivering combinations of two growth-associated genes to MPS IVA mice
|
Rintz, Estera
|
|
|
35 |
2 |
p.
|
artikel
|
| 7 |
A new immune-based prognostic scoring system for multiple myeloma
|
Hammad, Mohamed
|
|
|
35 |
2 |
p.
|
artikel
|
| 8 |
A novel function and mechanism of ischemia-induced retinal astrocyte-derived exosomes for RGC apoptosis of ischemic retinopathy
|
Ye, Xiaoyuan
|
|
|
35 |
2 |
p.
|
artikel
|
| 9 |
A Novel Pak1/ATF2/miR-132 Signaling Axis Is Involved in the Hematogenous Metastasis of Gastric Cancer Cells
|
Liu, Funan
|
|
|
35 |
2 |
p.
|
artikel
|
| 10 |
Anti-miR-141-3p maintains homeostasis between autophagy and apoptosis by targeting Yy1 in the fetal lumbosacral defecation center of rats
|
Li, Yue
|
|
|
35 |
2 |
p.
|
artikel
|
| 11 |
A potential therapeutic approach for cisplatin-induced hearing loss
|
Hu, Shao Wei
|
|
|
35 |
2 |
p.
|
artikel
|
| 12 |
ASOptimizer: Optimizing antisense oligonucleotides through deep learning for IDO1 gene regulation
|
Hwang, Gyeongjo
|
|
|
35 |
2 |
p.
|
artikel
|
| 13 |
Base editing in humanized dystrophic mice
|
Zhang, Chen
|
|
|
35 |
2 |
p.
|
artikel
|
| 14 |
Base editing rescues acid α-glucosidase function in infantile-onset Pompe disease patient-derived cells
|
Christensen, Chloe L.
|
|
|
35 |
2 |
p.
|
artikel
|
| 15 |
Blood pressure reduction through brain delivery of nanoparticles loaded with plasmid DNA encoding angiotensin receptor shRNA
|
Lamptey, Richard Nii Lante
|
|
|
35 |
2 |
p.
|
artikel
|
| 16 |
CD3 aptamers promote expansion and persistence of tumor-reactive T cells for adoptive T cell therapy in cancer
|
Menon, Ashwathi Puravankara
|
|
|
35 |
2 |
p.
|
artikel
|
| 17 |
Context base editing for splice correction of IVSI-110 β-thalassemia
|
Naiisseh, Basma
|
|
|
35 |
2 |
p.
|
artikel
|
| 18 |
Control of endothelial cell function and arteriogenesis by MEG3:EZH2 epigenetic regulation of integrin expression
|
Dunn-Davies, Hywel
|
|
|
35 |
2 |
p.
|
artikel
|
| 19 |
Correction of human nonsense mutation via adenine base editing for Duchenne muscular dystrophy treatment in mouse
|
Jin, Ming
|
|
|
35 |
2 |
p.
|
artikel
|
| 20 |
CRISPR-based editing strategies to rectify EYA1 complex genomic rearrangement linked to haploinsufficiency
|
Yi, Hwalin
|
|
|
35 |
2 |
p.
|
artikel
|
| 21 |
Deep learning facilitates efficient optimization of antisense oligonucleotide drugs
|
Lin, Shenggeng
|
|
|
35 |
2 |
p.
|
artikel
|
| 22 |
Effective intravitreal gene delivery to retinal pigment epithelium with hyaluronic acid nanospheres
|
Crane, Ryan
|
|
|
35 |
2 |
p.
|
artikel
|
| 23 |
Engineering miniature CRISPR-Cas Un1Cas12f1 for efficient base editing
|
Hu, Yueer
|
|
|
35 |
2 |
p.
|
artikel
|
| 24 |
Enhanced transgene expression from single-stranded AAV vectors in human cells in vitro and in murine hepatocytes in vivo
|
Lu, Yuan
|
|
|
35 |
2 |
p.
|
artikel
|
| 25 |
Enigmatic exosomal connection in lung cancer drug resistance
|
Patra, Sambit K.
|
|
|
35 |
2 |
p.
|
artikel
|
| 26 |
Expanding RNA editing toolkit using an IDR-based strategy
|
Di, Minghui
|
|
|
35 |
2 |
p.
|
artikel
|
| 27 |
Favorable efficacy and reduced acute neurotoxicity by antisense oligonucleotides with 2′,4′-BNA/LNA with 9-(aminoethoxy)phenoxazine
|
Matsubayashi, Taiki
|
|
|
35 |
2 |
p.
|
artikel
|
| 28 |
Favorable efficacy and reduced acute neurotoxicity by antisense oligonucleotides with 2′,4′ -BNA/LNA with 9-(aminoethoxy)phenoxazine
|
Matsubayashi, Taiki
|
|
|
35 |
2 |
p.
|
artikel
|
| 29 |
Fusion of multi-source relationships and topology to infer lncRNA-protein interactions
|
Zhang, Xinyu
|
|
|
35 |
2 |
p.
|
artikel
|
| 30 |
Identification of film-based formulations that move mRNA lipid nanoparticles out of the freezer
|
Doan, Trang Nguyen Kieu
|
|
|
35 |
2 |
p.
|
artikel
|
| 31 |
Inefficacy of anti-VEGF therapy reflected in VEGF-mediated photoreceptor degeneration
|
Xu, Xin
|
|
|
35 |
2 |
p.
|
artikel
|
| 32 |
Inhibition of miR-25 ameliorates cardiac and skeletal muscle dysfunction in aged mdx/utrn haploinsufficient (+/−) mice
|
Kepreotis, Sacha V.
|
|
|
35 |
2 |
p.
|
artikel
|
| 33 |
LNA-i-miR-221 activity in colorectal cancer: A reverse translational investigation
|
Ali, Asad
|
|
|
35 |
2 |
p.
|
artikel
|
| 34 |
Metabolism pathway-based subtyping in endometrial cancer: An integrated study by multi-omics analysis and machine learning algorithms
|
Liu, Xiaodie
|
|
|
35 |
2 |
p.
|
artikel
|
| 35 |
miR-200-mediated inactivation of cancer-associated fibroblasts via targeting of NRP2-VEGFR signaling attenuates lung cancer invasion and metastasis
|
Cheon, Inyoung
|
|
|
35 |
2 |
p.
|
artikel
|
| 36 |
Modifying miRs for effective reprogramming of fibroblasts to cardiomyocytes
|
Wang, Xinghua
|
|
|
35 |
2 |
p.
|
artikel
|
| 37 |
MRNACalc: An accurate RNA quantification tool in the era of modified nucleosides
|
den Roover, Sabine
|
|
|
35 |
2 |
p.
|
artikel
|
| 38 |
N4-acetylcytidine acetylation of neurexin 2 in the spinal dorsal horn regulates hypersensitivity in a rat model of cancer-induced bone pain
|
Xu, Longsheng
|
|
|
35 |
2 |
p.
|
artikel
|
| 39 |
Oligonucleotide therapies for nonalcoholic steatohepatitis
|
Li, Sixu
|
|
|
35 |
2 |
p.
|
artikel
|
| 40 |
Optimized allele-specific silencing of the dominant-negative COL6A1 G293R substitution causing collagen VI-related dystrophy
|
Brull, Astrid
|
|
|
35 |
2 |
p.
|
artikel
|
| 41 |
Phosphatidylcholine head group chemistry alters the extrahepatic accumulation of lipid-conjugated siRNA
|
Hariharan, Vignesh N.
|
|
|
35 |
2 |
p.
|
artikel
|
| 42 |
Physiologically based modeling of LNP-mediated delivery of mRNA in the vascular system
|
Parhiz, Hamideh
|
|
|
35 |
2 |
p.
|
artikel
|
| 43 |
Precise correction of a spectrum of β-thalassemia mutations in coding and non-coding regions by base editors
|
Prasad, Kirti
|
|
|
35 |
2 |
p.
|
artikel
|
| 44 |
Precision genome editing offers hope for treatment of β-thalassemia and other genetic disorders
|
Abbas, Zeeshan
|
|
|
35 |
2 |
p.
|
artikel
|
| 45 |
Proof-of-concept study for liver-directed miQURE technology in a dyslipidemic mouse model
|
Zancanella, Vanessa
|
|
|
35 |
2 |
p.
|
artikel
|
| 46 |
Retraction Notice to: circFMN2 Sponges miR-1238 to Promote the Expression of LIM-Homeobox Gene 2 in Prostate Cancer Cells
|
Shan, Guangyi
|
|
|
35 |
2 |
p.
|
artikel
|
| 47 |
Retraction Notice to: circIFT80 Functions as a ceRNA of miR-1236-3p to Promote Colorectal Cancer Progression
|
Feng, Wenming
|
|
|
35 |
2 |
p.
|
artikel
|
| 48 |
Retraction Notice to: circRASGRF2 functions as an oncogenic gene in hepatocellular carcinoma by acting as a miR-1224 sponge
|
Wu, Di
|
|
|
35 |
2 |
p.
|
artikel
|
| 49 |
Retraction Notice to: Circular RNA Cdr1as Upregulates SCAI to Suppress Cisplatin Resistance in Ovarian Cancer via miR-1270 Suppression
|
Zhao, Zhao
|
|
|
35 |
2 |
p.
|
artikel
|
| 50 |
Retraction Notice to: lncRNA SPRY4-IT1 Regulates Cell Proliferation and Migration by Sponging miR-101-3p and Regulating AMPK Expression in Gastric Cancer
|
Cao, Shuguang
|
|
|
35 |
2 |
p.
|
artikel
|
| 51 |
Retraction Notice to: lncRNA UCA1 Promotes Gefitinib Resistance as a ceRNA to Target FOSL2 by Sponging miR-143 in Non-small Cell Lung Cancer
|
Chen, Xiliu
|
|
|
35 |
2 |
p.
|
artikel
|
| 52 |
RNA therapeutics in targeting G protein-coupled receptors: Recent advances and challenges
|
Yuan, Wanjun
|
|
|
35 |
2 |
p.
|
artikel
|
| 53 |
SAP30, an oncogenic driver of progression, poor survival, and drug resistance in neuroblastoma
|
Prathipati, Philip
|
|
|
35 |
2 |
p.
|
artikel
|
| 54 |
Secondary follicles enable efficient germline mtDNA base editing at hard-to-edit site
|
Xie, Qin
|
|
|
35 |
2 |
p.
|
artikel
|
| 55 |
Selective targeting of chemically modified miR-34a to prostate cancer using a small molecule ligand and an endosomal escape agent
|
Abdelaal, Ahmed M.
|
|
|
35 |
2 |
p.
|
artikel
|
| 56 |
Sequencing-guided design of genetically encoded small RNAs targeting CAG repeats for selective inhibition of mutant huntingtin
|
Parasrampuria, Mansi A.
|
|
|
35 |
2 |
p.
|
artikel
|
| 57 |
Single-cell analysis of the survival mechanisms of fratricidal CAR-T targeting of T cell malignancies
|
Hu, Hui
|
|
|
35 |
2 |
p.
|
artikel
|
| 58 |
STAT6-targeting antisense oligonucleotides against solitary fibrous tumor
|
Li, Yi
|
|
|
35 |
2 |
p.
|
artikel
|
| 59 |
Supercoiled DNA percentage: A key in-process control of linear DNA template for mRNA drug substance manufacturing
|
Piao, Xijun
|
|
|
35 |
2 |
p.
|
artikel
|
| 60 |
Temporal restriction of Cas9 expression improves CRISPR-mediated deletion efficacy and fidelity
|
Weber, Jesse A.
|
|
|
35 |
2 |
p.
|
artikel
|
| 61 |
TGF-β1-triggered BMI1 and SMAD2 cooperatively regulate miR-191 to modulate bone formation
|
Zhang, Xiao-Fei
|
|
|
35 |
2 |
p.
|
artikel
|
| 62 |
The mRNACalc webserver accounts for the N1-methylpseudouridine hypochromicity to enable precise nucleoside-modified mRNA quantification
|
Finol, Esteban
|
|
|
35 |
2 |
p.
|
artikel
|
| 63 |
Trans-amplifying RNA expressing functional miRNA mediates target gene suppression and simultaneous transgene expression
|
Yıldız, Ayşegül
|
|
|
35 |
2 |
p.
|
artikel
|
| 64 |
Trans-amplifying RNA hitting new grounds: Gene regulation by microRNA
|
Lundstrom, Kenneth
|
|
|
35 |
2 |
p.
|
artikel
|
| 65 |
Unlocking the therapeutic potential of locked nucleic acids through lipid nanoparticle delivery
|
Qassem, Shahd
|
|
|
35 |
2 |
p.
|
artikel
|
| 66 |
Whole-transcriptome analysis of aluminum-exposed rat hippocampus and identification of ceRNA networks to investigate neurotoxicity of Al
|
He, Chanting
|
|
|
35 |
2 |
p.
|
artikel
|
| 67 |
WITHDRAWN: SPOP Promotes Acute Myeloid Leukemia Initiation and Development Through miR-183-Mediated METAP2 Inhibition
|
Yu, Jifeng
|
|
|
35 |
2 |
p.
|
artikel
|
| 68 |
WITHDRAWN: The miR-424/miR-503 MicroRNA Cluster Prevents the Malignant Phenotype in Cervical Cancer Cells by Negatively Regulating CCND1
|
Chen, Xiaomei
|
|
|
35 |
2 |
p.
|
artikel
|
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