| nr |
titel |
auteur |
tijdschrift |
jaar |
jaarg. |
afl. |
pagina('s) |
type |
| 1 |
A minimally invasive endovascular approach to the cerebellopontine angle cistern enables broad CNS biodistribution of scAAV9-CB-GFP
|
Benatti, Hector Ribeiro
|
|
|
32 |
10 |
p. 3346-3355
|
artikel
|
| 2 |
A platform to deliver single and bi-specific Cas9/guide RNA to perturb genes in vitro and in vivo
|
Li, Yi-Jia
|
|
|
32 |
10 |
p. 3629-3649
|
artikel
|
| 3 |
Approval of the first TCR-based cell therapy
|
Singh, Nathan
|
|
|
32 |
10 |
p. 3195
|
artikel
|
| 4 |
Armored bicistronic CAR T cells with dominant-negative TGF-β receptor II to overcome resistance in glioblastoma
|
Li, Nannan
|
|
|
32 |
10 |
p. 3522-3538
|
artikel
|
| 5 |
A small TAT-TrkB peptide prevents BDNF receptor cleavage and restores synaptic physiology in Alzheimer's disease
|
Fonseca-Gomes, João
|
|
|
32 |
10 |
p. 3372-3401
|
artikel
|
| 6 |
A systematic review of immunosuppressive protocols used in AAV gene therapy for monogenic disorders
|
Vrellaku, Besarte
|
|
|
32 |
10 |
p. 3220-3259
|
artikel
|
| 7 |
Blunting specific T-dependent antibody responses with engineered “decoy” B cells
|
Pitner, Ragan A.
|
|
|
32 |
10 |
p. 3453-3469
|
artikel
|
| 8 |
CAR spacers: Not just filling space
|
Brown, Michael P.
|
|
|
32 |
10 |
p. 3207-3208
|
artikel
|
| 9 |
CITED4 gene therapy: Can it be cited for preventing maladaptive post-ischemic cardiac remodeling?
|
Nording, Henry
|
|
|
32 |
10 |
p. 3217-3219
|
artikel
|
| 10 |
CITED4 gene therapy protects against maladaptive cardiac remodeling after ischemia/reperfusion injury in mice
|
Lerchenmüller, Carolin
|
|
|
32 |
10 |
p. 3683-3694
|
artikel
|
| 11 |
CRISPR-mediated ablation of TP53 and EGFR mutations enhances gefitinib sensitivity and anti-tumor efficacy in lung cancer
|
Yoon, A-Rum
|
|
|
32 |
10 |
p. 3618-3628
|
artikel
|
| 12 |
Development and IND-enabling studies of a novel Cas9 genome-edited autologous CD34+ cell therapy to induce fetal hemoglobin for sickle cell disease
|
Katta, Varun
|
|
|
32 |
10 |
p. 3433-3452
|
artikel
|
| 13 |
Dual neutralization of influenza virus hemagglutinin and neuraminidase by a bispecific antibody leads to improved antiviral activity
|
Moirangthem, Romila
|
|
|
32 |
10 |
p. 3712-3728
|
artikel
|
| 14 |
Effective knockdown-replace gene therapy in a novel mouse model of DNM1 developmental and epileptic encephalopathy
|
Jones, Devin J.
|
|
|
32 |
10 |
p. 3318-3330
|
artikel
|
| 15 |
Engineering a solution for allogeneic CAR-T rejection
|
Amini, Leila
|
|
|
32 |
10 |
p. 3204-3206
|
artikel
|
| 16 |
Extracellular vesicle surface display enhances the therapeutic efficacy and safety profile of cancer immunotherapy
|
Jayasinghe, Migara Kavishka
|
|
|
32 |
10 |
p. 3558-3579
|
artikel
|
| 17 |
Hematopoietic stem cell transplantation leads to biochemical and functional correction in two mouse models of acid ceramidase deficiency
|
Rybova, Jitka
|
|
|
32 |
10 |
p. 3402-3421
|
artikel
|
| 18 |
High-throughput screening identifies ibuprofen as an sEV PD-L1 inhibitor for synergistic cancer immunotherapy
|
Chen, Zhuo-Kun
|
|
|
32 |
10 |
p. 3580-3596
|
artikel
|
| 19 |
Hybrid non-viral and viral delivery strategy achieves potent gene editing in growing livers with reduced viral dosage
|
Gong, Fanglin
|
|
|
32 |
10 |
p. 3215-3216
|
artikel
|
| 20 |
Immune responses to cells and proteins after hematopoietic stem cell gene therapy for inherited diseases: A cause for concern
|
Jeffreys, Nathan
|
|
|
32 |
10 |
p. 3201-3202
|
artikel
|
| 21 |
Immunosuppressant therapy averts rejection of allogeneic FKBP1A-disrupted CAR-T cells
|
Maldini, Colby R.
|
|
|
32 |
10 |
p. 3485-3503
|
artikel
|
| 22 |
Inhibiting the inhibitors at the cellular level
|
Scott, David W.
|
|
|
32 |
10 |
p. 3203
|
artikel
|
| 23 |
Integrative proteomic and metabolomic elucidation of cardiomyopathy with in vivo and in vitro models and clinical samples
|
Hu, Yiwei
|
|
|
32 |
10 |
p. 3288-3312
|
artikel
|
| 24 |
In This Issue
|
|
|
|
32 |
10 |
p. 3196
|
artikel
|
| 25 |
Intrinsic ADRB2 inhibition improves CAR-T cell therapy efficacy against prostate cancer
|
Ajmal, Iqra
|
|
|
32 |
10 |
p. 3539-3557
|
artikel
|
| 26 |
Novel OX40 and 4-1BB derived spacers enhance CD30 CAR activity and safety in CD30 positive lymphoma models
|
Kua, Lindsay
|
|
|
32 |
10 |
p. 3504-3521
|
artikel
|
| 27 |
Preclinical studies of gene replacement therapy for CDKL5 deficiency disorder
|
Voronin, Gregory
|
|
|
32 |
10 |
p. 3331-3345
|
artikel
|
| 28 |
Rational design of self-amplifying virus-like vesicles with Ebola virus glycoprotein as vaccines
|
Zhang, Hong-Qing
|
|
|
32 |
10 |
p. 3695-3711
|
artikel
|
| 29 |
Reduction of circulating IgE and allergens by a pH-sensitive antibody with enhanced FcγRIIb binding
|
Li, Na
|
|
|
32 |
10 |
p. 3729-3742
|
artikel
|
| 30 |
Secondary failure of lentiviral vector gene therapy in a cerebral adrenoleukodystrophy patient with an ABCD1 whole-gene deletion
|
Lund, Troy C.
|
|
|
32 |
10 |
p. 3313-3317
|
artikel
|
| 31 |
Sirens and sphingolipids: What lures hematopoietic stem cells to the nervous system?
|
Li, Yedda
|
|
|
32 |
10 |
p. 3199-3200
|
artikel
|
| 32 |
Sleeping Beauty mRNA-LNP enables stable rAAV transgene expression in mouse and NHP hepatocytes and improves vector potency
|
Zakas, Philip M.
|
|
|
32 |
10 |
p. 3356-3371
|
artikel
|
| 33 |
Small-molecule-based targeted therapy in liver cancer
|
Ming, Yue
|
|
|
32 |
10 |
p. 3260-3287
|
artikel
|
| 34 |
Specific targeting of cancer vaccines to antigen-presenting cells via an endogenous TLR2/6 ligand derived from cysteinyl-tRNA synthetase 1
|
Kim, Hyeong Yun
|
|
|
32 |
10 |
p. 3597-3617
|
artikel
|
| 35 |
Synergic activity of FGFR2 and MEK inhibitors in the treatment of FGFR2-amplified cancers of unknown primary
|
Cavazzoni, Andrea
|
|
|
32 |
10 |
p. 3650-3668
|
artikel
|
| 36 |
Targeted, safe, and efficient gene delivery to human hematopoietic stem and progenitor cells in vivo using the engineered AVID adenovirus vector platform
|
Yao, Jia
|
|
|
32 |
10 |
p. 3743-3745
|
artikel
|
| 37 |
T-cell specific in vivo gene delivery with DART-AAVs targeted to CD8
|
Demircan, Muhammed Burak
|
|
|
32 |
10 |
p. 3470-3484
|
artikel
|
| 38 |
The ARDS microenvironment enhances MSC-induced repair via VEGF in experimental acute lung inflammation
|
Tunstead, Courteney
|
|
|
32 |
10 |
p. 3422-3432
|
artikel
|
| 39 |
The best of both worlds: AAV-mediated gene transfer empowered by LNP delivery of Sleeping Beauty transposase for durable transgene expression in vivo
|
Sandoval-Villegas, Nicolás
|
|
|
32 |
10 |
p. 3211-3214
|
artikel
|
| 40 |
Toward life without sickle cell disease
|
Davé, Utpal P.
|
|
|
32 |
10 |
p. 3197-3198
|
artikel
|
| 41 |
Tumor-intrinsic CDC42BPB confers resistance to anti-PD-1 immune checkpoint blockade in breast cancer
|
Deshpande, Ravindra Pramod
|
|
|
32 |
10 |
p. 3669-3682
|
artikel
|
| 42 |
Tumor-intrinsic kinase: A promising target for overcoming resistance to immune checkpoint blockade therapies
|
Wang, Jianhui
|
|
|
32 |
10 |
p. 3209-3210
|
artikel
|
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