| nr |
titel |
auteur |
tijdschrift |
jaar |
jaarg. |
afl. |
pagina('s) |
type |
| 1 |
A Hyperactive Transposase Promotes Persistent Gene Transfer of a piggyBac DNA Transposon
|
Burnight, Erin R
|
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2012
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1 |
C |
p. -
1 p.
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artikel
|
| 2 |
An RNA Alternative to Human Transferrin: A New Tool for Targeting Human Cells
|
Wilner, Samantha E
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|
2012
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1 |
C |
p. -
1 p.
|
artikel
|
| 3 |
Antisense 2′-Deoxy, 2′-Fluoroarabino Nucleic Acid (2′F-ANA) Oligonucleotides: In Vitro Gymnotic Silencers of Gene Expression Whose Potency Is Enhanced by Fatty Acids
|
Souleimanian, Naira
|
|
2012
|
1 |
C |
p. -
1 p.
|
artikel
|
| 4 |
Antisense Oligonucleotide (AON)-based Therapy for Leber Congenital Amaurosis Caused by a Frequent Mutation in CEP290
|
Collin, Rob WJ
|
|
2012
|
1 |
C |
p. -
1 p.
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artikel
|
| 5 |
AON-mediated Exon Skipping Restores Ciliation in Fibroblasts Harboring the Common Leber Congenital Amaurosis CEP290 Mutation
|
Gerard, Xavier
|
|
2012
|
1 |
C |
p. -
1 p.
|
artikel
|
| 6 |
A Promising Vector for TCR Gene Therapy: Differential Effect of siRNA, 2A Peptide, and Disulfide Bond on the Introduced TCR Expression
|
Okamoto, Sachiko
|
|
2012
|
1 |
C |
p. -
1 p.
|
artikel
|
| 7 |
Arresting the Culprit: Targeted Antagomir Delivery to Sequester Oncogenic miR-221 in HCC
|
Kasinski, Andrea L
|
|
2012
|
1 |
C |
p. -
1 p.
|
artikel
|
| 8 |
A Selective Inhibitor of Human C-reactive Protein Translation Is Efficacious In Vitro and in C-reactive Protein Transgenic Mice and Humans
|
Jones, Nicholas R
|
|
2012
|
1 |
C |
p. -
1 p.
|
artikel
|
| 9 |
Assessment of Integration-defective HIV-1 and EIAV Vectors In Vitro and In Vivo
|
Ellis, Scott
|
|
2012
|
1 |
C |
p. -
1 p.
|
artikel
|
| 10 |
Chemically Modified Oligonucleotides Modulate an Epigenetically Varied and Transient Form of Transcription Silencing of HIV-1 in Human Cells
|
Knowling, Stuart
|
|
2012
|
1 |
C |
p. -
1 p.
|
artikel
|
| 11 |
Cholesterol-lowering Action of BNA-based Antisense Oligonucleotides Targeting PCSK9 in Atherogenic Diet-induced Hypercholesterolemic Mice
|
Yamamoto, Tsuyoshi
|
|
2012
|
1 |
C |
p. -
1 p.
|
artikel
|
| 12 |
Deep Sequencing Analyses of DsiRNAs Reveal the Influence of 3′ Terminal Overhangs on Dicing Polarity, Strand Selectivity, and RNA Editing of siRNAs
|
Zhou, Jiehua
|
|
2012
|
1 |
C |
p. -
1 p.
|
artikel
|
| 13 |
Defined Folate-PEG-siRNA Conjugates for Receptor-specific Gene Silencing
|
Dohmen, Christian
|
|
2012
|
1 |
C |
p. -
1 p.
|
artikel
|
| 14 |
Delivery of Quantum Dot-siRNA Nanoplexes in SK-N-SH Cells for BACE1 Gene Silencing and Intracellular Imaging
|
Li, Shengliang
|
|
2012
|
1 |
C |
p. -
1 p.
|
artikel
|
| 15 |
Development of a 2′,4′-BNA/LNA-based siRNA for Dyslipidemia and Assessment of the Effects of Its Chemical Modifications In Vivo
|
Wada, Shunsuke
|
|
2012
|
1 |
C |
p. -
1 p.
|
artikel
|
| 16 |
DNA Damage Response Pathway and Replication Fork Stress During Oligonucleotide Directed Gene Editing
|
Bonner, Melissa
|
|
2012
|
1 |
C |
p. -
1 p.
|
artikel
|
| 17 |
Dual Myostatin and Dystrophin Exon Skipping by Morpholino Nucleic Acid Oligomers Conjugated to a Cell-penetrating Peptide Is a Promising Therapeutic Strategy for the Treatment of Duchenne Muscular Dystrophy
|
Malerba, Alberto
|
|
2012
|
1 |
C |
p. -
1 p.
|
artikel
|
| 18 |
Epigenetic Modification of the Repair Donor Regulates Targeted Gene Correction
|
Humbert, Olivier
|
|
2012
|
1 |
C |
p. -
1 p.
|
artikel
|
| 19 |
Exploiting the Intron-splicing Mechanism of Insect Cells to Produce Viral Vectors Harboring Toxic Genes for Suicide Gene Therapy
|
Chen, Haifeng
|
|
2012
|
1 |
C |
p. -
1 p.
|
artikel
|
| 20 |
Expression Analysis in Multiple Muscle Groups and Serum Reveals Complexity in the MicroRNA Transcriptome of the mdx Mouse with Implications for Therapy
|
Roberts, Thomas C
|
|
2012
|
1 |
C |
p. -
1 p.
|
artikel
|
| 21 |
Formulation of Small Activating RNA Into Lipidoid Nanoparticles Inhibits Xenograft Prostate Tumor Growth by Inducing p21 Expression
|
Place, Robert F
|
|
2012
|
1 |
C |
p. -
1 p.
|
artikel
|
| 22 |
Gene Expression Profile Changes After Short-activating RNA-mediated Induction of Endogenous Pluripotency Factors in Human Mesenchymal Stem Cells
|
Voutila, Jon
|
|
2012
|
1 |
C |
p. -
1 p.
|
artikel
|
| 23 |
Gene Silencing Mediated by siRNA-binding Fusion Proteins Is Attenuated by Double-stranded RNA-binding Domain Structure
|
Geoghegan, James C
|
|
2012
|
1 |
C |
p. -
1 p.
|
artikel
|
| 24 |
HIV-1 Escape From RNAi Antivirals: Yet Another Houdini Action?
|
Berkhout, Ben
|
|
2012
|
1 |
C |
p. -
1 p.
|
artikel
|
| 25 |
Intracellular Delivery of Short Interfering RNA in Rat Organ of Corti Using a Cell-penetrating Peptide PepFect6
|
Dash-Wagh, Suvarna
|
|
2012
|
1 |
C |
p. -
1 p.
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artikel
|
| 26 |
Intracerebral Infusion of Antisense Oligonucleotides Into Prion-infected Mice
|
Nazor Friberg, Karah
|
|
2012
|
1 |
C |
p. -
1 p.
|
artikel
|
| 27 |
Lentiviral Vector Gene Transfer to Porcine Airways
|
Sinn, Patrick L
|
|
2012
|
1 |
C |
p. -
1 p.
|
artikel
|
| 28 |
Long-term Exon Skipping Studies With 2′-O-Methyl Phosphorothioate Antisense Oligonucleotides in Dystrophic Mouse Models
|
Tanganyika-de Winter, Christa L
|
|
2012
|
1 |
C |
p. -
1 p.
|
artikel
|
| 29 |
LOX-1 Inhibition in ApoE KO Mice Using a Schizophyllan-based Antisense Oligonucleotide Therapy
|
Amati, Francesca
|
|
2012
|
1 |
C |
p. -
1 p.
|
artikel
|
| 30 |
Manipulation of Cell Physiology Enables Gene Silencing in Well-differentiated Airway Epithelia
|
Krishnamurthy, Sateesh
|
|
2012
|
1 |
C |
p. -
1 p.
|
artikel
|
| 31 |
Microfluidic Synthesis of Highly Potent Limit-size Lipid Nanoparticles for In Vivo Delivery of siRNA
|
Belliveau, Nathan M
|
|
2012
|
1 |
C |
p. -
1 p.
|
artikel
|
| 32 |
MicroRNA-181a* Targets Nanog in a Subpopulation of CD34+ Cells Isolated From Peripheral Blood
|
Mintz, Paul J
|
|
2012
|
1 |
C |
p. -
1 p.
|
artikel
|
| 33 |
miR-1289 and “Zipcode”-like Sequence Enrich mRNAs in Microvesicles
|
Bolukbasi, Mehmet Fatih
|
|
2012
|
1 |
C |
p. -
1 p.
|
artikel
|
| 34 |
Molecular Therapy's New Open-access Sibling
|
Frederickson, Robert M
|
|
2012
|
1 |
C |
p. -
1 p.
|
artikel
|
| 35 |
Moving Successful Virus-specific T-cell Therapy for Hematopoietic Stem Cell Recipients to Late Phase Clinical Trials
|
Rooney, Cliona
|
|
2012
|
1 |
C |
p. -
1 p.
|
artikel
|
| 36 |
Natural Antisense Makes Sense for Gene-specific Activation in Brain
|
Varela, Miguel A
|
|
2012
|
1 |
C |
p. -
1 p.
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artikel
|
| 37 |
Nonviral Direct Conversion of Primary Mouse Embryonic Fibroblasts to Neuronal Cells
|
Adler, Andrew F
|
|
2012
|
1 |
C |
p. -
1 p.
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artikel
|
| 38 |
Oligonucleotide Delivery to the Lung: Waiting to Inhale
|
Kjems, Jørgen
|
|
2012
|
1 |
C |
p. -
1 p.
|
artikel
|
| 39 |
Optimized In Vivo Transfer of Small Interfering RNA Targeting Dermal Tissue Using In Vivo Surface Electroporation
|
Broderick, Kate E
|
|
2012
|
1 |
C |
p. -
1 p.
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artikel
|
| 40 |
Peptide-mediated Cell and In Vivo Delivery of Antisense Oligonucleotides and siRNA
|
Järver, Peter
|
|
2012
|
1 |
C |
p. -
1 p.
|
artikel
|
| 41 |
Pharmacokinetics and Toxicity in Rats and Monkeys of coDbait: A Therapeutic Double-stranded DNA Oligonucleotide Conjugated to Cholesterol
|
Schlegel, Anne
|
|
2012
|
1 |
C |
p. -
1 p.
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artikel
|
| 42 |
Pip6-PMO, A New Generation of Peptide-oligonucleotide Conjugates With Improved Cardiac Exon Skipping Activity for DMD Treatment
|
Betts, Corinne
|
|
2012
|
1 |
C |
p. -
1 p.
|
artikel
|
| 43 |
Proliferation of Genetically Modified Human Cells on Electrospun Nanofiber Scaffolds
|
Borjigin, Mandula
|
|
2012
|
1 |
C |
p. -
1 p.
|
artikel
|
| 44 |
Quantitative Analysis of Survivin Protein Expression and Its Therapeutic Depletion by an Antisense Oligonucleotide in Human Lung Tumors
|
Olsen, Anna L
|
|
2012
|
1 |
C |
p. -
1 p.
|
artikel
|
| 45 |
Random Insertion of mCherry Into VP3 Domain of Adeno-associated Virus Yields Fluorescent Capsids With no Loss of Infectivity
|
Judd, Justin
|
|
2012
|
1 |
C |
p. -
1 p.
|
artikel
|
| 46 |
Response to “HIV Escape From RNAi Antivirals: Yet Another Houdini Action?”
|
Shah, Priya S
|
|
2012
|
1 |
C |
p. -
1 p.
|
artikel
|
| 47 |
Rolling Circle Transcription of Tandem siRNA to Generate Spherulitic RNA Nanoparticles for Cell Entry
|
Guo, Peixuan
|
|
2012
|
1 |
C |
p. -
1 p.
|
artikel
|
| 48 |
siRNA-optimized Modifications for Enhanced In Vivo Activity
|
Kenski, Denise M
|
|
2012
|
1 |
C |
p. -
1 p.
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artikel
|
| 49 |
Small RNA-Mediated Epigenetic Myostatin Silencing
|
Roberts, Thomas C
|
|
2012
|
1 |
C |
p. -
1 p.
|
artikel
|
| 50 |
Specific Inhibition of SRC Kinase Impairs Malignant Glioma Growth In Vitro and In Vivo
|
Stedt, Hanna
|
|
2012
|
1 |
C |
p. -
1 p.
|
artikel
|
| 51 |
Specific Jak3 Downregulation in Lymphocytes Impairs γc Cytokine Signal Transduction and Alleviates Antigen-driven Inflammation In Vivo
|
Gómez-Valadés, Alicia G
|
|
2012
|
1 |
C |
p. -
1 p.
|
artikel
|
| 52 |
Structure Activity Relationships of α-L-LNA Modified Phosphorothioate Gapmer Antisense Oligonucleotides in Animals
|
Seth, Punit P
|
|
2012
|
1 |
C |
p. -
1 p.
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artikel
|
| 53 |
Systemic RNAi-mediated Gene Silencing in Nonhuman Primate and Rodent Myeloid Cells
|
Novobrantseva, Tatiana I
|
|
2012
|
1 |
C |
p. -
1 p.
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artikel
|
| 54 |
Taking a Break From Huntingtin
|
Davidson, Beverly L
|
|
2012
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1 |
C |
p. -
1 p.
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artikel
|
| 55 |
Targeted Exon Skipping to Address “Leaky” Mutations in the Dystrophin Gene
|
Fletcher, Sue
|
|
2012
|
1 |
C |
p. -
1 p.
|
artikel
|
| 56 |
Targeted siRNA Delivery and mRNA Knockdown Mediated by Bispecific Digoxigenin-binding Antibodies
|
Schneider, Britta
|
|
2012
|
1 |
C |
p. -
1 p.
|
artikel
|
| 57 |
Targeting DNA With Fingers and TALENs
|
Carlson, Daniel F
|
|
2012
|
1 |
C |
p. -
1 p.
|
artikel
|
| 58 |
Targeting LDL Cholesterol With LNA
|
Krieg, Arthur M
|
|
2012
|
1 |
C |
p. -
1 p.
|
artikel
|
| 59 |
The Business of RNAi Therapeutics in 2012
|
Haussecker, Dirk
|
|
2012
|
1 |
C |
p. -
1 p.
|
artikel
|
| 60 |
The Cellular Processing Capacity Limits the Amounts of Chimeric U7 snRNA Available for Antisense Delivery
|
Eckenfelder, Agathe
|
|
2012
|
1 |
C |
p. -
1 p.
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artikel
|
| 61 |
Thermal Stability of siRNA Modulates Aptamer- conjugated siRNA Inhibition
|
Berezhnoy, Alexey
|
|
2012
|
1 |
C |
p. -
1 p.
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artikel
|
| 62 |
Virus-mediated Genetic Surgery: Homologous Recombination With a Little “Helper” From My Friends
|
Gruenert, Dieter C
|
|
2012
|
1 |
C |
p. -
1 p.
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artikel
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