| nr |
titel |
auteur |
tijdschrift |
jaar |
jaarg. |
afl. |
pagina('s) |
type |
| 1 |
AAV-mediated genome editing is influenced by the formation of R-loops
|
Puzzo, Francesco
|
|
|
32 |
12 |
p. 4256-4271
|
artikel
|
| 2 |
AAVrh.10 delivery of novel APOE2-Christchurch variant suppresses amyloid and Tau pathology in Alzheimer’s disease mice
|
Günaydin, Caner
|
|
|
32 |
12 |
p. 4303-4318
|
artikel
|
| 3 |
ANGPTL4-mediated inflammation: A new mechanism of disease and therapeutic approach for rheumatoid arthritis
|
Duran, Ivan
|
|
|
32 |
12 |
p. 4177-4179
|
artikel
|
| 4 |
A tumor-conditional IL-15 safely synergizes with immunotherapy to enhance antitumor immune responses
|
Shi, Wenqiang
|
|
|
32 |
12 |
p. 4482-4496
|
artikel
|
| 5 |
Bone-protective effects of neutralizing angiopoietin-like protein 4 monoclonal antibody in rheumatoid arthritis
|
Ke, Liqing
|
|
|
32 |
12 |
p. 4497-4513
|
artikel
|
| 6 |
Development of artificial transcription factors and their applications in cell reprograming, genetic screen, and disease treatment
|
Sang, Yetong
|
|
|
32 |
12 |
p. 4208-4234
|
artikel
|
| 7 |
Dual CRALBP isoforms unveiled: iPSC-derived retinal modeling and AAV2/5-RLBP1 gene transfer raise considerations for effective therapy
|
Damodar, Krishna
|
|
|
32 |
12 |
p. 4319-4336
|
artikel
|
| 8 |
Efficient and selective kidney targeting by chemically modified carbohydrate conjugates
|
Kumar, Vikas
|
|
|
32 |
12 |
p. 4383-4400
|
artikel
|
| 9 |
Engineered extracellular vesicles for combinatorial TNBC therapy: SR-SIM-guided design achieves substantial drug dosage reduction
|
Bhullar, Abhjeet S.
|
|
|
32 |
12 |
p. 4467-4481
|
artikel
|
| 10 |
Enhanced mucosal SARS-CoV-2 immunity after heterologous intramuscular mRNA prime/intranasal protein boost vaccination with a combination adjuvant
|
Laghlali, Gabriel
|
|
|
32 |
12 |
p. 4448-4466
|
artikel
|
| 11 |
Ex vivo-generated human CD1c+ regulatory B cells by a chemically defined system suppress immune responses and alleviate graft-versus-host disease
|
Bao, Yingying
|
|
|
32 |
12 |
p. 4372-4382
|
artikel
|
| 12 |
Gene editing efficiencies and hematopoietic stem cell fitness in sickle cell disease: A balancing act
|
Strouboulis, John
|
|
|
32 |
12 |
p. 4170-4171
|
artikel
|
| 13 |
Harnessing gene therapy for liver metabolic dysfunction: An innovative approach to MASH treatment
|
Unzu, Carmen
|
|
|
32 |
12 |
p. 4175-4176
|
artikel
|
| 14 |
Host RNA N6-methyladenosine and incoming DNA N6-methyldeoxyadenosine modifications cooperatively elevate the condensation potential of DNA to activate immune surveillance
|
Wang, Na
|
|
|
32 |
12 |
p. 4418-4434
|
artikel
|
| 15 |
Improving efficacy of in vivo therapy of sickle cell disease by hijacking natural biology of hematopoietic stem cells
|
Yao, Jia
|
|
|
32 |
12 |
p. 4167-4169
|
artikel
|
| 16 |
In this issue
|
|
|
|
32 |
12 |
p. 4165-4166
|
artikel
|
| 17 |
Introducing a hemoglobin G-Makassar variant in HSCs by in vivo base editing treats sickle cell disease in mice
|
Li, Chang
|
|
|
32 |
12 |
p. 4353-4371
|
artikel
|
| 18 |
Liver-directed AAV gene therapy normalizes disease symptoms and provides cross-correction in a model of lysosomal acid lipase deficiency
|
Lam, Patricia
|
|
|
32 |
12 |
p. 4272-4284
|
artikel
|
| 19 |
N6-Methyladenosine modification activates the serine synthesis pathway to mediate therapeutic resistance in liver cancer
|
Chan, For-Fan
|
|
|
32 |
12 |
p. 4435-4447
|
artikel
|
| 20 |
Not all carbs are bad for the kidney
|
Gusella, G. Luca
|
|
|
32 |
12 |
p. 4183-4184
|
artikel
|
| 21 |
Nucleic acid modifications in self-nonself discrimination
|
Jing, Qian
|
|
|
32 |
12 |
p. 4180-4182
|
artikel
|
| 22 |
Passing on the Molecular Therapy baton
|
Herzog, Roland W.
|
|
|
32 |
12 |
p. 4163-4164
|
artikel
|
| 23 |
PD-L1: From cancer immunotherapy to therapeutic implications in multiple disorders
|
Lee, Daeun
|
|
|
32 |
12 |
p. 4235-4255
|
artikel
|
| 24 |
Promoting readthrough of nonsense mutations in CF mouse model: Biodistribution and efficacy of NV848 in rescuing CFTR protein expression
|
Fiduccia, Ignazio
|
|
|
32 |
12 |
p. 4514-4523
|
artikel
|
| 25 |
Quantifying and mitigating motor phenotypes induced by antisense oligonucleotides in the central nervous system
|
Moazami, Michael P.
|
|
|
32 |
12 |
p. 4401-4417
|
artikel
|
| 26 |
Recombinant adeno-associated virus as a delivery platform for ocular gene therapy: A comprehensive review
|
Wang, Jiang-Hui
|
|
|
32 |
12 |
p. 4185-4207
|
artikel
|
| 27 |
Retraction Notice to: Inhibition of Multiple Protective Signaling Pathways and Ad.5/3 Delivery Enhances mda-7/IL-24 Therapy of Malignant Glioma
|
Hamed, Hossein A.
|
|
|
32 |
12 |
p. 4524
|
artikel
|
| 28 |
Reversion of metabolic dysfunction-associated steatohepatitis by skeletal muscle-directed FGF21 gene therapy
|
Jimenez, Veronica
|
|
|
32 |
12 |
p. 4285-4302
|
artikel
|
| 29 |
R-loops facilitate AAV-mediated nuclease-free gene targeting
|
Hu, Bryan
|
|
|
32 |
12 |
p. 4172-4174
|
artikel
|
| 30 |
Safety and efficacy studies of CRISPR-Cas9 treatment of sickle cell disease highlights disease-specific responses
|
Frati, Giacomo
|
|
|
32 |
12 |
p. 4337-4352
|
artikel
|
| 31 |
Thank you to our 2024 reviewers
|
|
|
|
32 |
12 |
p. 4525-4533
|
artikel
|
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