| nr |
titel |
auteur |
tijdschrift |
jaar |
jaarg. |
afl. |
pagina('s) |
type |
| 1 |
AAV1.NT-3 Gene Therapy for Charcot–Marie–Tooth Neuropathy
|
Sahenk, Zarife
|
|
2014
|
22 |
3 |
p. 511-521
11 p.
|
artikel
|
| 2 |
Adeno-associated Virus–mediated Delivery of a Recombinant Single-chain Antibody Against Misfolded Superoxide Dismutase for Treatment of Amyotrophic Lateral Sclerosis
|
Patel, Priyanka
|
|
2014
|
22 |
3 |
p. 498-510
13 p.
|
artikel
|
| 3 |
A Hitchhiker's Guide to the Blood–brain Barrier: In Trans Delivery of a Therapeutic Enzyme
|
Sands, Mark S
|
|
2014
|
22 |
3 |
p. 483-484
2 p.
|
artikel
|
| 4 |
Broad Therapeutic Benefit After RNAi Expression Vector Delivery to Deep Cerebellar Nuclei: Implications for Spinocerebellar Ataxia Type 1 Therapy
|
Keiser, Megan S
|
|
2014
|
22 |
3 |
p. 588-595
8 p.
|
artikel
|
| 5 |
CARs Move To the Fast Lane
|
Davila, Marco L
|
|
2014
|
22 |
3 |
p. 477-478
2 p.
|
artikel
|
| 6 |
Chondrogenic Differentiation Increases Antidonor Immune Response to Allogeneic Mesenchymal Stem Cell Transplantation
|
Ryan, Aideen E
|
|
2014
|
22 |
3 |
p. 655-667
13 p.
|
artikel
|
| 7 |
Clinical Assessment of a Novel Recombinant Simian Adenovirus ChAdOx1 as a Vectored Vaccine Expressing Conserved Influenza A Antigens
|
Antrobus, Richard D
|
|
2014
|
22 |
3 |
p. 668-674
7 p.
|
artikel
|
| 8 |
Design of a Novel Integration-deficient Lentivector Technology That Incorporates Genetic and Posttranslational Elements to Target Human Dendritic Cells
|
Tareen, Semih U
|
|
2014
|
22 |
3 |
p. 575-587
13 p.
|
artikel
|
| 9 |
Development of a Web Course on Gene Therapy by the International Consortium of Gene Therapy
|
Tremblay, Jacques P
|
|
2014
|
22 |
3 |
p. 482-
1 p.
|
artikel
|
| 10 |
Effective Intravenous Therapy for Neurodegenerative Disease With a Therapeutic Enzyme and a Peptide That Mediates Delivery to the Brain
|
Meng, Yu
|
|
2014
|
22 |
3 |
p. 547-553
7 p.
|
artikel
|
| 11 |
From Gut to Brain: Bioencapsulated Therapeutic Protein Reduces Amyloid Load Upon Oral Delivery
|
Mäger, Imre
|
|
2014
|
22 |
3 |
p. 485-486
2 p.
|
artikel
|
| 12 |
Immunological and Antiviral Responses After Therapeutic DNA Immunization in Chronic Hepatitis B Patients Efficiently Treated by Analogues
|
Godon, O
|
|
2014
|
22 |
3 |
p. 675-684
10 p.
|
artikel
|
| 13 |
Integration-deficient Lentiviral Vectors Expressing Codon-optimized R338L Human FIX Restore Normal Hemostasis in Hemophilia B Mice
|
Suwanmanee, Thipparat
|
|
2014
|
22 |
3 |
p. 567-574
8 p.
|
artikel
|
| 14 |
In This Issue
|
|
|
2014
|
22 |
3 |
p. 480-
1 p.
|
artikel
|
| 15 |
In Vivo Proof of Concept of Adoptive Immunotherapy for Hepatocellular Carcinoma Using Allogeneic Suicide Gene-modified Killer Cells
|
Leboeuf, Céline
|
|
2014
|
22 |
3 |
p. 634-644
11 p.
|
artikel
|
| 16 |
Kinetics of Tumor Destruction by Chimeric Antigen Receptor-modified T Cells
|
Anurathapan, Usanarat
|
|
2014
|
22 |
3 |
p. 623-633
11 p.
|
artikel
|
| 17 |
Long-distance Axonal Transport of AAV9 Is Driven by Dynein and Kinesin-2 and Is Trafficked in a Highly Motile Rab7-positive Compartment
|
Castle, Michael J
|
|
2014
|
22 |
3 |
p. 554-566
13 p.
|
artikel
|
| 18 |
Oral Delivery of Bioencapsulated Proteins Across Blood–Brain and Blood–Retinal Barriers
|
Kohli, Neha
|
|
2014
|
22 |
3 |
p. 535-546
12 p.
|
artikel
|
| 19 |
Parkinson's Disease Gene Therapy: Success by Design Meets Failure by Efficacy
|
Bartus, Raymond T
|
|
2014
|
22 |
3 |
p. 487-497
11 p.
|
artikel
|
| 20 |
Preclinical Demonstration of Lentiviral Vector-mediated Correction of Immunological and Metabolic Abnormalities in Models of Adenosine Deaminase Deficiency
|
Carbonaro, Denise A
|
|
2014
|
22 |
3 |
p. 607-622
16 p.
|
artikel
|
| 21 |
Research Highlights
|
|
|
2014
|
22 |
3 |
p. 481-
1 p.
|
artikel
|
| 22 |
Targeted Drug Delivery to Intestinal Macrophages by Bioactive Nanovesicles Released from Grapefruit
|
Wang, Baomei
|
|
2014
|
22 |
3 |
p. 522-534
13 p.
|
artikel
|
| 23 |
The Impact of Unprotected T Cells in RNAi-based Gene Therapy for HIV-AIDS
|
Herrera-Carrillo, Elena
|
|
2014
|
22 |
3 |
p. 596-606
11 p.
|
artikel
|
| 24 |
Therapeutic Potential of Genetically Modified Mesenchymal Stem Cells After Neonatal Hypoxic-Ischemic Brain Damage
|
van Velthoven, Cindy TJ
|
|
2014
|
22 |
3 |
p. 645-654
10 p.
|
artikel
|
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