| no |
title |
author |
magazine |
year |
volume |
issue |
page(s) |
type |
| 1 |
Adeno-associated Virus 9 Mediated FKRP Gene Therapy Restores Functional Glycosylation of α-dystroglycan and Improves Muscle Functions
|
Xu, Lei
|
|
2013
|
21 |
10 |
p. 1832-1840
9 p.
|
article
|
| 2 |
Adeno-associated Virus-mediated Rescue of Neonatal Lethality in Argininosuccinate Synthetase-deficient Mice
|
Kok, Cindy Y
|
|
2013
|
21 |
10 |
p. 1823-1831
9 p.
|
article
|
| 3 |
Amalgamating Oncolytic Viruses to Enhance Their Safety, Consolidate Their Killing Mechanisms, and Accelerate Their Spread
|
Ayala-Breton, Camilo
|
|
2013
|
21 |
10 |
p. 1930-1937
8 p.
|
article
|
| 4 |
Corrigendum to “Topical Application of Recombinant Type VII Collagen Incorporates Into the Dermal–Epidermal Junction and Promotes Wound Closure”
|
|
|
2013
|
21 |
10 |
p. 1969-
1 p.
|
article
|
| 5 |
DLK1: A Novel Target for Immunotherapeutic Remodeling of the Tumor Blood Vasculature
|
Chi Sabins, Nina
|
|
2013
|
21 |
10 |
p. 1958-1968
11 p.
|
article
|
| 6 |
Dose-dependent Neuroprotection of VEGF165 in Huntington's Disease Striatum
|
Ellison, Stuart M
|
|
2013
|
21 |
10 |
p. 1862-1875
14 p.
|
article
|
| 7 |
Hydrodynamic Delivery of mIL10 Gene Protects Mice From High-fat Diet-induced Obesity and Glucose Intolerance
|
Gao, Mingming
|
|
2013
|
21 |
10 |
p. 1852-1861
10 p.
|
article
|
| 8 |
Inactivation of Hepatitis B Virus Replication in Cultured Cells and In Vivo with Engineered Transcription Activator-Like Effector Nucleases
|
Bloom, Kristie
|
|
2013
|
21 |
10 |
p. 1889-1897
9 p.
|
article
|
| 9 |
In This Issue
|
|
|
2013
|
21 |
10 |
p. 1808-
1 p.
|
article
|
| 10 |
Intravenous Delivery of siRNA Targeting CD47 Effectively Inhibits Melanoma Tumor Growth and Lung Metastasis
|
Wang, Yuhua
|
|
2013
|
21 |
10 |
p. 1919-1929
11 p.
|
article
|
| 11 |
Myeloid/Microglial Driven Autologous Hematopoietic Stem Cell Gene Therapy Corrects a Neuronopathic Lysosomal Disease
|
Sergijenko, Ana
|
|
2013
|
21 |
10 |
p. 1938-1949
12 p.
|
article
|
| 12 |
NADH-dehydrogenase Type-2 Suppresses Irreversible Visual Loss and Neurodegeneration in the EAE Animal Model of MS
|
Talla, Venu
|
|
2013
|
21 |
10 |
p. 1876-1888
13 p.
|
article
|
| 13 |
On the Mechanism and Benefit of siRNA-mediated Targeting of CD47 in Cancer
|
Zhao, Xiwen
|
|
2013
|
21 |
10 |
p. 1811-
1 p.
|
article
|
| 14 |
Panorama From the Oncolytic Virotherapy Summit
|
Pol, Jonathan G
|
|
2013
|
21 |
10 |
p. 1814-1818
5 p.
|
article
|
| 15 |
Removing the Immune Response From Muscular Dystrophy Research
|
Chamberlain, Jeffrey S
|
|
2013
|
21 |
10 |
p. 1821-1822
2 p.
|
article
|
| 16 |
Reply to “On the Mechanism and Benefit of siRNA-mediated Targeting of CD47 in Cancer”
|
Wang, Yuhua
|
|
2013
|
21 |
10 |
p. 1812-1813
2 p.
|
article
|
| 17 |
Research Highlights
|
|
|
2013
|
21 |
10 |
p. 1809-
1 p.
|
article
|
| 18 |
Silencing Mutant ATXN3 Expression Resolves Molecular Phenotypes in SCA3 Transgenic Mice
|
Rodríguez-Lebrón, Edgardo
|
|
2013
|
21 |
10 |
p. 1909-1918
10 p.
|
article
|
| 19 |
Sonia Skarlatos: A Colleague and a Shepherd of Gene Therapy
|
|
|
2013
|
21 |
10 |
p. 1807-
1 p.
|
article
|
| 20 |
TALENs Targeting HBV: Designer Endonuclease Therapies for Viral Infections
|
Weber, Nicholas D
|
|
2013
|
21 |
10 |
p. 1819-1821
3 p.
|
article
|
| 21 |
The Rag2 – Il2rb – Dmd – Mouse: a Novel Dystrophic and Immunodeficient Model to Assess Innovating Therapeutic Strategies for Muscular Dystrophies
|
Vallese, Denis
|
|
2013
|
21 |
10 |
p. 1950-1957
8 p.
|
article
|
| 22 |
Toward RNAi Therapy for the Polyglutamine Disease Machado–Joseph Disease
|
do Carmo Costa, Maria
|
|
2013
|
21 |
10 |
p. 1898-1908
11 p.
|
article
|
| 23 |
Transcriptional Profiling of Hmgb1-Induced Myocardial Repair Identifies a Key Role for Notch Signaling
|
Limana, Federica
|
|
2013
|
21 |
10 |
p. 1841-1851
11 p.
|
article
|
Journal description