| nr |
titel |
auteur |
tijdschrift |
jaar |
jaarg. |
afl. |
pagina('s) |
type |
| 1 |
Allogeneic CAR T cells: A new player in the field and the peculiar opportunities of the hospital exemption path
|
Del Bufalo, Francesca
|
|
|
33 |
6 |
p. 2326-2327
|
artikel
|
| 2 |
Autologous CD7 CAR-T cells generated without T cell pre-selection in pediatric patients with relapsed/refractory T-ALL: A phase I trial
|
Zhao, Liping
|
|
|
33 |
6 |
p. 2753-2767
|
artikel
|
| 3 |
Autologous transplantation of mitochondria/rAAV IGF-I platforms in human osteoarthritic articular chondrocytes to treat osteoarthritis
|
Zhong, Gang
|
|
|
33 |
6 |
p. 2900-2912
|
artikel
|
| 4 |
CAR T cell therapy for glioblastoma: A review of the first decade of clinical trials
|
Begley, Sabrina L.
|
|
|
33 |
6 |
p. 2454-2461
|
artikel
|
| 5 |
CAR-T cell therapy for treatment of acute myeloid leukemia, advances and outcomes
|
Khalifeh, Malak
|
|
|
33 |
6 |
p. 2441-2453
|
artikel
|
| 6 |
Centrosome protein TAX1BP2 mediates STING-dependent immune response and potentiates anti-PD-1 efficacy in hepatocellular carcinoma
|
Zhang, Qingmei
|
|
|
33 |
6 |
p. 2913-2930
|
artikel
|
| 7 |
China’s first approved gene therapy for hemophilia B: A new era for global AAV-based treatments
|
Wei, Hongying
|
|
|
33 |
6 |
p. 2312-2313
|
artikel
|
| 8 |
Clinical advances in gene, cell, and RNA therapies
|
Milone, Michael C.
|
|
|
33 |
6 |
p. 2311
|
artikel
|
| 9 |
Clinical applications of exon-skipping antisense oligonucleotides in neuromuscular diseases
|
Torres-Masjoan, Laia
|
|
|
33 |
6 |
p. 2689-2704
|
artikel
|
| 10 |
Clinical applications of oligonucleotides for cancer therapy
|
DeFranciscis, Vittorio
|
|
|
33 |
6 |
p. 2705-2718
|
artikel
|
| 11 |
Clinical development of allogeneic chimeric antigen receptor αβ-T cells
|
Georgiadis, Christos
|
|
|
33 |
6 |
p. 2426-2440
|
artikel
|
| 12 |
Clinical development of therapeutic mRNA applications
|
Żak, Magdalena M.
|
|
|
33 |
6 |
p. 2583-2609
|
artikel
|
| 13 |
Clinical hematopoietic stem cell-based gene therapy
|
John, Tami
|
|
|
33 |
6 |
p. 2663-2678
|
artikel
|
| 14 |
Clinical perspective: Advancing hemophilia treatment through gene therapy approaches
|
Thornburg, Courtney D.
|
|
|
33 |
6 |
p. 2350-2362
|
artikel
|
| 15 |
Concept CARs are picking up speed
|
Mansilla-Soto, Jorge
|
|
|
33 |
6 |
p. 2363-2367
|
artikel
|
| 16 |
Current clinical applications of AAV-mediated gene therapy
|
Byrne, Barry J.
|
|
|
33 |
6 |
p. 2479-2516
|
artikel
|
| 17 |
DNA-based immunotherapy for cancer: In vivo approaches for recalcitrant targets
|
Bhojnagarwala, Pratik S.
|
|
|
33 |
6 |
p. 2719-2739
|
artikel
|
| 18 |
Effect of immunoadsorption on clinical presentation and immune alterations in COVID-19–induced and/or aggravated ME/CFS
|
Anft, Moritz
|
|
|
33 |
6 |
p. 2886-2899
|
artikel
|
| 19 |
Efficient gene delivery admitted by small metabolites specifically targeting astrocytes in the mouse brain
|
Zhou, Haibin
|
|
|
33 |
6 |
p. 2947-2949
|
artikel
|
| 20 |
Emerging combined CAR-NK cell therapies in cancer treatment: Finding a dancing partner
|
Hosseinalizadeh, Hamed
|
|
|
33 |
6 |
p. 2406-2425
|
artikel
|
| 21 |
Engineering resilient CAR T cells for immunosuppressive environment
|
Khalifeh, Malak
|
|
|
33 |
6 |
p. 2391-2405
|
artikel
|
| 22 |
Flavopiridol restores granulopoiesis in experimental models of severe congenital neutropenia
|
Nasri, Masoud
|
|
|
33 |
6 |
p. 2851-2871
|
artikel
|
| 23 |
GDF11 Protects against Endothelial Injury and Reduces Atherosclerotic Lesion Formation in Apolipoprotein E-Null Mice
|
Mei, Wen
|
|
|
33 |
6 |
p. 2946
|
artikel
|
| 24 |
Gene-based therapies for steatotic liver disease
|
Iakovleva, Viktoriia
|
|
|
33 |
6 |
p. 2527-2547
|
artikel
|
| 25 |
Gene therapy in China: From a clinician’s perspective
|
Wang, Xiaole
|
|
|
33 |
6 |
p. 2330-2331
|
artikel
|
| 26 |
GITRL enhances cytotoxicity and persistence of CAR-T cells in cancer therapy
|
Tan, Binghe
|
|
|
33 |
6 |
p. 2789-2800
|
artikel
|
| 27 |
Heterogeneity, a weak link between constrained AAV dose and long-term efficacy of gene therapy to muscular dystrophy: A critical and prospective review
|
Lu, Qi Long
|
|
|
33 |
6 |
p. 2517-2526
|
artikel
|
| 28 |
In this issue
|
|
|
|
33 |
6 |
p. 2314
|
artikel
|
| 29 |
Killing the killers: Natural killer cell therapy targeting glioma stem cells in high-grade glioma
|
Poorva, Poorva
|
|
|
33 |
6 |
p. 2462-2478
|
artikel
|
| 30 |
Long-term safety and efficacy of the fully human CAR-T therapy CT103A in relapsed/refractory multiple myeloma
|
Yu, Qiuxia
|
|
|
33 |
6 |
p. 2768-2777
|
artikel
|
| 31 |
Low-level shRNA Cytotoxicity Can Contribute to MYC-induced Hepatocellular Carcinoma in Adult Mice
|
Beer, Shelly
|
|
|
33 |
6 |
p. 2945
|
artikel
|
| 32 |
Lung endothelial transduction in a patient that succumbed to acute respiratory distress syndrome following high-dose rAAV9 gene therapy
|
Hordeaux, Juliette
|
|
|
33 |
6 |
p. 2339-2342
|
artikel
|
| 33 |
Lyophilized apoptotic vesicles improve hemostasis and bone regeneration in traumatic patients with impacted third molar extraction
|
Jiang, Yexiang
|
|
|
33 |
6 |
p. 2931-2944
|
artikel
|
| 34 |
Managing allorejection in off-the-shelf CAR-engineered cell therapies
|
Li, Yan-Ruide
|
|
|
33 |
6 |
p. 2368-2390
|
artikel
|
| 35 |
Mesenchymal stromal cell therapy: Progress to date and future outlook
|
Lu, Wen
|
|
|
33 |
6 |
p. 2679-2688
|
artikel
|
| 36 |
miRNAs as neuro-oncologic therapeutics: A narrative review
|
Das, Nikita
|
|
|
33 |
6 |
p. 2740-2752
|
artikel
|
| 37 |
Molecular Therapy family highlights
|
|
|
|
33 |
6 |
p. 2315
|
artikel
|
| 38 |
mRNA-LNPs induce immune activation and cytokine release in human whole blood assays across diverse health conditions
|
Nguyen, Hong-My
|
|
|
33 |
6 |
p. 2872-2885
|
artikel
|
| 39 |
Navigating the orphan medicinal product designation: Evidence requirements for gene therapies in Europe
|
Palomo, Gloria M.
|
|
|
33 |
6 |
p. 2834-2841
|
artikel
|
| 40 |
Patient-centered long-term follow-up for gene therapies aligns with ethics and science
|
Chapman, Carolyn Riley
|
|
|
33 |
6 |
p. 2336-2338
|
artikel
|
| 41 |
Perspective: Advancing safe and effective DNA therapeutics using bioactive lipid nanoparticles
|
Patel, Manthan N.
|
|
|
33 |
6 |
p. 2324-2325
|
artikel
|
| 42 |
Pilocytic astrocytoma in a child with spinal muscular atrophy treated with onasemnogene abeparvovec
|
Holzwarth, Dorothea
|
|
|
33 |
6 |
p. 2842-2850
|
artikel
|
| 43 |
Recent advances in therapeutic gene-editing technologies
|
Liu, Dongqi
|
|
|
33 |
6 |
p. 2619-2644
|
artikel
|
| 44 |
Recent developments in translational imaging of in vivo gene therapy outcomes
|
Day, Isabel L.
|
|
|
33 |
6 |
p. 2548-2564
|
artikel
|
| 45 |
Tailoring capsid-directed evolution technology for improved AAV-mediated CAR-T generation
|
Westhaus, Adrian
|
|
|
33 |
6 |
p. 2801-2818
|
artikel
|
| 46 |
Targeting human plasma cells using regulated BCMA CAR T cells eliminates circulating antibodies in humanized mice
|
Honaker, Yuchi
|
|
|
33 |
6 |
p. 2819-2833
|
artikel
|
| 47 |
The advent of clinical self-amplifying RNA vaccines
|
Casmil, Irafasha C.
|
|
|
33 |
6 |
p. 2565-2582
|
artikel
|
| 48 |
The high efficacy of claudin18.2-targeted CAR-T cell therapy in advanced pancreatic cancer with an antibody-dependent safety strategy
|
Zhong, Guocheng
|
|
|
33 |
6 |
p. 2778-2788
|
artikel
|
| 49 |
The impact of revised regenerative medicine regulations on unapproved gene therapies in Japan
|
Ukon, Yuichiro
|
|
|
33 |
6 |
p. 2332-2335
|
artikel
|
| 50 |
The landscape of cell and gene therapy today
|
Barrett, David
|
|
|
33 |
6 |
p. 2316-2323
|
artikel
|
| 51 |
Therapeutic mRNA vaccine applications in oncology
|
Elliott, Leighton
|
|
|
33 |
6 |
p. 2610-2618
|
artikel
|
| 52 |
The rise of cochlear gene therapy
|
Landegger, Lukas D.
|
|
|
33 |
6 |
p. 2343-2349
|
artikel
|
| 53 |
The risk of reactivity against healthy tissues: Novel CARs demand testing for overlooked binding properties
|
Holzinger, Astrid
|
|
|
33 |
6 |
p. 2328-2329
|
artikel
|
| 54 |
Treating genetic blood disorders in the era of CRISPR-mediated genome editing
|
Almotiri, Alhomidi
|
|
|
33 |
6 |
p. 2645-2662
|
artikel
|
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