| nr |
titel |
auteur |
tijdschrift |
jaar |
jaarg. |
afl. |
pagina('s) |
type |
| 1 |
AAV9-Mediated Expression of SMN Restricted to Neurons Does Not Rescue the Spinal Muscular Atrophy Phenotype in Mice
|
Besse, Aurore
|
|
|
28 |
8 |
p. 1887-1901
|
artikel
|
| 2 |
Antibacterial Fusion Protein BPI21/LL-37 Modification Enhances the Therapeutic Efficacy of hUC-MSCs in Sepsis
|
Li, Zhan
|
|
|
28 |
8 |
p. 1806-1817
|
artikel
|
| 3 |
A Single Dose of NILV-Based Vaccine Provides Rapid and Durable Protection against Zika Virus
|
Ku, Min Wen
|
|
|
28 |
8 |
p. 1772-1782
|
artikel
|
| 4 |
Broader Implications of Progressive Liver Dysfunction and Lethal Sepsis in Two Boys following Systemic High-Dose AAV
|
Morales, Leon
|
|
|
28 |
8 |
p. 1753-1755
|
artikel
|
| 5 |
Call for Papers: Expanding the Scale and Scope of Therapeutic Gene Editing
|
Kiem, Hans-Peter
|
|
|
28 |
8 |
p. 1743
|
artikel
|
| 6 |
Delivery of Oligonucleotides to the Liver with GalNAc: From Research to Registered Therapeutic Drug
|
Debacker, Alexandre J.
|
|
|
28 |
8 |
p. 1759-1771
|
artikel
|
| 7 |
Efficient Nuclease-Directed Integration of Lentivirus Vectors into the Human Ribosomal DNA Locus
|
Schenkwein, Diana
|
|
|
28 |
8 |
p. 1858-1875
|
artikel
|
| 8 |
Enhanced Efficacy of Combination of Gemcitabine and Phosphatidylserine-Targeted Nanovesicles against Pancreatic Cancer
|
N’Guessan, Kombo F.
|
|
|
28 |
8 |
p. 1876-1886
|
artikel
|
| 9 |
Exposed CendR Domain in Homing Peptide Yields Skin-Targeted Therapeutic in Epidermolysis Bullosa
|
Pemmari, Toini
|
|
|
28 |
8 |
p. 1833-1845
|
artikel
|
| 10 |
Family Highlights
|
|
|
|
28 |
8 |
p. 1746
|
artikel
|
| 11 |
Growing Impact and Growing Submissions
|
Frederickson, Robert M.
|
|
|
28 |
8 |
p. 1744
|
artikel
|
| 12 |
In Situ Gene Therapy via AAV-CRISPR-Cas9-Mediated Targeted Gene Regulation
|
Moreno, Ana M.
|
|
|
28 |
8 |
p. 1931
|
artikel
|
| 13 |
In This Issue
|
|
|
|
28 |
8 |
p. 1745
|
artikel
|
| 14 |
In Vivo Generation of CAR T Cells Selectively in Human CD4+ Lymphocytes
|
Agarwal, Shiwani
|
|
|
28 |
8 |
p. 1783-1794
|
artikel
|
| 15 |
Lentiviral-Vector-Based Dendritic Cell Vaccine Synergizes with Checkpoint Blockade to Clear Chronic Viral Infection
|
Norton, Thomas D.
|
|
|
28 |
8 |
p. 1795-1805
|
artikel
|
| 16 |
Ligand-Induced Degradation of a CAR Permits Reversible Remote Control of CAR T Cell Activity In Vitro and In Vivo
|
Richman, Sarah A.
|
|
|
28 |
8 |
p. 1932
|
artikel
|
| 17 |
Mutation-Independent Allele-Specific Editing by CRISPR-Cas9, a Novel Approach to Treat Autosomal Dominant Disease
|
Christie, Kathleen A.
|
|
|
28 |
8 |
p. 1846-1857
|
artikel
|
| 18 |
Neutralizing the Neutralizers in AAV Gene Therapy
|
Herzog, Roland W.
|
|
|
28 |
8 |
p. 1741-1742
|
artikel
|
| 19 |
One Two Punch: Combination Chemotherapy Knocks Out Pancreatic Cancer
|
Lumeau, Audrey
|
|
|
28 |
8 |
p. 1751-1752
|
artikel
|
| 20 |
Opa1 Overexpression Protects from Early-Onset Mpv17 −/−-Related Mouse Kidney Disease
|
Luna-Sanchez, Marta
|
|
|
28 |
8 |
p. 1918-1930
|
artikel
|
| 21 |
Perivascular Stem Cell-Derived Cyclophilin A Improves Uterine Environment with Asherman’s Syndrome via HIF1α-Dependent Angiogenesis
|
Park, Mira
|
|
|
28 |
8 |
p. 1818-1832
|
artikel
|
| 22 |
Quantification of CpG Motifs in rAAV Genomes: Avoiding the Toll
|
Wright, J. Fraser
|
|
|
28 |
8 |
p. 1756-1758
|
artikel
|
| 23 |
Redecorating the Mitochondrial Inner Membrane: A Treatment for mtDNA Disorders
|
Chrzanowska-Lightowlers, Zofia M.A.
|
|
|
28 |
8 |
p. 1749-1751
|
artikel
|
| 24 |
Research Highlights
|
|
|
|
28 |
8 |
p. 1747-1748
|
artikel
|
| 25 |
Upregulating Lin28a Promotes Axon Regeneration in Adult Mice with Optic Nerve and Spinal Cord Injury
|
Nathan, Fatima M.
|
|
|
28 |
8 |
p. 1902-1917
|
artikel
|
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