| nr |
titel |
auteur |
tijdschrift |
jaar |
jaarg. |
afl. |
pagina('s) |
type |
| 1 |
AAV capsid engineering identified two novel variants with improved in vivo tropism for cardiomyocytes
|
Rode, Laura
|
|
|
30 |
12 |
p. 3601-3618
|
artikel
|
| 2 |
AAV vectors: The Rubik’s cube of human gene therapy
|
Pupo, Amaury
|
|
|
30 |
12 |
p. 3515-3541
|
artikel
|
| 3 |
An armed oncolytic virus enhances the efficacy of tumor-infiltrating lymphocyte therapy by converting tumors to artificial antigen-presenting cells in situ
|
Ye, Kai
|
|
|
30 |
12 |
p. 3658-3676
|
artikel
|
| 4 |
CRISPR base editing of cis-regulatory elements enables the perturbation of neurodegeneration-linked genes
|
Lim, Colin K.W.
|
|
|
30 |
12 |
p. 3619-3631
|
artikel
|
| 5 |
Ectopic clotting factor VIII expression and misfolding in hepatocytes as a cause for hepatocellular carcinoma
|
Kapelanski-Lamoureux, Audrey
|
|
|
30 |
12 |
p. 3542-3551
|
artikel
|
| 6 |
First-in-human in vivo genome editing via AAV-zinc-finger nucleases for mucopolysaccharidosis I/II and hemophilia B
|
Harmatz, Paul
|
|
|
30 |
12 |
p. 3587-3600
|
artikel
|
| 7 |
From amputations to antibiotics: A future beyond “hacksaw” gene editing
|
Scott, Tristan
|
|
|
30 |
12 |
p. 3505-3506
|
artikel
|
| 8 |
Hemophilia “A” gene therapy: Lost in translation
|
VandenDriessche, Thierry
|
|
|
30 |
12 |
p. 3508-3509
|
artikel
|
| 9 |
IL-15 blockade and rapamycin rescue multifactorial loss of factor VIII from AAV-transduced hepatocytes in hemophilia A mice
|
Butterfield, John S.S.
|
|
|
30 |
12 |
p. 3552-3569
|
artikel
|
| 10 |
In this issue
|
|
|
|
30 |
12 |
p. 3507
|
artikel
|
| 11 |
Long-term safety of MRI-guided administration of AAV2-GDNF and gadoteridol in the putamen of individuals with Parkinson’s disease
|
Rocco, Matthew T.
|
|
|
30 |
12 |
p. 3632-3638
|
artikel
|
| 12 |
mmu-lncRNA 121686/hsa-lncRNA 520657 induced by METTL3 drive the progression of AKI by targeting miR-328-5p/HtrA3 signaling axis
|
Pan, Jian
|
|
|
30 |
12 |
p. 3694-3713
|
artikel
|
| 13 |
Modular capsid decoration boosts adenovirus vaccine-induced humoral immunity against SARS-CoV-2
|
Dicks, Matthew D.J.
|
|
|
30 |
12 |
p. 3639-3657
|
artikel
|
| 14 |
Overcoming resistance to oncolytic virus M1 by targeting PI3K-γ in tumor-associated myeloid cells
|
Liu, Yang
|
|
|
30 |
12 |
p. 3677-3693
|
artikel
|
| 15 |
Secondary hemophagocytic lymphohistiocytosis following Zolgensma therapy: An evolving story on the innate response to systemic gene therapy
|
Byrne, Barry J.
|
|
|
30 |
12 |
p. 3503-3504
|
artikel
|
| 16 |
The m6A methyltransferase Mettl3 deficiency attenuates hepatic stellate cell activation and liver fibrosis
|
Li, Yanli
|
|
|
30 |
12 |
p. 3714-3728
|
artikel
|
| 17 |
Transient expression of factor VIII and a chronic high-fat diet induces ER stress and late hepatocyte oncogenesis
|
Pierce, Glenn F.
|
|
|
30 |
12 |
p. 3510-3512
|
artikel
|
| 18 |
Tuning neurodegeneration-linked gene expression, one (edited) base at a time
|
Guerra-Resendez, Rosa Selenia
|
|
|
30 |
12 |
p. 3512-3514
|
artikel
|
| 19 |
Vector genome loss and epigenetic modifications mediate decline in transgene expression of AAV5 vectors produced in mammalian and insect cells
|
Handyside, Britta
|
|
|
30 |
12 |
p. 3570-3586
|
artikel
|
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