| nr |
titel |
auteur |
tijdschrift |
jaar |
jaarg. |
afl. |
pagina('s) |
type |
| 1 |
A comprehensive atlas of AAV tropism in the mouse
|
Walkey, Christopher J.
|
|
|
33 |
3 |
p. 1282-1299
|
artikel
|
| 2 |
Artificial enforcement of the unfolded protein response reduces disease features in multiple preclinical models of ALS/FTD
|
Valenzuela, Vicente
|
|
|
33 |
3 |
p. 1226-1245
|
artikel
|
| 3 |
Boosting the X factor: Increasing XBP1s-mediated ER stress signaling protects motor neurons in ALS/FTD
|
Saxena, Smita
|
|
|
33 |
3 |
p. 844-846
|
artikel
|
| 4 |
CDK1-loaded extracellular vesicles promote cell cycle to reverse impaired wound healing in diabetic obese mice
|
Choi, Wooil
|
|
|
33 |
3 |
p. 1118-1133
|
artikel
|
| 5 |
Characterization of a novel conditional knockout mouse model to assess efficacy of mRNA therapy in the context of severe OTC deficiency
|
Zhou, Jenny
|
|
|
33 |
3 |
p. 1197-1212
|
artikel
|
| 6 |
Characterization of the ocular inflammatory response to AAV reveals divergence by sex and age
|
Clare, Alison J.
|
|
|
33 |
3 |
p. 1246-1263
|
artikel
|
| 7 |
Depletion of alloreactive B cells by drug-resistant chimeric alloantigen receptor T cells to prevent transplant rejection
|
Dragon, Anna Christina
|
|
|
33 |
3 |
p. 1031-1047
|
artikel
|
| 8 |
Efficient gene delivery admitted by small metabolites specifically targeting astrocytes in the mouse brain
|
Zhou, Haibin
|
|
|
33 |
3 |
p. 1166-1179
|
artikel
|
| 9 |
Enhanced restoration of visual code after targeting ON bipolar cells compared with retinal ganglion cells with optogenetic therapy
|
Rodgers, Jessica
|
|
|
33 |
3 |
p. 1264-1281
|
artikel
|
| 10 |
Enhancing VEGF therapy in T2D wounds with PLCγ2 epigenetic targeting
|
Kashyap, Shiridhar
|
|
|
33 |
3 |
p. 828-830
|
artikel
|
| 11 |
Expanding the engineered Treg multiverse
|
Cochrane, Russell W.
|
|
|
33 |
3 |
p. 833-836
|
artikel
|
| 12 |
FKBP51 inhibition ameliorates neurodegeneration and motor dysfunction in the neuromelanin-SNCA mouse model of Parkinson’s disease
|
Garcia-Gomara, Marta
|
|
|
33 |
3 |
p. 895-916
|
artikel
|
| 13 |
Focused ultrasound and microbubble-mediated delivery of CRISPR-Cas9 ribonucleoprotein to human induced pluripotent stem cells
|
Hazel, Kyle
|
|
|
33 |
3 |
p. 986-996
|
artikel
|
| 14 |
Focused-ultrasound-mediated CRISPR-Cas9 gene editing in human induced pluripotent stem cells
|
Owusu-Yaw, Bernie Simone
|
|
|
33 |
3 |
p. 831-832
|
artikel
|
| 15 |
Functional rescue of F508del-CFTR through revertant mutations introduced by CRISPR base editing
|
Carrozzo, Irene
|
|
|
33 |
3 |
p. 970-985
|
artikel
|
| 16 |
Gene editing of CD3 epsilon to redirect regulatory T cells for adoptive T cell transfer
|
Du, Weijie
|
|
|
33 |
3 |
p. 997-1013
|
artikel
|
| 17 |
Genetically reprogrammed exosomes for cancer immunotherapy
|
Gu, Wenxing
|
|
|
33 |
3 |
p. 837-839
|
artikel
|
| 18 |
Genetically reprogrammed exosomes for immunotherapy of acute myeloid leukemia
|
Zhang, Lei
|
|
|
33 |
3 |
p. 1091-1104
|
artikel
|
| 19 |
In situ blockade of TNF-TNFR2 axis via oncolytic adenovirus improves antitumor efficacy in solid tumors
|
Kang, Xiaozhen
|
|
|
33 |
3 |
p. 1300
|
artikel
|
| 20 |
In this issue
|
|
|
|
33 |
3 |
p. 826-827
|
artikel
|
| 21 |
Introducing John Bell, PhD: Molecular Therapy’s first front matter editor
|
|
|
|
33 |
3 |
p. 825
|
artikel
|
| 22 |
Long-read RNA sequencing: A transformative technology for exploring transcriptome complexity in human diseases
|
Ament, Isabelle Heifetz
|
|
|
33 |
3 |
p. 883-894
|
artikel
|
| 23 |
mRNA therapy as primary and bridge therapy for inborn errors of metabolism
|
Vockley, Jerry
|
|
|
33 |
3 |
p. 842-843
|
artikel
|
| 24 |
Optimizing CAR-T treatment: A T2EVOLVE guide to raw and starting material selection
|
Navarro, Sergio
|
|
|
33 |
3 |
p. 847-865
|
artikel
|
| 25 |
Pancreatic cancer-derived extracellular vesicles enhance chemoresistance by delivering KRASG12D protein to cancer-associated fibroblasts
|
Liu, Xinyuan
|
|
|
33 |
3 |
p. 1134-1153
|
artikel
|
| 26 |
PBAE-PEG-based lipid nanoparticles for lung cell-specific gene delivery
|
Liu, Bingxin
|
|
|
33 |
3 |
p. 1154-1165
|
artikel
|
| 27 |
Pharmacological blocking of microfibrillar-associated protein 4 reduces retinal neoangiogenesis and vascular leakage
|
Schlosser, Anders
|
|
|
33 |
3 |
p. 1048-1072
|
artikel
|
| 28 |
Retraction Notice to: ESCRT-mediated Uptake and Degradation of Brain-targeted α-synuclein Single Chain Antibody Attenuates Neuronal Degeneration In Vivo
|
Spencer, Brian
|
|
|
33 |
3 |
p. 1302
|
artikel
|
| 29 |
Retraction Notice to: Hypoxia-induced lncHILAR promotes renal cancer metastasis via ceRNA for the miR-613/206/ 1-1-3p/Jagged-1/Notch/CXCR4 signaling pathway
|
Hu, Guanghui
|
|
|
33 |
3 |
p. 1303
|
artikel
|
| 30 |
Retraction Notice to: Lentivirus Mediated Delivery of Neurosin Promotes Clearance of Wild-type α-Synuclein and Reduces the Pathology in an α-Synuclein Model of LBD
|
Spencer, Brian
|
|
|
33 |
3 |
p. 1301
|
artikel
|
| 31 |
Scalable control of stem cell fate by riboswitch-regulated RNA viral vector without genomic integration
|
Kim, Narae
|
|
|
33 |
3 |
p. 1213-1225
|
artikel
|
| 32 |
SINEUP RNA rescues molecular phenotypes associated with CHD8 suppression in autism spectrum disorder model systems
|
Di Leva, Francesca
|
|
|
33 |
3 |
p. 1180-1196
|
artikel
|
| 33 |
Targeting the TRIM21-PD-1 axis potentiates immune checkpoint blockade and CAR-T cell therapy
|
Shi, Jie
|
|
|
33 |
3 |
p. 1073-1090
|
artikel
|
| 34 |
Tissue nanotransfection-based endothelial PLCγ2-targeted epigenetic gene editing rescues perfusion and diabetic ischemic wound healing
|
Verma, Sumit S.
|
|
|
33 |
3 |
p. 950-969
|
artikel
|
| 35 |
TRAF1 promotes osteoclastogenesis by enhancing metabolic adaptation to oxidative phosphorylation in an AKT-dependent manner
|
Kang, Honglei
|
|
|
33 |
3 |
p. 933-949
|
artikel
|
| 36 |
Transforming bacterial pathogens into wonder tools in cancer immunotherapy
|
Senevirathne, Amal
|
|
|
33 |
3 |
p. 866-882
|
artikel
|
| 37 |
Turning ON the inner retinal circuity: An exciting new approach to optogenetic therapy
|
Rosin, Boris
|
|
|
33 |
3 |
p. 840-841
|
artikel
|
| 38 |
Virus-free CRISPR knockin of a chimeric antigen receptor into KLRC1 generates potent GD2-specific natural killer cells
|
Shankar, Keerthana
|
|
|
33 |
3 |
p. 1014-1030
|
artikel
|
| 39 |
Visualizing lipid nanoparticle trafficking for mRNA vaccine delivery in non-human primates
|
Buckley, Maureen
|
|
|
33 |
3 |
p. 1105-1117
|
artikel
|
| 40 |
Vitronectin regulates lung tissue remodeling and emphysema in chronic obstructive pulmonary disease
|
Liu, Gang
|
|
|
33 |
3 |
p. 917-932
|
artikel
|
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