| no |
title |
author |
magazine |
year |
volume |
issue |
page(s) |
type |
| 1 |
AAV-CRISPR Persistence in the Eye of the Beholder
|
Recchia, Alessandra
|
|
|
27 |
1 |
p. 12-14
|
article
|
| 2 |
Addgene: Molecular Therapy Interview with Melina Fan and Karen Guerin
|
Vandenberghe, Luk H.
|
|
|
27 |
1 |
p. 6-9
|
article
|
| 3 |
A Potent Tumor-Reactive p53-Specific Single-Chain TCR without On- or Off-Target Autoimmunity In Vivo
|
Echchannaoui, Hakim
|
|
|
27 |
1 |
p. 261-271
|
article
|
| 4 |
A Stem Cell-Based Screening Platform Identifies Compounds that Desensitize Motor Neurons to Endoplasmic Reticulum Stress
|
Thams, Sebastian
|
|
|
27 |
1 |
p. 87-101
|
article
|
| 5 |
Bioselection Reveals miR-99b and miR-485 as Enhancers of Adenoviral Oncolysis in Pancreatic Cancer
|
Rovira-Rigau, Maria
|
|
|
27 |
1 |
p. 230-243
|
article
|
| 6 |
CD7 CAR T Cells for the Therapy of Acute Myeloid Leukemia
|
Gomes-Silva, Diogo
|
|
|
27 |
1 |
p. 272-280
|
article
|
| 7 |
Development of Novel DNA-Encoded PCSK9 Monoclonal Antibodies as Lipid-Lowering Therapeutics
|
Khoshnejad, Makan
|
|
|
27 |
1 |
p. 188-199
|
article
|
| 8 |
Discovery of New Fusion Transcripts in a Cohort of Pediatric Solid Cancers at Relapse and Relevance for Personalized Medicine
|
Dupain, Célia
|
|
|
27 |
1 |
p. 200-218
|
article
|
| 9 |
Efficacy of Multi-exon Skipping Treatment in Duchenne Muscular Dystrophy Dog Model Neonates
|
Lim, Kenji Rowel Q.
|
|
|
27 |
1 |
p. 76-86
|
article
|
| 10 |
Gesicle-Mediated Delivery of CRISPR/Cas9 Ribonucleoprotein Complex for Inactivating the HIV Provirus
|
Campbell, Lee A.
|
|
|
27 |
1 |
p. 151-163
|
article
|
| 11 |
IGF1 Treatment Improves Cardiac Remodeling after Infarction by Targeting Myeloid Cells
|
Heinen, Andre
|
|
|
27 |
1 |
p. 46-58
|
article
|
| 12 |
In This Issue
|
|
|
|
27 |
1 |
p. 3
|
article
|
| 13 |
In Vivo PET Tracking of 89Zr-Labeled Vγ9Vδ2 T Cells to Mouse Xenograft Breast Tumors Activated with Liposomal Alendronate
|
Man, Francis
|
|
|
27 |
1 |
p. 219-229
|
article
|
| 14 |
Keeping the Heart Fitm2 during Chemotherapy
|
Eding, Joep E.C.
|
|
|
27 |
1 |
p. 10-12
|
article
|
| 15 |
Long Non-coding RNA ECRAR Triggers Post-natal Myocardial Regeneration by Activating ERK1/2 Signaling
|
Chen, Yanmei
|
|
|
27 |
1 |
p. 29-45
|
article
|
| 16 |
Long-Term Effects of In Vivo Genome Editing in the Mouse Retina Using Campylobacter jejuni Cas9 Expressed via Adeno-Associated Virus
|
Jo, Dong Hyun
|
|
|
27 |
1 |
p. 130-136
|
article
|
| 17 |
Long-Term Persistence of Anti-HIV Broadly Neutralizing Antibody-Secreting Hematopoietic Cells in Humanized Mice
|
Kuhlmann, Anne-Sophie
|
|
|
27 |
1 |
p. 164-177
|
article
|
| 18 |
miR-212/132 Cluster Modulation Prevents Doxorubicin-Mediated Atrophy and Cardiotoxicity
|
Gupta, Shashi Kumar
|
|
|
27 |
1 |
p. 17-28
|
article
|
| 19 |
Modulating the Tumor Microenvironment via Oncolytic Viruses and CSF-1R Inhibition Synergistically Enhances Anti-PD-1 Immunotherapy
|
Shi, Gang
|
|
|
27 |
1 |
p. 244-260
|
article
|
| 20 |
Non-viral, Tumor-free Induction of Transient Cell Reprogramming in Mouse Skeletal Muscle to Enhance Tissue Regeneration
|
de Lázaro, Irene
|
|
|
27 |
1 |
p. 59-75
|
article
|
| 21 |
Optimization of CRISPR/Cas9 Delivery to Human Hematopoietic Stem and Progenitor Cells for Therapeutic Genomic Rearrangements
|
Lattanzi, Annalisa
|
|
|
27 |
1 |
p. 137-150
|
article
|
| 22 |
Preclinical Evaluation of ADVM-022, a Novel Gene Therapy Approach to Treating Wet Age-Related Macular Degeneration
|
Grishanin, Ruslan
|
|
|
27 |
1 |
p. 118-129
|
article
|
| 23 |
Promoting Axon Regeneration in Adult CNS by Targeting Liver Kinase B1
|
Ohtake, Yosuke
|
|
|
27 |
1 |
p. 102-117
|
article
|
| 24 |
Research Highlights
|
|
|
|
27 |
1 |
p. 4-5
|
article
|
| 25 |
The Bumpy Road to CAR Activation
|
Janelle, Valérie
|
|
|
27 |
1 |
p. 14-16
|
article
|
| 26 |
Two Decades of Molecular Therapy: The Journey Continues
|
Frederickson, Robert M.
|
|
|
27 |
1 |
p. 1-2
|
article
|
| 27 |
ZFN-Mediated In Vivo Genome Editing Corrects Murine Hurler Syndrome
|
Ou, Li
|
|
|
27 |
1 |
p. 178-187
|
article
|
Journal description