| nr |
titel |
auteur |
tijdschrift |
jaar |
jaarg. |
afl. |
pagina('s) |
type |
| 1 |
Advances in stem cell and cellular therapeutics from the 9th Midwest Conference on Cell Therapy and Regenerative Medicine
|
Balusu, Ramesh
|
|
|
33 |
8 |
p. 3464-3469
|
artikel
|
| 2 |
Age-sensitive response of systemic AAV-mediated gene therapy in a newly characterized feline model of mucolipidosis II
|
Pyne, Nettie K.
|
|
|
33 |
8 |
p. 3808-3821
|
artikel
|
| 3 |
BIN1 gene replacement reverses BIN1-related centronuclear myopathy
|
Ji, Jacqueline
|
|
|
33 |
8 |
p. 3701-3717
|
artikel
|
| 4 |
Designing better gene therapies for lysosomal storage disorders using engineered enzymes
|
Miller-Hodges, Eve
|
|
|
33 |
8 |
p. 3483-3484
|
artikel
|
| 5 |
Engineering TME-gated inducible CAR-T cell therapy for solid tumors
|
Nguyen, Huong T.X.
|
|
|
33 |
8 |
p. 3546-3558
|
artikel
|
| 6 |
Enhanced CAR-T cell function and mitochondrial fitness from earlier unfractionated stem cell product in multiple myeloma
|
Freeman, Ciara L.
|
|
|
33 |
8 |
p. 3576-3589
|
artikel
|
| 7 |
ErbB2/HER2-targeted CAR-NK cells eliminate breast cancer cells in an organoid model that recapitulates tumor progression
|
Röder, Jasmin
|
|
|
33 |
8 |
p. 3559-3575
|
artikel
|
| 8 |
FLT201, a novel liver-directed AAV gene therapy candidate for Gaucher disease type 1
|
Comper, Fabrizio
|
|
|
33 |
8 |
p. 3789-3807
|
artikel
|
| 9 |
Galectin-4 potentiates CD8+ T cell immunity by enhancing MHC-I expression on dendritic cells
|
Lee, In-Gu
|
|
|
33 |
8 |
p. 3662-3679
|
artikel
|
| 10 |
Gene replacement therapy for centronuclear myopathy: A breakthrough in complex genetic muscle disease
|
Takeda, Tetsuya
|
|
|
33 |
8 |
p. 3474-3475
|
artikel
|
| 11 |
GRP94 is indispensable for definitive endoderm specification of human induced pluripotent stem cells
|
Wei, Hua
|
|
|
33 |
8 |
p. 3994-4006
|
artikel
|
| 12 |
Guarding glomeruli from immune injury
|
Navratil, Emma M.
|
|
|
33 |
8 |
p. 3479-3480
|
artikel
|
| 13 |
Highly conserved brain vascular receptor ALPL mediates transport of engineered AAV vectors across the blood-brain barrier
|
Moyer, Tyler C.
|
|
|
33 |
8 |
p. 3902-3916
|
artikel
|
| 14 |
Histone deacetylases and their inhibitors in kidney diseases
|
Zheng, Yue
|
|
|
33 |
8 |
p. 3485-3527
|
artikel
|
| 15 |
Hypoxia-regulatable CAR T cells
|
Fry, Terry J.
|
|
|
33 |
8 |
p. 3473
|
artikel
|
| 16 |
Identification of a robust promoter in mouse and human hepatocytes by in vivo biopanning of a barcoded AAV library
|
Becker, Jonas
|
|
|
33 |
8 |
p. 3881-3901
|
artikel
|
| 17 |
IGFBP7: A potential target for tubular lipogenesis in CKD
|
Liu, Min
|
|
|
33 |
8 |
p. 3481-3482
|
artikel
|
| 18 |
IL-2-independent expansion, persistence, and antitumor activity in TIL expressing regulatable membrane-bound IL-15
|
Burga, Rachel A.
|
|
|
33 |
8 |
p. 3605-3623
|
artikel
|
| 19 |
In this issue
|
|
|
|
33 |
8 |
p. 3453-3454
|
artikel
|
| 20 |
Intravitreal adenine base editing of RS1 improves vision in a preclinical mouse model of retinoschisis
|
Jo, Dong Hyun
|
|
|
33 |
8 |
p. 3955-3967
|
artikel
|
| 21 |
Intrinsic/proximal cell surface marker logic-gated extracellular targeted protein degradation in specific cell population
|
Wang, Yafeng
|
|
|
33 |
8 |
p. 3644-3661
|
artikel
|
| 22 |
In vivo programming of adult pericytes aids axon regeneration by providing cellular bridges for SCI repair
|
Sun, Wenjing
|
|
|
33 |
8 |
p. 3968-3993
|
artikel
|
| 23 |
Locking CBL TKBD in its native conformation presents a novel therapeutic opportunity in mutant CBL-dependent leukemia
|
Ahmed, Syed Feroj
|
|
|
33 |
8 |
p. 3624-3643
|
artikel
|
| 24 |
Long-term effects of s-KL treatment in wild-type mice: Enhancing longevity, physical well-being, and neurological resilience
|
Roig-Soriano, Joan
|
|
|
33 |
8 |
p. 4007
|
artikel
|
| 25 |
Molecular Therapy family highlights
|
|
|
|
33 |
8 |
p. 3455
|
artikel
|
| 26 |
Neurons fuel cancer metastasis through mitochondrial transfer
|
Zhang, Yaguang
|
|
|
33 |
8 |
p. 3462-3463
|
artikel
|
| 27 |
Neuron-targeted gene therapy rescues multiple phenotypes of STXBP1-related disorders in mice and is well tolerated in nonhuman primates
|
Aeran, Rangoli
|
|
|
33 |
8 |
p. 3822-3840
|
artikel
|
| 28 |
NOTCH2 mutation in centronuclear myopathy: Beyond the scope
|
Tehrani, Eric
|
|
|
33 |
8 |
p. 3476-3478
|
artikel
|
| 29 |
Osteoarthritis gene therapy: Expanding the scope of genetic therapies
|
Evans, Christopher H.
|
|
|
33 |
8 |
p. 3456-3457
|
artikel
|
| 30 |
Renal tubular epithelial IGFBP7 interacts with PKM2 to drive renal lipid accumulation and fibrosis
|
Yu, Ju-tao
|
|
|
33 |
8 |
p. 3757-3777
|
artikel
|
| 31 |
Restoring AIBP expression in the retina provides neuroprotection in glaucoma
|
Ju, Won-Kyu
|
|
|
33 |
8 |
p. 3841-3862
|
artikel
|
| 32 |
Retraction Notice to: LncRNA ODRUL Contributes to Osteosarcoma Progression through the miR-3182/MMP2 Axis
|
Zhu, Kun-Peng
|
|
|
33 |
8 |
p. 4008
|
artikel
|
| 33 |
RNAi-mediated silencing of SOD1 profoundly extends survival and functional outcomes in ALS mice
|
Weiss, Alexandra
|
|
|
33 |
8 |
p. 3917-3938
|
artikel
|
| 34 |
Safety and efficacy of CRISPR-mediated genome ablation of VEGFA as a treatment for choroidal neovascularization in nonhuman primate eyes
|
Sin, Tzu-Ni
|
|
|
33 |
8 |
p. 3939-3954
|
artikel
|
| 35 |
SARS-CoV-2 N protein induces hypokalemia in acute kidney injury mice via ENaC-dependent mechanism
|
Zhang, Dan-Dan
|
|
|
33 |
8 |
p. 3778-3788
|
artikel
|
| 36 |
Small molecule inhibition of SUMOylation increases expression from AAV vectors both during and after initial transduction in mice
|
Seleme, Maria C.
|
|
|
33 |
8 |
p. 3863-3880
|
artikel
|
| 37 |
Spatial multi-omics reveals the potential involvement of SPP1+ fibroblasts in determining metabolic heterogeneity and promoting metastatic growth of colorectal cancer liver metastasis
|
Gao, Yuzhen
|
|
|
33 |
8 |
p. 3680-3700
|
artikel
|
| 38 |
Structure-guided engineering of CD112 receptor variants for optimized immunotherapy
|
Singh, Srishti
|
|
|
33 |
8 |
p. 3590-3604
|
artikel
|
| 39 |
Template-assisted sequence knockin rescues skeletal and cardiac muscle function in a deletion model of Duchenne muscular dystrophy
|
Fatehi, Sina
|
|
|
33 |
8 |
p. 3733-3745
|
artikel
|
| 40 |
Tolerogenic antigen-specific vaccine induces VISTA-enriched regulatory T cells and protects against arthritis in DRB1∗04:01 mice
|
Romero-Castillo, Laura
|
|
|
33 |
8 |
p. 3528-3545
|
artikel
|
| 41 |
Truncated complement factor H Y402 gene therapy rescues C3 glomerulonephritis
|
Chew, Lindsey A.
|
|
|
33 |
8 |
p. 3746-3756
|
artikel
|
| 42 |
Tumor-targeted cytokine delivery by engineered myeloid cells unlocks CAR T cell efficacy and endogenous T cell responses in glioblastoma
|
Rossari, Federico
|
|
|
33 |
8 |
p. 3458-3461
|
artikel
|
| 43 |
Understanding the role of NOTCH2 mutation in centronuclear myopathy
|
Lin, Youxi
|
|
|
33 |
8 |
p. 3718-3732
|
artikel
|
| 44 |
Vaccine therapy for rheumatoid arthritis: A step forward
|
Nikhat, Sameena
|
|
|
33 |
8 |
p. 3470-3472
|
artikel
|
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