| nr |
titel |
auteur |
tijdschrift |
jaar |
jaarg. |
afl. |
pagina('s) |
type |
| 1 |
AAT-MSC-EVs: Novel implications for suppressing ferroptosis, fibrosis and pain associated with chronic pancreatitis
|
Shoeibi, Sara
|
|
|
33 |
7 |
p. 3321-3338
|
artikel
|
| 2 |
AAV-Sparcl1 promotes hair cell regeneration by increasing supporting cell plasticity
|
Li, Nianci
|
|
|
33 |
7 |
p. 3022-3035
|
artikel
|
| 3 |
Ad-justing macrophages for cancer immunotherapy
|
Giacca, Giovanna
|
|
|
33 |
7 |
p. 2972-2974
|
artikel
|
| 4 |
An engineered antibody-lectin conjugate targeting the HIV glycan shield protects humanized mice against HIV challenge
|
Kumariya, Rashmi
|
|
|
33 |
7 |
p. 3147-3162
|
artikel
|
| 5 |
An engineered mitoCBE facilitates efficient mitochondrial DNA editing and modified mitochondrial transfer
|
Liu, Jie
|
|
|
33 |
7 |
p. 3114-3127
|
artikel
|
| 6 |
A precision medicine approach to primary immunodeficiency disease: Ataluren strikes nonsense mutations once again
|
Lentini, Laura
|
|
|
33 |
7 |
p. 3231-3241
|
artikel
|
| 7 |
Astrocytic BEST1 can serve as a target for functional recovery after ischemic stroke
|
Xiong, Shuai
|
|
|
33 |
7 |
p. 3209-3230
|
artikel
|
| 8 |
Beyond the bench: Revitalizing ataluren development for rare genetic disorders
|
Bezzerri, Valentino
|
|
|
33 |
7 |
p. 2968-2969
|
artikel
|
| 9 |
Bispecific receptor decoy proteins block ocular neovascularization via simultaneous blockade of vascular endothelial growth factor A and C
|
Sargunas, Paul R.
|
|
|
33 |
7 |
p. 3128-3146
|
artikel
|
| 10 |
Bispecific receptor decoys: A new player to a crowded field
|
Yiu, Glenn
|
|
|
33 |
7 |
p. 2964-2965
|
artikel
|
| 11 |
CD38hi macrophages promote fibrotic transition following acute kidney injury by modulating NAD+ metabolism
|
Yao, Weijian
|
|
|
33 |
7 |
p. 3434-3452
|
artikel
|
| 12 |
CD47 peptide-cloaked lipid nanoparticles promote cell-specific mRNA delivery
|
Papp, Tyler Ellis
|
|
|
33 |
7 |
p. 3195-3208
|
artikel
|
| 13 |
Combinatorial gene therapy for gyrate atrophy of the choroid and retina
|
Chekuri, Anil
|
|
|
33 |
7 |
p. 2955-2956
|
artikel
|
| 14 |
Combined AAV-mediated specific Gjb2 expression restores hearing in DFNB1 mouse models
|
Sun, Qiuhan
|
|
|
33 |
7 |
p. 3006-3021
|
artikel
|
| 15 |
Combined intraocular and intravenous gene delivery for therapy of gyrate atrophy of the choroid and retina
|
Dell’Aquila, Fabio
|
|
|
33 |
7 |
p. 2997-3005
|
artikel
|
| 16 |
Correcting a patient-specific Rhodopsin mutation with adenine base editor in a mouse model
|
He, Xiaoxue
|
|
|
33 |
7 |
p. 3101-3113
|
artikel
|
| 17 |
DNA-based delivery of G-CSF as a durable and efficacious approach to treat severe chronic neutropenia
|
Drozdz, Marek M.
|
|
|
33 |
7 |
p. 3257-3269
|
artikel
|
| 18 |
Double trouble: Non-relapse mortality with bispecific antibodies in lymphoma and myeloma
|
Banerjee, Rahul
|
|
|
33 |
7 |
p. 2966-2967
|
artikel
|
| 19 |
Extrachromosomal DNA maintenance and DNA damage response: A bidirectional axis in cancer progression and therapy
|
Meng, Yang
|
|
|
33 |
7 |
p. 2984-2986
|
artikel
|
| 20 |
Gene delivery of SUMO1-derived peptide rescues neuronal degeneration and motor deficits in a mouse model of Parkinson’s disease
|
Liang, Zhaohui
|
|
|
33 |
7 |
p. 3056-3072
|
artikel
|
| 21 |
Genetically engineered macrophages reverse the immunosuppressive tumor microenvironment and improve immunotherapeutic efficacy in TNBC
|
Jiang, Ranran
|
|
|
33 |
7 |
p. 3339-3359
|
artikel
|
| 22 |
Harnessing B19-directed CAR T cells for AAV vector administration in seropositive patients: The importance of the niche
|
Saliba, Hanadi
|
|
|
33 |
7 |
p. 2962-2963
|
artikel
|
| 23 |
Harnessing engineered NK cells for refractory CD30+ lymphoma
|
Nieto, Yago
|
|
|
33 |
7 |
p. 2981-2983
|
artikel
|
| 24 |
IFN-γ-mediated suppression of Caspase-7 exacerbates acute lung injury induced by CAR-T cells
|
Hou, Rui
|
|
|
33 |
7 |
p. 3392-3406
|
artikel
|
| 25 |
Immunophenotype of CAR T cells and apheresis products predicts response in CD22 CAR T cell trial for B cell acute lymphoblastic leukemia
|
Dreyzin, Alexandra
|
|
|
33 |
7 |
p. 3360-3374
|
artikel
|
| 26 |
Improved SARS-CoV-2 vaccine based on intranasally administered replicon RNA
|
Lundstrom, Kenneth
|
|
|
33 |
7 |
p. 2970-2971
|
artikel
|
| 27 |
Interaction between stromal cells and tumor cells promotes GCB-DLBCL cell survival via the CD40/RANK-KDM6B-NF-κB axis
|
Liu, Dandan
|
|
|
33 |
7 |
p. 3407-3422
|
artikel
|
| 28 |
In this issue
|
|
|
|
33 |
7 |
p. 2952-2953
|
artikel
|
| 29 |
Intranasal replicon SARS-CoV-2 vaccine produces protective respiratory and systemic immunity and prevents viral transmission
|
Jennewein, Madeleine F.
|
|
|
33 |
7 |
p. 3286-3306
|
artikel
|
| 30 |
In utero genetic therapy: Treatment of early onset neurological disorders before they start
|
Borges, Beltran
|
|
|
33 |
7 |
p. 2977-2980
|
artikel
|
| 31 |
Living myocardial slices as a model for testing cardiac pro-reparative gene therapies
|
Caliandro, Rocco
|
|
|
33 |
7 |
p. 2990-2996
|
artikel
|
| 32 |
Memory matters: T cell phenotype shapes CAR T cell fate
|
Di Meo, Francesco
|
|
|
33 |
7 |
p. 2975-2976
|
artikel
|
| 33 |
Molecular Therapy family highlights
|
|
|
|
33 |
7 |
p. 2954
|
artikel
|
| 34 |
Myeloma cell-intrinsic ANXA1 elevation and T cell dysfunction contribute to BCMA-negative relapse after CAR-T therapy
|
Yang, Shuangshuang
|
|
|
33 |
7 |
p. 3375-3391
|
artikel
|
| 35 |
Non-relapse mortality with bispecific antibodies: A systematic review and meta-analysis in lymphoma and multiple myeloma
|
Tix, Tobias
|
|
|
33 |
7 |
p. 3163-3176
|
artikel
|
| 36 |
Novel AAV-based GJB2 gene therapy restores hearing function
|
Landegger, Lukas D.
|
|
|
33 |
7 |
p. 2957-2958
|
artikel
|
| 37 |
Preclinical development of lentiviral vector gene therapy for Diamond-Blackfan anemia syndrome
|
Bhoopalan, Senthil Velan
|
|
|
33 |
7 |
p. 3086-3100
|
artikel
|
| 38 |
Pro-inflammatory microglia-targeted peptide therapy ameliorates neonatal hypoxic-ischemic encephalopathy in mice
|
Zen, Rika
|
|
|
33 |
7 |
p. 3177-3194
|
artikel
|
| 39 |
RNA interference targeting lipoprotein(a): A “big hit” against “little a”?
|
Stewart, Duncan J.
|
|
|
33 |
7 |
p. 2951
|
artikel
|
| 40 |
Seltoplasmid promotes ulcer healing versus placebo for treating patients with chronic limb-threatening ischemia: HOPE CLTI-2 trial
|
Di, Xiao
|
|
|
33 |
7 |
p. 3423-3433
|
artikel
|
| 41 |
Single-dose intranasal AdC68-vectored vaccines rapidly protect Syrian hamsters against lethal Nipah virus infection
|
Lu, Mingqing
|
|
|
33 |
7 |
p. 3270-3285
|
artikel
|
| 42 |
Targeting EBV gp42 for nasopharyngeal carcinoma prevention
|
Sun, Cong
|
|
|
33 |
7 |
p. 2987-2989
|
artikel
|
| 43 |
TNFAIP8L2 as a dual regulator of mTORC1 signaling: Implications for therapy in presbycusis
|
Wang, Yanfei
|
|
|
33 |
7 |
p. 2959-2961
|
artikel
|
| 44 |
TNFAIP8L2 maintains hair cell function and regulates age-related hearing loss via mTORC1 signaling
|
Li, Wen
|
|
|
33 |
7 |
p. 3036-3055
|
artikel
|
| 45 |
Urine-derived stem cells display homing, incorporation, and regeneration in human organoid and mouse models of acute kidney injury
|
Bejoy, Julie
|
|
|
33 |
7 |
p. 3307-3320
|
artikel
|
| 46 |
Use of CD19-targeted immune modulation to eradicate AAV-neutralizing antibodies
|
Doshi, Bhavya S.
|
|
|
33 |
7 |
p. 3073-3085
|
artikel
|
| 47 |
VEGF-B is a novel mediator of ER stress which induces cardiac angiogenesis via RGD-binding integrins independent of VEGFR1/NRP activities
|
Mallick, Rahul
|
|
|
33 |
7 |
p. 3242-3256
|
artikel
|
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