| nr |
titel |
auteur |
tijdschrift |
jaar |
jaarg. |
afl. |
pagina('s) |
type |
| 1 |
A complex microRNA regulatory network may control the HCP5/UTP3/c-Myc/VAMP3 signaling axis
|
Cristóbal, Ion
|
|
|
31 |
4 |
p. 922-923
|
artikel
|
| 2 |
Advances in gene therapy hold promise for treating hereditary hearing loss
|
Jiang, Luoying
|
|
|
31 |
4 |
p. 934-950
|
artikel
|
| 3 |
Adverse event reporting to US Food and Drug Administration and risk evaluation and mitigation strategies
|
Thompson, Deborah L.
|
|
|
31 |
4 |
p. 918
|
artikel
|
| 4 |
A luciferase reporter mouse model to optimize in vivo gene editing validated by lipid nanoparticle delivery of adenine base editors
|
Yu, Si-Yue
|
|
|
31 |
4 |
p. 1159-1166
|
artikel
|
| 5 |
Analyzing clinical observations to better understand and manage immune responses to AAV gene therapies
|
Chan, Ying Kai
|
|
|
31 |
4 |
p. 913-914
|
artikel
|
| 6 |
An optimized IgG-based B7-H3xCD3 bispecific antibody for treatment of gastrointestinal cancers
|
Zekri, Latifa
|
|
|
31 |
4 |
p. 1033-1045
|
artikel
|
| 7 |
Comparative analysis of CRISPR off-target discovery tools following ex vivo editing of CD34+ hematopoietic stem and progenitor cells
|
Cromer, M. Kyle
|
|
|
31 |
4 |
p. 1074-1087
|
artikel
|
| 8 |
3D genome alterations and editing in pathology
|
Tiukacheva, Eugenia A.
|
|
|
31 |
4 |
p. 924-933
|
artikel
|
| 9 |
Evaluation of repRNA vaccine for induction and in utero transfer of maternal antibodies in a pregnant rabbit model
|
Khandhar, Amit P.
|
|
|
31 |
4 |
p. 1046-1058
|
artikel
|
| 10 |
Fasudil alleviates the vascular endothelial dysfunction and several phenotypes of Fabry disease
|
Choi, Jong Bin
|
|
|
31 |
4 |
p. 1002-1016
|
artikel
|
| 11 |
Genome editing with natural and engineered CjCas9 orthologs
|
Gao, Siqi
|
|
|
31 |
4 |
p. 1177-1187
|
artikel
|
| 12 |
Gut microbial metabolite hyodeoxycholic acid targets the TLR4/MD2 complex to attenuate inflammation and protect against sepsis
|
Li, Jiaxin
|
|
|
31 |
4 |
p. 1017-1032
|
artikel
|
| 13 |
Immunomodulatory effect of locoregional therapy in the tumor microenvironment
|
Xie, Lin
|
|
|
31 |
4 |
p. 951-969
|
artikel
|
| 14 |
In this issue
|
|
|
|
31 |
4 |
p. 917
|
artikel
|
| 15 |
Long-term reversal of chronic pain behavior in rodents through elevation of spinal agmatine
|
Peterson, Cristina D.
|
|
|
31 |
4 |
p. 1123-1135
|
artikel
|
| 16 |
Obtaining the best igRNAs for bystander-less correction of all ABE-reversible pathogenic SNVs using high-throughput screening
|
Li, Bo
|
|
|
31 |
4 |
p. 1167-1176
|
artikel
|
| 17 |
Potential clinical use of azacitidine and MEK inhibitor combination therapy in PTPN11-mutated juvenile myelomonocytic leukemia
|
Pasupuleti, Santhosh Kumar
|
|
|
31 |
4 |
p. 986-1001
|
artikel
|
| 18 |
Preferential delivery of lipid-ligand conjugated DNA/RNA heteroduplex oligonucleotide to ischemic brain in hyperacute stage
|
Li, Fuying
|
|
|
31 |
4 |
p. 1106-1122
|
artikel
|
| 19 |
Protein expression/secretion boost by a novel unique 21-mer cis-regulatory motif (Exin21) via mRNA stabilization
|
Zhu, Yuanjun
|
|
|
31 |
4 |
p. 1136-1158
|
artikel
|
| 20 |
Stable HIV decoy receptor expression after in vivo HSC transduction in mice and NHPs: Safety and efficacy in protection from SHIV
|
Li, Chang
|
|
|
31 |
4 |
p. 1059-1073
|
artikel
|
| 21 |
Stable HIV decoy receptor expression after in vivo HSC transduction in mice and NHPs: Safety and efficacy in protection from SHIV
|
Li, Chang
|
|
|
31 |
4 |
p. 1188
|
artikel
|
| 22 |
The power of 2,6-diaminopurine in correcting UGA nonsense codons in CFTR mRNA
|
Romão, Luísa
|
|
|
31 |
4 |
p. 921-922
|
artikel
|
| 23 |
Transcriptional reprogramming restores UBE3A brain-wide and rescues behavioral phenotypes in an Angelman syndrome mouse model
|
O’Geen, Henriette
|
|
|
31 |
4 |
p. 1088-1105
|
artikel
|
| 24 |
Two gene therapies for hemophilia available: Now what?
|
Pierce, Glenn F.
|
|
|
31 |
4 |
p. 919-920
|
artikel
|
| 25 |
Use of 2,6-diaminopurine as a potent suppressor of UGA premature stop codons in cystic fibrosis
|
Leroy, Catherine
|
|
|
31 |
4 |
p. 970-985
|
artikel
|
| 26 |
Vaccinations in pregnancy against TORCH pathogens
|
Beharier, Ofer
|
|
|
31 |
4 |
p. 915-916
|
artikel
|
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