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nr titel auteur tijdschrift jaar jaarg. afl. pagina('s) type
1 317. AAV Based Gene Therapy Rescues the Murine Cardiac Phenotype Associated with Friedreich's Ataxia 2012
 20 S1 p. S125-
1 p.
 artikel
2 251. AAV Capsid Antigen Cross-Presentation Is Dependent on Proteasomal Degradation and Nuclear Virion Uncoating 2012
 20 S1 p. S99-
1 p.
 artikel
3 72. AAV2/2-CBA-REP1 Vector with WPRE Provides Functional Expression of the Transgene in Choroideremia Mouse Knock-Out and Patient Cells 2012
 20 S1 p. S30-
1 p.
 artikel
4 491. AAV Delivery to the Nasopharynx for Pharmacologically-Regulated Systemic Expression of Therapeutic Proteins 2012
 20 S1 p. S190-
1 p.
 artikel
5 111. AAV6 Functional Endocytosis in Mouse Embryo Fibroblast Is Independent of Clathrin and Caveolin Mechanisms and Does Not Require EGFR Activation 2012
 20 S1 p. S46-
1 p.
 artikel
6 74. AAV Gene Therapy with Cholesterol 24-Hydroxylase for Alzheimer Disease: In Vivo Consequences on Amyloid and Tau Components of the Pathology 2012
 20 S1 p. S30-S31
2 p.
 artikel
7 334. AAV-Mediated CNS Gene Transfer of Bevacizumab Reduces Glioblastoma Growth and Increases Survival in Mice 2012
 20 S1 p. S131-S132
2 p.
 artikel
8 75. AAV8-Mediated Expression of VEGF Antagonist Ranibizumab in Macaque Eye: Comparison of Subretinal vs. Intravitreal Delivery of Vector 2012
 20 S1 p. S31-
1 p.
 artikel
9 162. AAV Mediated Gene Delivery Suppresses Inflammatory Response Associated with GM2 Gangliosidosis 2012
 20 S1 p. S65-
1 p.
 artikel
10 59. AAV-Mediated Gene Repair Is Significantly Enhanced by Transient Inhibition of NHEJ or the Proteasome In Vivo 2012
 20 S1 p. S24-S25
2 p.
 artikel
11 176. AAV-Mediated Gene Therapy in Limb-Girdle Muscular Dystrophy 2I (LGMD2I) Mouse Model 2012
 20 S1 p. S70-S71
2 p.
 artikel
12 434. AAV8-Mediated Gene Transfer to Cone and Rod Photoreceptors 2012
 20 S1 p. S169-
1 p.
 artikel
13 441. AAV Mediated RNAi and Antisense Knockdown of Intranuclear DMPK Transcripts in DM1 Cells 2012
 20 S1 p. S171-S172
2 p.
 artikel
14 388. AAV-Mediated Targeted Gene Addition in Patient-Specific SCID-X1 Induced Pluripotent Stem Cells 2012
 20 S1 p. S152-
1 p.
 artikel
15 185. AAV Micro-Dystrophin Therapy Alleviates Stress-Induced Cardiac Death but Does Not Reduce Myocardial Fibrosis in >21-m-Old mdx Mice 2012
 20 S1 p. S73-S74
2 p.
 artikel
16 36. AAV-MTM1 Prolongs Survival and Rescues Severe Muscle Weakness in Mouse and Canine Models of X-Linked Myotubular Myopathy 2012
 20 S1 p. S14-S15
2 p.
 artikel
17 228. AAV Vector and Transgene Modifications for Improved Efficacy in Hemophilia Gene Therapy with Continuous Expression of FVIIa 2012
 20 S1 p. S90-
1 p.
 artikel
18 252. AAV Vector-Mediated Systemic Delivery of Interleukin-10 Attenuates the Progression of Peritoneal Fibrosis in a Rat Model of Peritoneal Dialysis 2012
 20 S1 p. S99-S100
2 p.
 artikel
19 504. AAV Vectors for Tissue-Specific, Regulated Expression In Muscle 2012
 20 S1 p. S195-
1 p.
 artikel
20 555. AAV2(Y-F) Vector Substantially Reduces Targeting of Transduced Hepatocytes by Capsid-Specific CD8+ T Cells 2012
 20 S1 p. S215-
1 p.
 artikel
21 181. Abbreviated Dystrophins Restore the Passive Properties of the Extensor Digitorum Longus Muscle in Dystrophin-Null Mice 2012
 20 S1 p. S72-
1 p.
 artikel
22 45. Abrogation of EAE and Tolerance Induction of Naïve and Effector T Cells by Antigen Presenting Dendritic Cells 2012
 20 S1 p. S18-S19
2 p.
 artikel
23 525. Absence of Integration Hotspots in Non-Human Primates after Intravenous Injection of AAV2/5-AAT-coPBGD 2012
 20 S1 p. S202-S203
2 p.
 artikel
24 756. Absolute Determination of Single-Stranded and Self -Complementary AAV Vector Genome Titers by Digital PCR 2012
 20 S1 p. S291-
1 p.
 artikel
25 610. Abstract Withdrawn 2012
 20 S1 p. S235-
1 p.
 artikel
26 699. Abstract Withdrawn 2012
 20 S1 p. S270-
1 p.
 artikel
27 490. Abstract Withdrawn 2012
 20 S1 p. S190-
1 p.
 artikel
28 713. Abstract Withdrawn 2012
 20 S1 p. S275-
1 p.
 artikel
29 598. Abstract Withdrawn. 2012
 20 S1 p. S231-
1 p.
 artikel
30 3. Accessing the Unmappable Genome for Viral Integration Site Analysis 2012
 20 S1 p. S1-S2
2 p.
 artikel
31 349. A Cell-Based Assay To Detect Rare Psi-Gag Recombinants in Lentiviral Vector Preparations 2012
 20 S1 p. S137-
1 p.
 artikel
32 10. A Comprehensive Analysis of Structural and Functional Significance of the 381 Amino Acids in the C-Terminal Half of AAV9 Capsid 2012
 20 S1 p. S4-S5
2 p.
 artikel
33 461. A Comprehensive Road Map for Risk Assessment of Sleeping Beauty Transposition Events in T-Cell Immunotherapy 2012
 20 S1 p. S179-
1 p.
 artikel
34 256. A Comprehensive Study on Immunology and Persistence of AAV8 Vectors with Self-Complementary and Single-Stranded Genome in Mice: Implications for Transient Immune Suppression with AAV8 Vectors 2012
 20 S1 p. S101-
1 p.
 artikel
35 402. A Controlled DNA Complex Release System Comprising Injectable Auto-Forming Alginate Gel Including Amorphous Calcium Phosphate 2012
 20 S1 p. S157-
1 p.
 artikel
36 341. Activation of Latent HIV-1 by Targeted Suppression of an Endogenous HIV-1 Expressed Antisense Non-Coding RNA 2012
 20 S1 p. S134-
1 p.
 artikel
37 363. Activation of the Cellular Unfolded Protein Response by Recombinant Adeno-Associated Virus Vectors: Implications in Gene Therapy 2012
 20 S1 p. S142-
1 p.
 artikel
38 459. Acute Intrahepatic CD8 T Cell Activation by Plasmid DNA Induces Defective CD8 T Cell Immune Response 2012
 20 S1 p. S178-
1 p.
 artikel
39 470. AdCD40L— From Model Systems to Clinical Trials for Malignant Melanoma 2012
 20 S1 p. S183-
1 p.
 artikel
40 471. AdCD40L Immunostimulating Gene Therapy as a Sensitizer to T Cell Therapy 2012
 20 S1 p. S183-
1 p.
 artikel
41 197. AdCD40L Reduces the Presence of Myeloid-Derived Suppressor Cells in the Tumor Microenvironment 2012
 20 S1 p. S78-
1 p.
 artikel
42 347. Addition of a Modified polyA Signal and Intron into a Lentiviral Platform for RNAi and Protein Over-Expression Provides Potent Efficacy While Maintaining High Vector Titers 2012
 20 S1 p. S136-
1 p.
 artikel
43 222. Addressing the Genotoxic Potential of SIN Lentiviral Vectors for Liver Gene Transfer in Mouse Models of Hepatocarcinogenesis 2012
 20 S1 p. S87-
1 p.
 artikel
44 180. Adeno Associated Virus (AAV) Mediated Follistatin Gene Transfer Toxicology Studies in Preparation of Phase I/II Clinical Trial 2012
 20 S1 p. S72-
1 p.
 artikel
45 104. Adeno-Associated Virus-Directed Persistent Expression of an Anti-Nicotine Antibody Gene for Smoking Cessation 2012
 20 S1 p. S43-
1 p.
 artikel
46 429. Adenoviral and Lentiviral Vectors for Efficient Gene Transfer to Mouse Retina 2012
 20 S1 p. S167-
1 p.
 artikel
47 700. Adenoviral Vectors Retargeted towards Receptor Tyrosine Kinase EphA2 Show Increased Tumor to Liver Ratio after Systemic Application 2012
 20 S1 p. S270-S271
2 p.
 artikel
48 479. Adenoviruses-Mediated Up-Regulation of p53 Expression Produces Cytotoxic Effects on INK4A/ARF-Defective Mesothelioma and Increases the Susceptibility to Chemotherapeutic Agents and Small G Protein Inhibitors 2012
 20 S1 p. S186-
1 p.
 artikel
49 268. Adenovirus Expressing Artificial microRNAs Inhibit the Replication of H1N1 Influenza A Virus in Infected Cells 2012
 20 S1 p. S105-S106
2 p.
 artikel
50 451. Adenovirus Vaccine Vectors Encoding Full-Length Merozoite Surface Protein-1 from Plasmodium falciparum Effectively Induce Adaptive Immune Responses in Different Prime-Boost Combinations with Recombinant Protein 2012
 20 S1 p. S175-
1 p.
 artikel
51 37. Adjunctive β2-Agonist Therapy Enhances Biochemical Correction of Skeletal Muscle from an AAV Vector-Mediated Liver Depot in Advanced Pompe Disease 2012
 20 S1 p. S15-
1 p.
 artikel
52 54. Administration of TGFβ-Resistant Tumor-Specific Cytotoxic T Lymphocytes (CTL) to Patients with EBV-Associated Hodgkin's Lymphoma (HL) and Non-Hodgkin Lymphoma (NHL) 2012
 20 S1 p. S22-S23
2 p.
 artikel
53 672. Adoptive Therapy Evaluating Human IL13-Zetakine T Cells Engineered To Target Glioblastomas Expressing IL13Rα2, a Biomarker Predicting Poor Prognosis 2012
 20 S1 p. S259-S260
2 p.
 artikel
54 715. A Dynamic Shift from Cytokine to Cell Death-Mediated Stimuli Orchestrates Macrophage-Driven Local Neutrophilic Inflammation in Response to Adenovirus In Vivo 2012
 20 S1 p. S276-
1 p.
 artikel
55 494. A Hematopoietic Stem Cell Expansion Medium Increased Transduction Efficiency for Human CD34+ Cells 2012
 20 S1 p. S191-S192
2 p.
 artikel
56 86. A Highly Compact Epitope-Based Marker Suicide Gene for Safer and Easier Adoptive T-Cell Gene Therapy 2012
 20 S1 p. S35-S36
2 p.
 artikel
57 433. A Highly Effective Equine Infectious Anaemia Virus-Based Lentiviral Gene Therapy Platform for the Treatment of Ocular Diseases 2012
 20 S1 p. S168-S169
2 p.
 artikel
58 2. A Lentiviral Vector Pseudotyped with a Baboon Retrovirus Envelope Glycoprotein Outperforms VSV-G-LVs for Gene Transfer into Hematopoietic Stem Cells and Resting Lymphocytes 2012
 20 S1 p. S1-
1 p.
 artikel
59 473. Allele-Specific Inhibition of Nanog Family Members Inhibits Three-Dimensional (3-D) Growth of Human Colorectal Carcinoma (CRC) In Vitro 2012
 20 S1 p. S184-
1 p.
 artikel
60 73. Allele-Specific Silencing of Mutant Huntingtin in HD Neural Stem Cells and In Vivo 2012
 20 S1 p. S30-
1 p.
 artikel
61 269. Allele Specific Targeting of LRRK2 G2019S with shRNA-Induced RNA Interference as a Potential Gene Therapy for Parkinson's Disease 2012
 20 S1 p. S106-
1 p.
 artikel
62 232. Alpha-1 Antitrypsin (AAT) Expression 1 Year after IM Administration of rAAV1-CB-hAAT in a Phase 2 Clinical Trial 2012
 20 S1 p. S231-S232
2 p.
 artikel
63 167. Alpha-Synuclein Overexpression in the Aged Rat Brain: Is the Aging Nigrostriatal System More Suseptible to α-Synuclein Mediated Neurodegeneration? 2012
 20 S1 p. S67-
1 p.
 artikel
64 527. Altering Tissue Glycan Patterns Improves the Transduction Profile of AAV9 Vectors 2012
 20 S1 p. S203-
1 p.
 artikel
65 191. Amelioration of Colitis and Its Associated Colorectal Tumors by CEA — Redirected Tregs 2012
 20 S1 p. S75-S76
2 p.
 artikel
66 American Society of Gene & Cell Therapy 15th Annual Meeting 2012
 20 S1 p. i-xvi
nvt p.
 artikel
67 144. A Murine Model of Aromatic L-Amino Acid Decarboxylase (AADC) Deficiency 2012
 20 S1 p. S58-
1 p.
 artikel
68 530. An AAV Vector-Based Toolbox for Somatic Reprogramming and for iPS Cell Tracking and Purging 2012
 20 S1 p. S204-
1 p.
 artikel
69 376. An Adenovirus Serotype 5 Vector with Tat-PTD Hexon Modification and Serotype 35 Fiber Shows Greatly Enhanced Transduction Capacity of Human Primary Cell Cultures 2012
 20 S1 p. S147-S148
2 p.
 artikel
70 190. Analysis of Gene Expression in Adoptively Transferred TCR-Engineered Lymphocytes 2012
 20 S1 p. S75-
1 p.
 artikel
71 271. Analysis of Growth and Invasion of Human Glioma Cell Lines after Gene Silencing of IL-13Ra2 In Vitro 2012
 20 S1 p. S107-
1 p.
 artikel
72 442. An Approach for Systemic Delivery of Embryonic Stem Cells into Mouse Skeletal Muscle 2012
 20 S1 p. S172-
1 p.
 artikel
73 203. A New Class of Glioblastoma Restricted oHSV Replication Based on microRNA Control of Essential Virus Gene Expression 2012
 20 S1 p. S80-
1 p.
 artikel
74 480. Angiotensin Type 2 Receptors Inhibit Growth of Hepatocellular Carcinoma through Cell Cycle Arrest and Apoptosis 2012
 20 S1 p. S186-
1 p.
 artikel
75 97. An Optimized Two-Finger Archive for Efficient ZFN-Mediated Gene Targeting 2012
 20 S1 p. S40-S41
2 p.
 artikel
76 387. A Novel Approach for Zinc-Finger Nuclease Assembly Using Selected Two-Finger Modules 2012
 20 S1 p. S151-S152
2 p.
 artikel
77 394. A Novel Binary Transfection System for the Targeted Gene Delivery in Prostate Cancer 2012
 20 S1 p. S154-
1 p.
 artikel
78 182. A Novel Cell Therapy for Muscular Dystrophy by Bone Marrow Stromal Cell: Mesenchymal Stem Cell Derived from Bone Marrow Can Affect Skeletal Muscle Regeneration 2012
 20 S1 p. S72-S73
2 p.
 artikel
79 538. A Novel Immune Receptor Expressed by T Cells for Universal Targeting of Diverse and Multiple Tumor Associated Antigens 2012
 20 S1 p. S208-
1 p.
 artikel
80 651. A Novel iPSC-Based Strategy To Correct the Bleeding Phenotype in Hemophilia A 2012
 20 S1 p. S251-
1 p.
 artikel
81 348. A Novel Jurkat-LMO2 Assay System for Vector Safety Testing and Insulator Screening 2012
 20 S1 p. S136-S137
2 p.
 artikel
82 8. A Novel Lentiviral Pseudotype for Vascular Targeted Gene Therapy 2012
 20 S1 p. S4-
1 p.
 artikel
83 616. A Novel Plasmid-Based Therapy Using a Bi-Functional shRNA Vector Targeted to Mesothelin Reduces Pancreatic Cancer Cell Aggressiveness 2012
 20 S1 p. S237-
1 p.
 artikel
84 758. A Novel Platform of Genetically-Modified Cell Transplantation Using 3D Spheroid Culture System on Micropatterned Substrates and Polyplex Nanomicelles 2012
 20 S1 p. S292-
1 p.
 artikel
85 174. A Novel Rationally Designed AAV Micro-Utrophin Vector Recruits nNOS to the Sarcolemma 2012
 20 S1 p. S70-
1 p.
 artikel
86 602. A Novel sLRP6E1E2 Inhibits Canonical Wnt Signaling, Epithelial-to-Mesenchymal Transition, and Induces Mitochondria-Dependent Apoptosis in Lung Cancer 2012
 20 S1 p. S232-
1 p.
 artikel
87 343. A Novel U3 LTR Attachment Site Deleted Non-Integrating Lentiviral Vector 2012
 20 S1 p. S134-S135
2 p.
 artikel
88 614. A Novel Viral Promoter Exhibits Bi-Directional and Highly Inducible Gene Expression Following Stable Delivery in Mammalian Cells 2012
 20 S1 p. S236-
1 p.
 artikel
89 669. Antibody-Mediated Neutralization and Enhancement of Measles Virus Infectivity in Microglial Cells 2012
 20 S1 p. S258-
1 p.
 artikel
90 77. Anti-Cocaine Vaccine dAd5GNE Blocks Cocaine from Binding to the CNS Dopamine Transporter Critical to the Dopamine “Addiction” Pathway 2012
 20 S1 p. S32-
1 p.
 artikel
91 456. Anti-HIV-1 Gene Therapy: In Vitro Safety and Efficacy of Human CD4+ T Cells Modified with a Gamma-Retrovirus Vector Conditionally Expressing the Bacterial Endoribonuclease MazF 2012
 20 S1 p. S177-
1 p.
 artikel
92 95. Anti-Hypertrophic Actions of Cardiac Expression of a GC-A Agonist and a Novel Dual GC-A and GC-B Agonist in a Rat Model of Hypertensive Heart Disease 2012
 20 S1 p. S39-
1 p.
 artikel
93 718. Anti-Luciferase Immune Response after Sleeping Beauty-Mediated Gene Transfer In Vivo 2012
 20 S1 p. S277-
1 p.
 artikel
94 427. Antisense Oligonucleotide-Mediated Exon Skipping Restores Primary Cilia Assembly in Fibroblasts Harbouring the Common Leber Congenital Amaurosis CEP290 Mutation 2012
 20 S1 p. S166-S167
2 p.
 artikel
95 267. Antiviral Potency of Cleaved and Uncleaved Anti-HIV RT Aptamers Expressed Intracellularly Via a Hammerhead Ribozyme Cassette 2012
 20 S1 p. S105-
1 p.
 artikel
96 204. A Phase I Dose Escalation Trial of Intratumoral Injection with Oncoloytic Adenovirus (Ad) Vector VRX-007 in Patients with Advanced Solid Tumors 2012
 20 S1 p. S80-
1 p.
 artikel
97 88. A Phase II Clinical Trial of Recombinant Human Endostatin Adenovirus (E10A) in Combination with Paclitaxel and Cisplatin in Patients with Head and Neck Carcinomas 2012
 20 S1 p. S36-S37
2 p.
 artikel
98 107. A Potential Functional Domain Rich in Basic Amino Acids within the AAV2 Assembly-Activating Protein (AAP) Constrains the Structural Diversity of the AAV2 Capsid 2012
 20 S1 p. S44-S45
2 p.
 artikel
99 393. Application of Mammalian Artificial Chromosomes Suitable for Bioengineering of the Blood Brain Barrier and Delivery of Gene-Based Therapeutics 2012
 20 S1 p. S153-S154
2 p.
 artikel
100 678. A Pre-Clinical Dataset Exploring the Effects of a 19F-MRI Cellular Label on Dendritic Cells 2012
 20 S1 p. S261-S262
2 p.
 artikel
101 241. A Preclinical Model To Study Tumor-Infiltrating Lymphocyte (TIL) Anergy/Exhaustion in Adoptive T Cell Therapy (ACT) of Thoracic Malignancies 2012
 20 S1 p. S95-
1 p.
 artikel
102 682. A Protocol for Ex Vivo Expansion of Effector T Cells That Are Resistant to Oxidative and Apoptotic Stress 2012
 20 S1 p. S263-
1 p.
 artikel
103 640. Aptamer Mediated Delivery of Synthetically Derived Modified mRNA 2012
 20 S1 p. S246-S247
2 p.
 artikel
104 263. Aptamer-siRNA Chimera Inhibitors of Intimal Hyperplasia 2012
 20 S1 p. S103-S104
2 p.
 artikel
105 333. A Rationally Designed Oncolytic Adenovirus, Ad-TD-IL-12, Cures Pancreatic Cancer in the Immunocompetent Syrian Hamster 2012
 20 S1 p. S131-
1 p.
 artikel
106 436. A Recombinant Frataxin Protein Fused with a Cell Penetrating Peptide Prevents the Death of Fibroblasts with Knock-Out Frataxin Genes 2012
 20 S1 p. S169-S170
2 p.
 artikel
107 746. A Red-Nucleus Retro-Vector for Rat Muscle-Derived Stem Cell Modification 2012
 20 S1 p. S288-S289
2 p.
 artikel
108 361. Arsenic Trioxide Treatment Increases the Transduction of Adeno-Associated Virus Serotype 2 (AAV2) Vectors Both In Vitro and In Vivo 2012
 20 S1 p. S141-
1 p.
 artikel
109 409. Arsonium-Based Lipophosphoramides: Antibacterial Effect and Transfection Ability — Both Activities in One Pot 2012
 20 S1 p. S159-S160
2 p.
 artikel
110 595. Artificial RNA Switches for Regulation of Gene Transfer by Adenovectors and Oncolytic Adenoviruses 2012
 20 S1 p. S230-
1 p.
 artikel
111 753. A Simple and Effective Method To Generate Lentiviral Vectors for Ex Vivo Gene Delivery to Mature Human Peripheral Blood Lymphocytes 2012
 20 S1 p. S290-
1 p.
 artikel
112 754. A Simple and Scalable Method To Concentrate Measles Virus Glycoprotein-Pseudotyped Lentiviral Vectors 2012
 20 S1 p. S290-S291
2 p.
 artikel
113 392. A Simple, Flexible System for the Assay of Zinc Finger Nuclease Specificity and Activity 2012
 20 S1 p. S153-
1 p.
 artikel
114 458. A Single Oral Administration of Human Adenovirus 40 Vaccine Against Allergy and Anaphylaxis 2012
 20 S1 p. S178-
1 p.
 artikel
115 460. A Solid Dosage Form for Buccal Delivery of Bacteria-Based Vaccines: Role of Excipients, Crystallinity and Drying Surface 2012
 20 S1 p. S178-S179
2 p.
 artikel
116 659. A Study of Wnt and Notch Signaling in Muscle Stem Cells from Progeria Mouse Models 2012
 20 S1 p. S254-S255
2 p.
 artikel
117 685. A Transcriptionally Targeted, Systemically Administered AAV-sTRAIL in Combination with Lanatoside C for Glioblastoma Therapy 2012
 20 S1 p. S264-S265
2 p.
 artikel
118 242. A Truncation Mutant of CFTR, Δ27-264 CFTR, Corrects Processing Mutants of CFTR 2012
 20 S1 p. S95-S96
2 p.
 artikel
119 466. Attenuated CTLA-4 Inhibition in CD19-Targeted T Cells Expressing a Second-Generation CD28-Based Chimeric Antigen Receptor 2012
 20 S1 p. S466-
1 p.
 artikel
120 282. A Ubiquitous Chromatin Opening Element (UCOE) Prevents Transgene Silencing in Murine Pluripotent Cells and Their Differentiated Hematopoietic Progeny 2012
 20 S1 p. S112-
1 p.
 artikel
121 AUTHOR INDEX 2012
 20 S1 p. S295-S308
14 p.
 artikel
122 751. Autologous Circulating Angiogenic Cells Treated with Osteopontin and Delivered Via a Collagen Scaffold Enhances Wound Healing in the Alloxan-Induced Diabetic Rabbit Ear Ulcer Model 2012
 20 S1 p. S290-
1 p.
 artikel
123 443. Autologous Muscle-Derived Stem Cell Treatment for Female Stress Urinary Incontinence: A 1-Year Follow-Up of Polish Investigation 2012
 20 S1 p. S172-
1 p.
 artikel
124 560. Autophagy Induced by Oncolytic Adenoviruses Combined with Temozolomide Triggers Antitumor Immune Responses Preclinically and in Cancer Patients 2012
 20 S1 p. S217-
1 p.
 artikel
125 379. Baculovirus Administration Triggered Adaptive Immune Response and Hindered the Subsequent Transgene Expression 2012
 20 S1 p. S149-
1 p.
 artikel
126 447. Baculovirus as a Vector for Genetic Modification of Adipose-Derived Mesenchymal Stem Cells and Its Applications in Cartilage Tissue Engineering 2012
 20 S1 p. S173-S174
2 p.
 artikel
127 364. Biased Cardiac Gene Expression by Systemic Administration of AAV Vectors Irrespective of Mice Strain 2012
 20 S1 p. S142-S143
2 p.
 artikel
128 353. bInSiGHT: Bioinformatics Integration Sites Tool for Gene Therapy with High-Throughput Platforms 2012
 20 S1 p. S138-
1 p.
 artikel
129 115. Bio-Engineering of Adeno-Associated Virus Serotype (AAV)-2 Capsid at Serine/Threonine Residues Improves Its Transduction Efficiency Both In Vitro and In Vivo 2012
 20 S1 p. S47-S48
2 p.
 artikel
130 438. Biomaterial-Mediated Gene Delivery for Tissue Engineering of Articular Cartilage 2012
 20 S1 p. S170-
1 p.
 artikel
131 739. Bioprinted Amniotic Fluid-Derived Stem Cells Accelerate Wound Healing in Skin 2012
 20 S1 p. S285-
1 p.
 artikel
132 408. Bioreducible and Acid-Labile Poly(Amido Amine)s for Efficient Gene Delivery 2012
 20 S1 p. S159-
1 p.
 artikel
133 472. Blockade of Bcl-2 Family Apoptosis Inhibitors Using ABT-737 (ABT-263 Analog) Potentiate CAR T Cells 2012
 20 S1 p. S183-
1 p.
 artikel
134 446. Blunted Ventilatory Response to Central Nervous Stimulation in a Canine Model of X-Linked Myotubular Myopathy 2012
 20 S1 p. S173-
1 p.
 artikel
135 617. Broadening the DNA-Recognition Potential of Homeodomains To Create New Modules for Targeted Genome Editing 2012
 20 S1 p. S238-
1 p.
 artikel
136 551. Broadening the Donor Pool by Disrupting HLA Expression in Hematopoietic Stem Cells without Compromising Stem Cell Properties 2012
 20 S1 p. S213-
1 p.
 artikel
137 662. Broad Neutralizing Immune Responses Against Hepatitis C Virus Induced by Vectored Measles Virus and a Recombinant Envelope Protein Boost 2012
 20 S1 p. S255-
1 p.
 artikel
138 668. Capsid Modified AAV2 Vectors Are Capable of Generating Vaccine-Mediated Protection 2012
 20 S1 p. S257-S258
2 p.
 artikel
139 439. Cartilage Matrix Recovery after Chondrocyte Transduction with a Dual Expressing Long Hairpin Plasmid Targeting IL-1 beta and TNF-alpha Knockdown 2012
 20 S1 p. S170-S171
2 p.
 artikel
140 431. CCR5-Transduced Neural Stem Cells Confer Accelerated and Enhanced Therapeutic Effect on Experimental Autoimmune Encephalomyelitis 2012
 20 S1 p. S168-
1 p.
 artikel
141 377. CD46 Does Not Affect the In Vivo Biodistribution of Species D Adenoviruses, Ad26 or Ad48 in CD46 Transgenic Mice Following IV Delivery 2012
 20 S1 p. S148-
1 p.
 artikel
142 517. CD15-Enrichment of Donor Primary Murine Neural Stem Cells Increases Total Engraftment and Results in Wider Dissemination within Host Brains 2012
 20 S1 p. S200-
1 p.
 artikel
143 189. CD40-Ligand Armed Vaccinia Virus for Induction of Anti-Tumor Immune Response 2012
 20 S1 p. S75-
1 p.
 artikel
144 475. CD19-Specific T-Cell Therapy for Refractory Philadelphia-Chromosome-Positive Acute Lymphoblastic Leukemia Using PiggyBac Transposon-Based Gene Modification and Low Autoserum-Containing, but Xeno-Free and Tumor Cell Line-Free Culture System 2012
 20 S1 p. S184-S185
2 p.
 artikel
145 765. Cell Therapy Industry Market Characteristics: Implications for Clinicians, Investors, Patients and Translational Researchers 2012
 20 S1 p. S294-
1 p.
 artikel
146 430. CEP290 Minigene Model of Common Splice Site Mutation in Leber Congenital Amaurosis 2012
 20 S1 p. S167-S168
2 p.
 artikel
147 101. CFTR Gene Correction of Only the Surface Airway Epithelium Restores Antimicrobial Activity to CFTR Knockout Ferret Tracheas Ex Vivo 2012
 20 S1 p. S42-
1 p.
 artikel
148 759. cGMP Plasmid Manufacturing and Release Criteria for Phase I/II Trials 2012
 20 S1 p. S292-
1 p.
 artikel
149 762. Characterisation of Viral Count by Nanoparticle Tracking and Analysis (NTA) Technique and Its Application to Gene Therapy 2012
 20 S1 p. S293-
1 p.
 artikel
150 557. Characterization of AAV T Cell Epitopes Presented by Splenocytes from Normal Human Donors 2012
 20 S1 p. S215-S216
2 p.
 artikel
151 257. Characterization of Naturally-Occurring Humoral Immunity to AAV in Sheep 2012
 20 S1 p. S101-
1 p.
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152 113. Characterization of Porcine Adeno-Associated Viruses Belonging to Unique Clades 2012
 20 S1 p. S46-S47
2 p.
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153 365. Characterization of Residual Plasmid DNA Impurities in Recombinant AAV; Correlation with Size of Transgene Expression Cassette 2012
 20 S1 p. S143-
1 p.
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154 694. Characterization of the Mechanisms of Tumor Dormancy and Recurrence Following Front Line Immuno-, Viro- or Suicide Gene-, Therapy 2012
 20 S1 p. S268-
1 p.
 artikel
155 120. Characterization of the Role of Vaccinia Virus in the Activation of Adeno-Associated Virus Promoters 2012
 20 S1 p. S49-
1 p.
 artikel
156 102. Chemically Modified mRNA Encoding mFoxp3 Protects Against Airway Inflammation in a Murine Model of Allergic Asthma 2012
 20 S1 p. S42-S43
2 p.
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157 606. Chimpanzee Adenovirus Expressing microRNA as a New Therapeutic Strategy Against HPV-Related Cervical Cancer 2012
 20 S1 p. S234-
1 p.
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158 411. Chitosan-Hyaluronic Acid Hybrid Vectors for Retinal Gene Therapy 2012
 20 S1 p. S160-
1 p.
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159 748. Chondrogenesis of Mesenchymal Stem Cells In Vivo 2012
 20 S1 p. S289-
1 p.
 artikel
160 510. Circulating microRNA as a Potential Biomarker of Ischemic Stroke 2012
 20 S1 p. S197-
1 p.
 artikel
161 420. Clinical Grade Lentiviral Vector Production for the Inherited Skin Disease, Netherton Syndrome 2012
 20 S1 p. S164-
1 p.
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162 450. Clinical Methods of Intramuscular Diaphragm Injections for Gene Therapy 2012
 20 S1 p. S174-S175
2 p.
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163 613. Closed-Ended Linear Duplex AAV (celdAAV) DNA for Non-Viral Gene Transfer 2012
 20 S1 p. S236-
1 p.
 artikel
164 642. Co-Delivery of Minicircle-Endostatin and ZD6474, a Small Molecule Tyrosine Kinase Inhibitor from Biodegradable Cationic Micelles for Cancer Therapy 2012
 20 S1 p. S247-
1 p.
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165 356. Codon Optimization of RD114-TR Envelope Glycoprotein Leads to Lack of Correct Processing and Therefore Correct Function of the Envelope 2012
 20 S1 p. S139-
1 p.
 artikel
166 416. Co-Encapsulation of Islets with Mesenchymal Stem Cells Improves Islet Function 2012
 20 S1 p. S162-
1 p.
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167 638. Combinational Anti-Cancer Therapy with Doxorubicin and EGFR-Targeted Immunonanoparicles Containing IL12/Salmosin Genes 2012
 20 S1 p. S245-S246
2 p.
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168 401. Combination of Doxorubicin and EGFR-Directed Immunonanoplexes Containing Vimentin/JAK3 siRNA for Anticancer Therapy 2012
 20 S1 p. S157-
1 p.
 artikel
169 665. Combinatorial Approach Using MGMT P140K Transgene and Multiplexed RNAs in Gene Therapy Against HIV-1 2012
 20 S1 p. S256-S257
2 p.
 artikel
170 96. Combined Gene- and Drug-Based Intervention Is Protective Following Cerebral Ischaemia/Reperfusion 2012
 20 S1 p. S40-
1 p.
 artikel
171 205. Combined Therapies with Oncolytic Adenovirus Suppress Tumor Growth in Hamsters 2012
 20 S1 p. S80-S81
2 p.
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172 194. Combining the Dual Tyrosine Kinase Inhibitor, Lapatinib, with HER2 Specific Cytotoxic T-Lymphocytes in the Treatment of HER2 Overexpressing Breast Cancer 2012
 20 S1 p. S77-
1 p.
 artikel
173 247. Comparative Analysis of the Transduction Efficiency of Five AAV Serotypes and Lentiviral Vectors in Lung Cancer Cells 2012
 20 S1 p. S97-
1 p.
 artikel
174 512. Comparison of Commercially Available Furin ELISA Kits To Assess Furin Knockdown in cGMP Manufactured FANG™ Vaccines 2012
 20 S1 p. S198-
1 p.
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175 7. Comparison of Different Internal Promoter Performance in the CL20 SIN HIV Lentivector Used To Correct Human X-Linked Chronic Granulomatous Disease as Evaluated Ex Vivo and in NSG Mice Transplanted with Transduced Patient CD34+ Stem Cells 2012
 20 S1 p. S3-S4
2 p.
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176 290. Comparison of Enzymatic and Non-Enzymatic Passaging of Human Embryonic Stem Cells 2012
 20 S1 p. S114-
1 p.
 artikel
177 493. Comparison of Safety and Effectiveness between Gamma-Retroviral, Lentiviral and Foamy Virus Gene Transfer Vectors 2012
 20 S1 p. S191-
1 p.
 artikel
178 226. Complete Long-Term Correction of Hemophilic B Mice Using Integration-Defective Lentiviral Vectors Expressing Codon-Optimized R338L Human Factor IX 2012
 20 S1 p. S89-
1 p.
 artikel
179 579. Complete Tropism Restriction by Display of High Affinity Ligands on Adeno-Associated Viral Vectors 2012
 20 S1 p. S225-
1 p.
 artikel
180 422. Compromised Platelet Fragmentation, Size, and Function Resulting from May-Hegglin Mutations of NMM-II 2012
 20 S1 p. S164-S165
2 p.
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181 712. Conditionally Replicating Adenovirus Influences Intracranial Infiltration of Regulatory T Cells in Experimental Mouse Model of Brain Tumor 2012
 20 S1 p. S275-
1 p.
 artikel
182 569. Correction of Artemis Deficiency in Murine Hematopoietic Stem Cell by I-Sce1 Meganuclease and Artemis Recombination Matrix Mediated Homologous Recombination 2012
 20 S1 p. S221-
1 p.
 artikel
183 57. Correction of Hemophilia B Phenotype Following ZFN Mediated Genome Editing in Adult Mice 2012
 20 S1 p. S24-
1 p.
 artikel
184 230. Correction of Immunity in Murine Rag2 Severe Combined Immunodeficiency by Lentiviral Gene Therapy Using a Codon-Optimized RAG2 Therapeutic Transgene 2012
 20 S1 p. S90-S91
2 p.
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185 464. Correlation of Immune Response with Long Term Survival of Refractory Cancer Patients Who Received TGF-β2 Antisense/GM-CSF Gene Modified Autologous Tumor Cell (TAG) Vaccine 2012
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1 p.
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186 14. Critical Amino Acid Redisues Contribute to Crossing Vascular Barrier 2012
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1 p.
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187 738. Cyclooxygenase-2 Plays a Critical Role in BMP4GFP Transduced Muscle Derived Stem Cell Mediated Bone Healing in the Critical Sized Calvarial Defect Model 2012
 20 S1 p. S284-S285
2 p.
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188 737. Defective Proliferation and Myogenic Differentiation Potential of Muscle-Derived Stem Cells Isolated from Dystrophin/Utrophin Double Knock-Out Mice 2012
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1 p.
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189 253. Deficiency in MyD88 Signaling Results in Decreased Antibody Responses to Adeno-Associated Virus Vector Containing a CMV Enhancer/Chicken β-Actin Cassette in Murine Pompe Disease 2012
 20 S1 p. S100-
1 p.
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190 509. Deletion of Proline 45 (PDX-1 ΔP45) Enhances Oncogenic Properties of PDX-1 2012
 20 S1 p. S197-
1 p.
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191 163. Delivery of a Therapeutic Molecule to the Brain for the Treatment of Neurodegenerative Diseases: Production of AAV-5-GDNF by a GMP-Compliant and Scalable Production Platform Results in a Highly Efficient Gene Therapy Vector 2012
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1 p.
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192 293. Delivery of Novel microRNAs Improves Cardiac Myocyte Proliferation In Vivo 2012
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2 p.
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193 145. Demonstration of Pre-Clinical Efficacy of rAAV8 Gene Transfer as a Treatment for Methylmalonic Acidemia Using a Vector Suitable for Human Clinical Trials 2012
 20 S1 p. S58-
1 p.
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194 34. Demonstration of Systemic Exon 45-55 Multiple Skipping in Dystrophic mdx52 Mice 2012
 20 S1 p. S14-
1 p.
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195 294. De Novo Design of Tissue-Specific Regulatory Elements Results in Robust Transduction in Heart and Liver: Implications for Cardiovascular Disease and Hemophilia 2012
 20 S1 p. S116-
1 p.
 artikel
196 279. Derivation and Functional Analysis of Patient Specific Induced Pluripotent Stem Cells as an In Vitro Model of Chronic Granulomatous Disease 2012
 20 S1 p. S110-
1 p.
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 20 S1 p. S20-
1 p.
 artikel
198 112. Design and Characterization of New Generation Synthetic AAV Capsid Libraries 2012
 20 S1 p. S46-
1 p.
 artikel
199 58. Designer Nuclease Platform Comparison: ZFNs Versus TALENs 2012
 20 S1 p. S24-
1 p.
 artikel
200 339. Detection Methods for In Vitro and In Vivo Characterization of Cell-Specific, Cell-Internalizing RNA Aptamers for siRNA Delivery 2012
 20 S1 p. S133-
1 p.
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201 521. Determinants of Extrahepatic Biliary-Derived Cell Transdifferentiation into Endocrine beta-Like Cells In Vitro 2012
 20 S1 p. S201-
1 p.
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202 175. Determining the Therapeutic Window: Central Nervous System Administration for Vector Mediated Gene Replacement in a Severe Model of Spinal Muscular Atrophy 2012
 20 S1 p. S70-
1 p.
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203 169. Developing Engineered Zinc Finger Repressors of Huntingtin as a Potential Therapy for Huntington's Disease 2012
 20 S1 p. S68-
1 p.
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204 691. Developing Inhibitor-Directed Enzyme Prodrug Therapy for the Treatment of Prostate Cancer 2012
 20 S1 p. S267-
1 p.
 artikel
205 195. Development of a CAR T Cell Platform with Dissociated Signalling Domains for Selective Reactivity Against Ovarian Cancer 2012
 20 S1 p. S77-
1 p.
 artikel
206 225. Development of a Clinically-Applicable Lentiviral Vector for RS-SCID Gene Therapy 2012
 20 S1 p. S88-S89
2 p.
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207 322. Development of a Highly Efficient Second Generation Nicotine-Conjugate Vaccine To Treat Nicotine Addiction 2012
 20 S1 p. S127-
1 p.
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208 99. Development of a High-Through Approach for Quantitating Cellular microRNA Activity and Identifying Optimal Target Sites for microRNA-Based Vector Targeting 2012
 20 S1 p. S41-
1 p.
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209 415. Development of a Lentiviral Gene Therapy for Adenosine Deaminase-Deficient Severe Combined Immunodeficiency (ADA-SCID) 2012
 20 S1 p. S162-
1 p.
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210 643. Development of Anionic Nanocomplexes for Targeted SiRNA and Plasmid DNA Delivery 2012
 20 S1 p. S248-
1 p.
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211 381. Development of a Novel Adenovirus Vector Carrying microRNA-Targeted Sequences in the 3'-Untranslated Region of the pIX, E2A, or E4 Gene for Suppression of the Leaky Expression of Adenovirus Genes 2012
 20 S1 p. S149-
1 p.
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212 661. Development of a Novel DNA Vaccine Strategy for Prevention of Clostridium difficile Infection 2012
 20 S1 p. S255-
1 p.
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213 380. Development of a Novel Targeted Adenovirus Vector Displaying Monobody Binding to Anti-Vascular Endothelial Growth Factor Receptor 2 in a Fiber Protein 2012
 20 S1 p. S149-
1 p.
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214 658. Development of a Physiologically Relevant In Vitro Model of AAV8 Transduction of Primary Mouse Hepatocytes 2012
 20 S1 p. S254-
1 p.
 artikel
215 378. Development of a Recombinase-Based Hybrid Baculoviral Vector for Sustained Transgene Expression 2012
 20 S1 p. S148-
1 p.
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216 403. Development of Dexamethasone Conjugated Low Molecular Weight Polyethylenimine as a Gene Delivery Carrier for Gene Therapy of Glioblastoma 2012
 20 S1 p. S157-S158
2 p.
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217 217. Development of Efficient Oncolytic Adenoviruses Against Melanoma by Combining Rational Engineering and Directed Evolution 2012
 20 S1 p. S85-
1 p.
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218 318. Development of Gene Therapy for Hemophagocytic Lymphohistiocytosis (HLH) Due to Perforin Deficiency 2012
 20 S1 p. S125-S126
2 p.
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219 453. Development of Intranasal Formulations for a Human Adenovirus Serotype 5-Based Vaccine with Potential To Bypass Pre-Existing Immunity 2012
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1 p.
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220 498. Development of In Vivo Gene Therapy of Hemophilia A Mice by Intra-Bone Marrow Injection of Lentiviral Vectors Containing a B-Domain Variant of Human Factor VIII 2012
 20 S1 p. S193-
1 p.
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221 636. Development of Non-Viral Gene Delivery Particles Based on the Dynein Light Chain Rp3 2012
 20 S1 p. S245-
1 p.
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222 612. Development of Non-Viral Vectors for the Prophylactic Gene Therapy of Birt—Hogg—Dubé (BHD) Syndrome 2012
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2 p.
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223 639. Development of Novel Phosphonium-Containing Block Copolymers for siRNA Delivery 2012
 20 S1 p. S246-
1 p.
 artikel
224 646. Development of pH Responsive Cationic Amphipathic Peptides for the Delivery of Plasmid DNA and siRN A 2012
 20 S1 p. S249-
1 p.
 artikel
225 635. Development of Plasmid-Lipoparticle Systemic Delivery System That Overcome the Paradox of PEG-Stabilization While Maintaining High Transfection Potency 2012
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1 p.
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226 564. Development of Universal Donor Human Pluripotent Stem Cells by Engineering of the HLA Locus 2012
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2 p.
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227 18. Development of Vaxfectin®-Formulated HSV-2 Plasmid DNA Vaccines for Prophylactic and Therapeutic Applications 2012
 20 S1 p. S7-S8
2 p.
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228 625. Differential Perturbations of the Salivary Gland Proteome Following AAV-Mediated or Ultrasound-Assisted Gene Transfer 2012
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1 p.
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229 502. Differential Regulation of Multiple Transgenes in AAV Vectors by Alternative Splicing 2012
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2 p.
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230 287. Differentiation of Human Pluripotent Parthenogenetic and Embryonic Stem Cells into Cornea-Like Constructs for Transplantation and for Studying Ocular Drug Absorption In Vitro 2012
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1 p.
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231 358. Directed Evolution of AAV for Enhanced Evasion of Human Neutralizing Antibodies 2012
 20 S1 p. S140-
1 p.
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232 591. Directed Evolution To Create Choroid Plexus-Permissive AAV Capsid Variants: Toward Novel Clinical Management of Lysosomal Storage Disorders 2012
 20 S1 p. S229-
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233 351. Directed Integration of Insulated Lentiviral Vectors to the Heterochromatin towards Safer Gene Transfer to Stem Cells 2012
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2 p.
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234 142. Direct Hepatic Injections of HDAd Vector Are More Efficient and Safer Than Systemic Intravenous Injections for Liver-Directed Gene Therapy of Crigler-Najjar Syndrome Type I 2012
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2 p.
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235 586. Distinct Transduction Difference between Adeno-Associated Virus Type 1 and Type 6 Vectors in Human Polarized Airway Epithelia 2012
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1 p.
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236 648. DMSO Shock Yields Highly Efficient Transient Transfection by PEI/DNA Nanoparticles 2012
 20 S1 p. S250-
1 p.
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237 362. DNA Repair Dependent Viral Vectors Interrogate the Host DNA Damage Response and Offer Efficient Large Therapeutic Gene Delivery 2012
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1 p.
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238 324. DNA Vaccination To Generate Chikungunya Virus-Specific Immunity 2012
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1 p.
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239 532. Donor T Cells Specific for Multiple Leukemia Antigens for Adoptive Immunotherapy of Myeloid Leukemias after Stem Cell Transplantation 2012
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240 733. Dose-Dependent Knocking-Down on Eag1 from Glioma Cells in Culture Caused by Synthetic siRNAs 2012
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241 655. Dose-Response Relationship of Factor IX Expression in Non-Human Primates Following IV Administration of AAV8 Vectors 2012
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242 80. Dose-Response Study of Continuous DOPA Delivery with AAV Gene Therapy Reveals Threshold and Kinetics for Restoration of Motor Function in a Rodent Model of Parkinson's Disease 2012
 20 S1 p. S33-
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243 25. Dramatic Phenotypic Improvement in a Feline Model of Sandhoff Disease Treated by Adeno-Associated Virus Gene Therapy 2012
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244 465. Dual Transgenesis of T Cells with a CD44v6 CAR and a Suicide Gene for the Safe Eradication of Myeloid Leukemia and Myeloma 2012
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2 p.
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245 274. Eag1 Gene Silencing by Non-Viral Expression Vector Reduces the Viability of Neuroblastoma Cells in Culture 2012
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246 654. Early AAV-Mediated Intrauterine Gene Therapy at 0.4G in Non-Human Primates 2012
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247 83. Early Acute Phase Response and Distribution of pbi-shRNA PDX-1 Lipoplex in Yucatan Swine 2012
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248 338. Effective Regression of Melanoma Cancer by Delivery of Combinatorial siRNA Using an Arginine-Engrafted Biodegradable Polymer 2012
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1 p.
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249 66. Effective Treatment of Hemophilia A Using Hematopoietic Stem Cell Transplantation and a Bioengineered Factor VIII Transgene 2012
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250 337. Effect of Argonaute-2 in Mediating Non-Coding RNA Expression 2012
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251 266. Effect of Continuous Exposure to Antisense BNA Slowly Released in Intraperitoneal or Subcutaneous Tissue 2012
 20 S1 p. S105-
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252 200. Effect of γ34.5 Deletions on Oncolytic Herpes Simplex Virus Activity in Glioblastoma Stem Cells 2012
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253 419. Effect of Exendin-4 Expressed by Two-Step Transcription Amplification Plasmid System with Arginine-Grafted Bioreducible Polymer for Type 2 Diabetes 2012
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254 637. Effect of PEG Grafting Degree on Morphology and Transfection Efficiency of Polycation-g-PEG/DNA Nanoparticles 2012
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255 726. Effect of 5’ Terminal Triphosphate in Exogenous siRNA and shRNA on Gene Silencing and Innate Immune Response 2012
 20 S1 p. S280-
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256 481. Effects of Angiotensin Type 2 Receptor Overexpression on Gene Expression Profiles in Human Prostate Cancer Cells 2012
 20 S1 p. S186-S187
2 p.
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257 732. Effects of hEag1 shRNA Expression Vector on Cell Viability of Glioma Cells In Vitro 2012
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1 p.
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258 211. Efficacy and Safety of Gene-Chemo Therapy Using Oncolytic Adenovirus Expressing Uracil Phosphoribosyl Transferase (UPRT) Followed by 5-Fluorouracil Administration in Syngenic Pancreatic and Biliary Cancers in Immunocompetent Adenovirus-Permissive Syrian Hamsters 2012
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1 p.
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259 221. Efficacy and Safety of the Foamy Viral Vector ΔΦMscvCD18 in Long-Term Follow-Up (4-6 years) of Four Dogs with Canine Leukocyte Adhesion Deficiency 2012
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1 p.
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260 615. Efficiency of AAV Versus DNA Nanoparticle Formulation in Retinal Gene Targeting 2012
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1 p.
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261 727. Efficiency of RNAi-Induced Silencing in Airway Epithelial Cells Is Reduced 2012
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2 p.
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262 352. Efficient and Non-Toxic Targeting of a Human Safe Harbor Locus with a Lentiviral Vector Associated Meganuclease 2012
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1 p.
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263 406. Efficient and Specific Co-Delivery of Vimentin siRNA and Doxorubicin with Aptamosomes for Combination Cancer Therapy 2012
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1 p.
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264 243. Efficient Apical Transduction of Polarized Human Airway Epithelium by Adenovirus Serotype 3 2012
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1 p.
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265 385. Efficient Enrichment of Cells with Programmable Nuclease-Induced Mutations by Surrogate Reporter 2012
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1 p.
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266 44. Efficient Generation of Gene-Corrected, Vector- and Reprogramming Factor-Free iPS Cells from SCID-X1 Patients 2012
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1 p.
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267 570. Efficient Generation of Induced Pluripotent Stem Cells by the Inhibition of PTEN Tumor Suppressor 2012
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1 p.
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268 572. Efficient High Titer Production of Recombinant Lentiviral Vectors for Cancer Immunotherapy 2012
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1 p.
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269 542. Efficient HSV-1 Retargeting by Modification of Glycoproteins D and B 2012
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1 p.
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270 628. Efficient Hydrodynamic Limb Perfusion of an AAV9 Mini-Dystrophin in Adult GRMD Dogs by a Clinically Used, Pressure- and Speed-Controlled Pump 2012
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1 p.
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271 444. Efficient Myoblast Expansion for Urinary Incontinence Treatment 2012
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2 p.
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272 303. Efficient Site-Specific Integration in Human Hematopoietic Stem and Progenitor Cells by Zinc Finger Nucleases and Integrase-Defective Lentiviral Vectors 2012
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1 p.
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273 435. Efficient Transduction of Tyrosine-to-Phenylalanine Mutated AAV2 Vectors Carrying Human ND4 Gene and Biodistribution Following Intravitreal Delivery in a Rodent Model — A Gene Therapy for Leber Hereditary Optic Neuropathy 2012
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1 p.
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274 620. Electroporation Enhanced Human Kallistatin Expression for the Prevention of TNBS-Induced Colitis in Mice 2012
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1 p.
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275 664. Electroporation-Mediated Genetic Vaccination for Antigen Mapping: Application to Plasmodium Falciparum VAR2CSA Protein 2012
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276 463. Elimination of Metastatic Tumors Using Gold Nanoshell-Enabeled Photothermal Therapy Pretreatment Followed by Adoptive T Cell Therapy 2012
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1 p.
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277 421. Engineered Insulin Secretion in Human Primary Thyroid Cells 2012
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1 p.
 artikel
278 227. Engineered Nuclease Mediated Gene Targeting of the Human IL2Rγ Gene 2012
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1 p.
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279 304. Engineered Zinc Finger Nickases for Stimulating Homology-Directed Repair with Decreased Mutagenic Effects 2012
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280 193. Engineering CD20-Specific Chimeric Receptor-Redirected T Cells with Inducible Co-Expression of a Caspase-9 Based Suicide Switch for Adoptive Immunotherapy of CD20 Positive Lymphoma 2012
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1 p.
 artikel
281 360. Enhanced Alpha-1 Antitrypsin (AAT) Expression and Decrease Immune Response with Isolated Limb Perfusion (ILP) Delivery of rAAV1-CB-hAAT 2012
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1 p.
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282 250. Enhanced Amplitude and Functionality of T Cell Responses in Virally Infected Human-Like Cmah Null Mice 2012
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2 p.
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283 455. Enhanced DNA Vaccine with Protein Boost Delivered by EP Expands B and T Cell Responses and Neutralizing Phenotype In Vivo 2012
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2 p.
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284 589. Enhanced Fracture Healing Utilizing In Vivo Biopanning of Adeno-Associated Virus from a Directed Evolution Library 2012
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1 p.
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285 123. Enhancement of Transfection of Linear Expression Cassettes after Ligation 2012
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286 91. Enhancing Gene Transfection In Vivo Using Therapeutic Ultrasound and New Microbubbles 2012
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287 238. Enhancing Immunotherapy with a Replicating Vaccinia Virus Expressing CXCL11 to Chemoattract T-Cells into Tumors 2012
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288 764. Enhancing the Expression of Foreign Genes with Caffeine in Transfected and Infected Cells 2012
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289 506. Epigenetic Status of Cell-Fate Associated Promoters during Expansion of Bone-Marrow Derived Multipotent Mesenchymal Stromal Cells 2012
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290 260. Epirubicin Potentiates rAAV2/5-Mediated TRAIL Expression in Fibroblast-Like Synoviocytes and Augments the Anti-Arthritis Effects of rAAV2/5-TRAIL 2012
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291 158. Evaluating Huntington's Disease Therapeutics In Vivo Using a Sensitive Measure of Transcriptional Dysregulation 2012
 20 S1 p. S63-
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292 62. Evaluating the Safety of PiggyBac Mediated Gene Transfer in Human Cells 2012
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293 695. Evaluation of a Novel Oncolytic Herpes Simplex Virus Type-1 Encoding Human Sodium Iodide Symporter for Human Prostate Cancer Radiovirotherapy 2012
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2 p.
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294 677. Evaluation of Anti-Tumor Effects Mediated by Engineered T Lymphocytes Expressing a CD19 Specific CAR for B Cell Lymphoma 2012
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295 462. Evaluation of Immune Response to Treatment with TAG or FANG™ Vaccine by Assessing IFNγ Expression Using ELISPOT (Enzyme Linked Immunospot) Assay 2012
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296 710. Evaluation of Membrane-Anchored Versions of Interleukin-12 as Transgenes in Armed Oncolytic Adenoviruses 2012
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297 529. Evaluation of Porcine AAVs as Vaccine Vectors Against Avian Flu and Zaire Ebolavirus Infections 2012
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298 599. Evaluation of the Cytokines SCF and IL-3 and Charged-Based Polymers for Targeting of Adenovirus Vectors to Human Hematopoietic Progenitor Cells 2012
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299 561. Expansion of FoxP3+ Regulatory T Cells in Mucopolysaccharidosis Type I Mice Prior to Lentiviral Gene Transfer Promotes Tolerance to α-l-Iduronidase 2012
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300 683. Exploiting Endogenous microRNA Regulation To Target Gene Therapy to Tumors by Infiltrating Macrophages 2012
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2 p.
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301 576. Exploiting the Mechanism of Intron-Splicing in Insect Cells To Produce Viral Vectors Harboring Toxin Genes for Cancer Gene Therapy 2012
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2 p.
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302 323. Expression of Broadly Neutralizing Antibodies (NAbs) Against HIV in RAG KO Mice 2012
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2 p.
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303 511. Expression of GMCSF, TGFβ1, TGFβ2 and Correlation to FURIN Expression in Culture Supernatants from Pre- and Post-FANG™ Plasmid Transfected Autologous Tumor Cells 2012
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304 582. Expression of Therapeutic Levels of Human Clotting Factor IX in Non Human Primates from an AAV5-Based Gene Therapeutic Vector Generated Using a Fully-Scalable GMP-Compliant Production System 2012
 20 S1 p. S226-
1 p.
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305 566. Extreme Skewing of X-Chromosome Inactivation in Female Carriers of X-CGD Can Be Reversed during iPSC Reprogramming To Restore Neutrophil Function 2012
 20 S1 p. S219-S220
2 p.
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306 60. Extrinsic Determinants of ZFN and TALEN-Mediated Gene Disruption 2012
 20 S1 p. S25-
1 p.
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307 515. Ex Vivo Conditioning Regimen by Reversible Non-Muscle Myosin-II Inhibition and Aryl Hydrocarbon Receptor Antagonism Increases Platelet Recovery and Maintains Long-Term Hematopoietic Reconstitution after Human Bone Marrow Transplantation 2012
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1 p.
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308 23. Facial Amphipathic Deoxycholic Acid-Modified Polyethyleneimine Used as SHP-1 siRNA Carrier for the Treatment of Ischemia-Reperfusion Cardiac Injury 2012
 20 S1 p. S9-S10
2 p.
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309 391. Factors Affecting Maintenance of the Sleeping Beauty Transposon-Mediated Expression of Human alpha-L-Iduronidase in Mice 2012
 20 S1 p. S153-
1 p.
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310 719. Fc gamma Receptor Polymorphisms as Prognostic and Predictive Biomarkers for Oncolytic Adenovirus Therapy 2012
 20 S1 p. S277-S278
2 p.
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311 213. [F18]-FDG-PET Versus CT for Evaluation of Oncolytic Virus Treatment in Advanced Cancer Patients 2012
 20 S1 p. S84-
1 p.
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312 184. Follistatin N-Terminal Mutation Diminishes Muscle Growth Effects In Vivo 2012
 20 S1 p. S73-
1 p.
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313 492. Foxp3-Retrovirus Transduction to CD4+ T Cells Induce Regulatory Potential with Decreased Secretion of Interferon-gamma 2012
 20 S1 p. S190-S191
2 p.
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314 246. Functional Decline, Remodeling, and Compensation in the Respiratory System of a Canine Model of Duchenne Muscular Dystrophy 2012
 20 S1 p. S97-
1 p.
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315 634. Fusogenic Cell Entry of Bilamellar Invaginated Vesicle (BIV) Complexes with or without Small Molecules for Targeted Delivery 2012
 20 S1 p. S244-
1 p.
 artikel
316 514. FVIII Expression and Secretion in Circulating Blood Cell Types Capable of Correcting Bleeding in Hemophilia A Mice 2012
 20 S1 p. S198-S199
2 p.
 artikel
317 621. Gene Delivery to Skin by Electroporation 2012
 20 S1 p. S239-
1 p.
 artikel
318 92. Gene Electrotransfer to a Beating Heart in a Porcine Ischemia Model 2012
 20 S1 p. S38-
1 p.
 artikel
319 396. Gene Expression from Linearized Gene Expression Cassettes Capped with Multi-Arm DNA Junctions 2012
 20 S1 p. S155-
1 p.
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320 603. Generating a Replication Competent Adenovirus Vector That Targets the c-Met Receptor 2012
 20 S1 p. S232-S233
2 p.
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321 311. Generation and Correction of a Novel Mouse Model of Acid Ceramidase Deficiency 2012
 20 S1 p. S123-
1 p.
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322 355. Generation of a Barcoded Lentiviral Plasmid Library for Analyzing Clonal Complexity and Evaluation of Library Complexity Using Next Generation Sequencing 2012
 20 S1 p. S139-
1 p.
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323 467. Generation of Antigen Specific T Cells from Human Hematopoietic Stem/Progenitor Cells (HSPC) Transduced with the cDNA for a T Cell Receptor Specific for the MART-1 Antigen 2012
 20 S1 p. S466-
1 p.
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324 289. Generation of Footprint Free iPSCs from CD34+ and PBMCs Using Sendai Virus Vector and Application of Alkaline Phosphatase Live Stainning Dye 2012
 20 S1 p. S114-
1 p.
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325 280. Generation of Integration-Free iPSCs from an X-CGD Patient's Blood Cells as Clinically Relevant Target for Gene-Repair Using Designer ZFN or TALEN 2012
 20 S1 p. S110-S111
2 p.
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326 747. Generation of Vascularized Nervous or Insulin-Secreting Tissues 2012
 20 S1 p. S289-
1 p.
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327 307. Gene Targeting of the Human Globin Loci Using Engineered Nucleases 2012
 20 S1 p. S121-S122
2 p.
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328 160. Gene Therapy for Stargardt Disease Using Helper-Dependent Adenoviral Vectors 2012
 20 S1 p. S64-
1 p.
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329 484. Gene Therapy for Wiskott Aldrich Syndrome: Sustained Expression from the MND Promoter in Platelets and Blood Cells upon Serial Transplantation 2012
 20 S1 p. S188-
1 p.
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330 31. Gene Therapy of Adult MLD Model Mice by Intrathecal Administration of Type 9 AAV Vector 2012
 20 S1 p. S13-
1 p.
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331 680. Gene Therapy of Chondroitin Sulfate-Coated Ternary GM-CSF Plasmid Complex for Ovarian Cancer 2012
 20 S1 p. S262-S263
2 p.
 artikel
332 46. Gene Therapy of Congenital Erythropoietic Porphyria Using Genetically Modified Induced Pluripotent Stem Cells 2012
 20 S1 p. S19-
1 p.
 artikel
333 236. Gene Therapy of Cystic Fibrosis: Impact of Plasmid DNA on In Vivo Lipid-Based Transfection Efficacy 2012
 20 S1 p. S93-
1 p.
 artikel
334 278. Gene Therapy of Erythropoietic Porphyria Mice with Induced Pluripotent Stem Cells 2012
 20 S1 p. S109-S110
2 p.
 artikel
335 552. Gene Therapy of Human Blnk Deficiency in NOD/SCID/gc ko Murine Model 2012
 20 S1 p. S213-S214
2 p.
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336 134. Gene Therapy Versus Enzyme Replacement Therapy in a Murine Model of Mucopolysaccharidosis VI 2012
 20 S1 p. S54-S55
2 p.
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337 240. Genetically Engineered Measles Virus Edmonston Strain Expressing the Wild-Type N, P, L Genes (MV-NPL) Is a Promising Oncolytic Virotherapy Agent Against Lung Cancer Stem Cells 2012
 20 S1 p. S95-
1 p.
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338 64. Genetic Correction of Dystrophin by Engineered Nucleases 2012
 20 S1 p. S26-S27
2 p.
 artikel
339 611. Genetic Modification of Cancer Cells Using Non-Viral, Episomal S/MAR Vectors for In Vivo Tumour Modelling 2012
 20 S1 p. S235-
1 p.
 artikel
340 321. Genetic Modification of Stem Cells Leads to an Enhanced Immune Response and Reduced Viral Pathogenesis upon SHIV-Challenge in the Macaque Model of AIDS 2012
 20 S1 p. S127-
1 p.
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341 757. Gene Transfer to Human Hematopoietic Cells with GaLV Pseudotyped Retroviruses Concentrated from Serum-Free Supernatants by PEG Precipitation with Polyvalent Immunoglobulin 2012
 20 S1 p. S291-S292
2 p.
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342 98. Genome Wide Characterization of Aberrant Splicing Events Induced by Lentiviral Vector Integrations 2012
 20 S1 p. S41-
1 p.
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343 153. GM-CSF Gene Therapy for Rabbit Acute Hind Limb Ischemia by Electroporation 2012
 20 S1 p. S61-S62
2 p.
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344 650. Gold Nanoparticle Mediated Gene Delivery Via Surface Charge Reversal with Pyridinium Amphiphiles 2012
 20 S1 p. S251-
1 p.
 artikel
345 326. HCV Inhibition by a Multicistronic Anti-HCV miRNA AAV Vector In Vitro and In Vivo 2012
 20 S1 p. S128-S129
2 p.
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346 389. Helper Independent Self-Inactivating Chimeric piggyBac Transposases for Genomic Targeting in Human Cells 2012
 20 S1 p. S152-
1 p.
 artikel
347 314. Hematopoietic Stem Cell Gene Therapy with Lentiviral Vector in 4 Patients with Cerebral X-Linked Adrenoleukodystrophy 2012
 20 S1 p. S124-
1 p.
 artikel
348 188. Hematopoietic Stem Cell Immunotherapy for Melanoma 2012
 20 S1 p. S74-S75
2 p.
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349 315. Hepatic Gene Transfer of TFEB Results in Clearance of Mutant alpha-1-Antitrypsin 2012
 20 S1 p. S124-
1 p.
 artikel
350 413. Hepatic Lentiviral Gene Transfer Is Associated with Mild Clonal Selection, but Not with Clonal Dominance or Tumour Formation in a Serial Transplantation Mouse Model 2012
 20 S1 p. S161-
1 p.
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351 146. Hepatocyte Therapy for MUT Methylmalonic Acidemia 2012
 20 S1 p. S59-
1 p.
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352 118. High-Efficiency Transduction of Primary Human Hematopoietic Stem Cells by Optimized AAV6 Serotype Vectors and Erythroid Lineage-Restricted Transcriptional Targeting Using the Human Parvovirus B19 Promoter 2012
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2 p.
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353 368. High-Efficiency Transduction of Primary Human Monocyte-Derived Dendritic Cells by Recombinant Adeno-Associated Virus 2 Vectors Containing Mutations in Surface-Exposed Serine and Threonine Residues 2012
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2 p.
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354 367. High-Efficiency Transgene Expression in Monocyte-Derived Dendritic (moDCs) Mediated by Recombinant Adeno-Associated Virus Vectors Containing Short Subsets of Human CD11c Promoter 2012
 20 S1 p. S144-
1 p.
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355 593. High-Efficieny Transduction of Primary Human Hematopoietic Stem Cells with Recombinant Adeno-Associated Virus Vectors at a Low Multiplicity of Infection 2012
 20 S1 p. S230-
1 p.
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356 549. High-Level Clustering of Vector Integrations in the German WAS Clinical Gene Therapy Trial 2012
 20 S1 p. S212-
1 p.
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357 519. High-Level Ectopic Expression of CFTR Imposes a Selective Disadvantage to Airway Epithelial Stem/Progenitor Cells 2012
 20 S1 p. S200-S201
2 p.
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358 63. High-Level, Long-Term Gene Expression in Mice after Hydrodynamic Delivery of Sleeping Beauty Transposon/SB100x Transposase Combinations across a Surprisingly Broad Dose Range 2012
 20 S1 p. S26-
1 p.
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359 690. High Resolution In Vivo Bioluminescent Imaging for the Study of Bacterial Vector Trafficking 2012
 20 S1 p. S267-
1 p.
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360 239. High Speed X-Ray Imaging Reveals Dosed Fluid Dynamics and Fate in Mouse Nasal and Lung Airways 2012
 20 S1 p. S94-
1 p.
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361 310. High-Throughput Gene Editing in Human Cells Enabled by Fast Ligation-Based Automatable Solid-Phase High-Throughput (FLASH) Assembly of TALENs 2012
 20 S1 p. S122-S123
2 p.
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362 573. High-Throughput Screening Identifies Effective Enhancers of Lentiviral Transduction 2012
 20 S1 p. S222-S223
2 p.
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363 109. High-Throughput Small Molecule Screen Yields Novel Classes of Compounds That Modulate Adeno-Associated Virus Transduction 2012
 20 S1 p. S45-
1 p.
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364 4. Histone Deacetylases Hinder Transgene Expression from Non-Integrating Lentiviral Vectors in Dividing and Non-Dividing Cells 2012
 20 S1 p. S2-
1 p.
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365 199. HLA Typing as an Identity Test for Patients and Their FANGTM Autologous Cancer Vaccines 2012
 20 S1 p. S78-
1 p.
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366 399. Homogeneous Reducible Polypeptides for Nucleic Acid Delivery 2012
 20 S1 p. S156-
1 p.
 artikel
367 306. Homologous-Recombination Mediated Genome Editing at the Adesonine Deaminase Locus in Patient-Derived Fibroblasts Using TAL Effector Nucleases 2012
 20 S1 p. S121-
1 p.
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368 320. HPV Specific CTLs Induced in CIN2/3 Patients after DNA Immunization Using Electroporation in a Phase I Trial 2012
 20 S1 p. S126-
1 p.
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369 124. Human Artificial Chromosome (HAC) Vector with a Conditional Centromere for Correction of Genetic Deficiencies in Human Cells 2012
 20 S1 p. S50-S51
2 p.
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370 760. Human CD20-Transduced Packaging Cell Lines Express hCD20Δ Alternative Transcripts but Produce Low Level of Retroviral Particles Carrying Spliced RNA 2012
 20 S1 p. S292-S293
2 p.
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371 497. Human Erythropoietin Gene Delivery Using an Arginine-Grafted Bioreducible Polymer System 2012
 20 S1 p. S192-S193
2 p.
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372 141. Human Versus Murine Phosphoglycerate Kinase (PGK) Promoter/Enhancer in Canine Leukocyte Adhesion Deficiency 2012
 20 S1 p. S57-
1 p.
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373 291. Human Visual Cortex Response to Retinal Gene Therapy Re-Administration 2012
 20 S1 p. S114-S115
2 p.
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374 489. Humoral Tolerance to FVIII in Hemophilia A Mice Using Cytokine-Conditioned Dendritic Cells 2012
 20 S1 p. S190-
1 p.
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375 148. Hydrodynamic Gene Transfer of a Cox-1/ Prostacyclin Synthase Fusion Protein Results in Endogenous Production of Supra-Therapeutic Levels of Prostacyclin in Rats 2012
 20 S1 p. S59-S60
2 p.
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376 346. Identification of a Domain Responsible for the Dose-Dependent Antiproliferative and Apoptotic Effects of Sleeping Beauty Transposase 2012
 20 S1 p. S136-
1 p.
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377 297. Identification of a Novel Small Molecule Inhibitor of FX-Mediated Ad5 Gene Transfer for Gene Therapy Applications 2012
 20 S1 p. S117-
1 p.
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378 183. Identification of Decorin Derived Peptides with a Zn2+ Dependent Anti-Myostatin Activity 2012
 20 S1 p. S73-
1 p.
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379 94. Identification of Novel Cardioprotective Factors by In Vivo Functional Gene Selection Using AAV Vectors 2012
 20 S1 p. S39-
1 p.
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380 105. Identification of Novel Genes Regulating AAV Transduction by High-Throughput, Genome-Wide siRNA Screening 2012
 20 S1 p. S44-
1 p.
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381 9. Identification of the Galactose Binding Domain of the AAV9 Capsid 2012
 20 S1 p. S4-
1 p.
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382 567. Identifying Molecular Targets for the Rejuvenation of Aged Muscle Stem Cells 2012
 20 S1 p. S220-
1 p.
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383 76. Identifying Motor Neuron Transduction Efficiencies That Are Efficacious in SMA Mice and Achievable by Intrathecal Delivery in a Large Animal Model 2012
 20 S1 p. S31-
1 p.
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384 619. IL30 — A Novel Cytokine Candidate for Prevention and Treatment of Biological Therapy-Induced Liver Injury and Hepatitis 2012
 20 S1 p. S238-
1 p.
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385 485. Illumina Platform Sequencing Provides Adequate Read Lengths To Map Lentiviral Vector Insertion Sites in Human Cells and Uncovers Both Mis-Mapped and False Positive Reads from Traditional LAM-PCR and nrLAM-PCR Products 2012
 20 S1 p. S188-
1 p.
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386 89. Image-Guided, Lobe-Specific Hydrodynamic Gene Delivery to Baboon Liver 2012
 20 S1 p. S37-
1 p.
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387 755. Immobilized Colanic Acid Degrading Enzyme Reactor Chromatography and Its Application in SuperClean Therapeutic Plasmid DNA Production 2012
 20 S1 p. S291-
1 p.
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388 520. Immortalized Adults Human Neural Stem Cells Differentiate into Functional Neurons after Transplantation into the Mouse Rat Brain with Intracerebral Hemorrhage 2012
 20 S1 p. S201-
1 p.
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389 68. Immune Responses to Factor VIII Following Overexpression by Liver-Directed AAV Gene Therapy Do Not Correlate with Hepatic Cellular Stress Markers 2012
 20 S1 p. S28-
1 p.
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390 452. Immunogenicity of an Engineered HIV-1 Clade a Consensus-Based Envelope DNA Vaccine 2012
 20 S1 p. S175-S176
2 p.
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391 671. Immunological Response to CD40L Coding, Replicating and Non-Replicating Adenoviruses 2012
 20 S1 p. S259-
1 p.
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392 697. Immunomodulatory Transgene Armed Oncolytic Measles Virus Induces Anti-Tumor Immunity 2012
 20 S1 p. S269-
1 p.
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393 644. Impact of Novel Biologically Active Chromophores on Common Bioassays 2012
 20 S1 p. S248-
1 p.
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394 255. Impact of Pre-Existing Neutralizing Antibodies (NAbs) on Expression of a SIV Antibody Following Intramuscular (IM) Administration of AAV2/8 2012
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2 p.
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395 128. Implementation of a Nuclear Factor Kappa B DNA Nuclear Targeting Sequence Improves In Vitro Suicide Gene Therapy Efficacy in Both Small- and Non-Small Cell Lung Cancer Cell Lines 2012
 20 S1 p. S52-
1 p.
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396 702. Improved Antitumor Effect of Adenovirus-Mediated Interferon Therapy in Combination with Chemoradiotherapy in a Syngeneic Immunocompetent Hamster Model 2012
 20 S1 p. S271-
1 p.
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397 170. Improved Neuroplasticity and Decreased Apoptosis by Intralesional Transplantation of Mesenchymal Stem Cells after Severe Spinal Cord Injury in Rats 2012
 20 S1 p. S68-
1 p.
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398 39. Improved Repair of Equine Articular Cartilage 8 Weeks Following Implantation of Chondrocytes Transduced with rAAV5-IGF-1 2012
 20 S1 p. S16-
1 p.
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399 424. Improving Axon Growth of Transected Spinal Cord Using Multichannel Collagen Conduits Carrying NT-3 Gene 2012
 20 S1 p. S165-S166
2 p.
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400 541. Improving the Efficacy of Adoptive T Cell Therapy by Combination with Viro-/Immuno-/ Radio-Therapy 2012
 20 S1 p. S209-
1 p.
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401 375. Incorporation of Pseudomonas aeruginosa Epitope in Novel Adenovirus Fiber Loops To Circumvent Anti-Adenovirus Immunity and To Induce Protective Immunity 2012
 20 S1 p. S147-
1 p.
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402 136. Increased Frequency of Permanent Integration Following Liver-Directed Gene Therapy with rDNA-AAV2/8 In Murine Phenylketonuria 2012
 20 S1 p. S55-
1 p.
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403 168. Increased Longevity of Rescue of Light-Induced Retinal Damage in an Adult Mouse Using Peptide for Ocular Delivery (POD) as a Gene Transfer Vector 2012
 20 S1 p. S67-S68
2 p.
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404 178. Increased Overexpression of Human Alpha7 Integrin as a Potential Therapy for Duchenne Muscular Dystrophy 2012
 20 S1 p. S71-S72
2 p.
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405 52. Increases in CD4 Counts and Effects on HIV in Aviremic HIV-Infected Subjects Infused with Zinc Finger Nuclease (ZFN) CCR5 Modified Autologous CD4 T-Cells (SB-728-T) 2012
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2 p.
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406 218. Inducible Caspase 9 as Safety Switch in Gene Therapies Targeting Hematopoietic Stem Cells 2012
 20 S1 p. S85-S86
2 p.
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407 725. Induction of CD4+CD25+ T Cells and Control of Cardiac Allograft Rejection by CD40 RNAi in Mice 2012
 20 S1 p. S280-
1 p.
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408 536. Infusion of CD19-Directed/Multivirus-Specific CTLs Post HSCT for B Cell Malignancies 2012
 20 S1 p. S207-
1 p.
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409 482. Inhibition of Breast Tumor Growth by Adenoviral-Mediated p16 Gene Transfer Via Combined Effects of Cell Cycle Arrest, Senescence and Apoptotic Induction, and Angiogenesis Inhibition 2012
 20 S1 p. S187-
1 p.
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410 478. Inhibition of Metastasis from Targeted Interleukin 12 Immunotherapy and Revelation of the Mechanism by Cell Profiling 2012
 20 S1 p. S185-S186
2 p.
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411 657. In-Mouse Propagation of Hemophilic Hepatocytes toward Gene Correction and Cell Therapy 2012
 20 S1 p. S254-
1 p.
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412 258. Innate Immune Response Affects AAV-Mediated Hepatic Trangene Expression 2012
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2 p.
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413 580. Insight into the Mechanism of Increased Transduction of AAV Vectors with Ad Proteins E1B55k/E4orf6 and Generalization to Other Substrates of the Cellular DNA Damage Response Pathway 2012
 20 S1 p. S225-
1 p.
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414 65. Integration of ß-Globin Expressing Lentiviral Vectors in the Human Genome Induces Alternative Splicing and the Generation of Aberrant Transcripts 2012
 20 S1 p. S27-
1 p.
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415 583. Integration Site Analysis Following Transduction with the Novel Recombinant AAVHSC15 Reveals Trends in Proviral-Chromosome Junction Formation 2012
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1 p.
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416 50. Integration Site Analysis in a Clinical Trial of Lentiviral Vector-Based HSC Gene Therapy for MLD Shows High Levels of Polyclonal Hematopoietic Reconstitution and No Signs of Genotoxicity at One Year after Transplant 2012
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417 553. Integration Site Analysis Indicates Decade-Long Safety of Gammaretroviral-Modified Chimeric Antigen Receptor T-Cells 2012
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418 220. Integration Site Analysis of Wiskott-Aldrich Syndrome Patients Treated with Lentiviral Vector Gene Therapy 2012
 20 S1 p. S86-
1 p.
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419 316. Integration Site Distribution of Lentiviral Vector in Gene Therapy for X-Adrenoleukodystrophy 2012
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2 p.
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420 562. Interactions of Adenovirus Vectors with Coagulation Factor X and Natural Antibodies: Lack of an Absolute Requirement for Factor X in Liver Transduction by Adenovirus Vectors 2012
 20 S1 p. S218-
1 p.
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421 686. Intercellular Transfer of microRNAs Via Tumor Microvesicles 2012
 20 S1 p. S265-
1 p.
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422 156. Interleukin-35 Gene Therapy Alleviated Cardiac Allograft Rejection in Mice 2012
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2 p.
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423 622. Intranasal Delivery of HMGB1 Inhibitory Heptamer Peptides Confers Robust Neuroprotection in the Postischemic Brain 2012
 20 S1 p. S239-
1 p.
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424 432. Intraocular Gene Therapy with Erythropoietin: Identification of Therapeutic Doses 2012
 20 S1 p. S168-
1 p.
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425 526. Intravasuclar Delivery of RAAVRH.8 Generates Widespreading Transduction of Neuronal and Glial Cell Types in the Adult Mouse Central Nervous System 2012
 20 S1 p. S203-
1 p.
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426 623. Intravenous PMO Delivery System with Bubble Liposomes and Ultrasound Exposure into Skeletal Muscles of the mdx Mice 2012
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2 p.
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427 164. In Utero Brain-Directed AAV5 Gene Therapy Results in Rapid, Robust, and Specific Transduction of Choroid Plexus Epithelia: Implications for Rescue of Prenatal Lethal Mouse Models of Neurometabolic Disease 2012
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1 p.
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428 147. In Vitro and In Vivo Delivery of Surface Immobilized AAV-2/9 to Arterial Cells 2012
 20 S1 p. S59-
1 p.
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429 663. In Vitro Characterization of the Anti-Viral Activity of TT-034, a RNAi-Therapeutic Against the Hepatitis C Virus 2012
 20 S1 p. S256-
1 p.
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430 286. In Vivo and In Vitro Characterization of Early Hepatocytes Derived from Human Parthenogenetic Stem Cells 2012
 20 S1 p. S113-
1 p.
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431 6. In Vivo Gene Delivery to the Striatum Using a Novel Entry-Targeted Lentivirus: An Entry Restricted Lentivirus Vector for Neurodegenerative Diseases 2012
 20 S1 p. S3-
1 p.
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432 119. In Vivo Gene Delivery Using Microvesicle-Associated AAV 2012
 20 S1 p. S49-
1 p.
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433 139. In Vivo Gene Transfer of Different Isoforms of the MeCP2 (Rett Syndrome) Gene Is Associated with Very Different Toxicity 2012
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2 p.
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434 15. In Vivo Knock-Down of MRN Complex Members Improves Liver and Cardiac Transduction with AAV Vectors 2012
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2 p.
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435 5. In Vivo Mouse Models for Vector Genotoxicity Testing and Lentiviral Vector-Based Cancer Gene Discovery 2012
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2 p.
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436 395. In Vivo mRNA Delivery to Central Nervous System Using Polyplex Nanomicelles 2012
 20 S1 p. S154-
1 p.
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437 292. In Vivo Nanoparticle Delivery for Site-Specific Genome Editing of Hematopoietic Cells in a Humanized Mouse 2012
 20 S1 p. S115-
1 p.
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438 741. In Vivo Real-Time Imaging of Cell Dynamics in Tissues of a Living Mouse by Confocal Microscope with the Suction Device 2012
 20 S1 p. S286-
1 p.
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439 122. In Vivo Selection of Hepatocytes Engineered To Express CrmA Using the Sleeping Beauty Transposon System 2012
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1 p.
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440 19. In Vivo Structure-Activity Relationships for PEGylated Polyacridine Peptide Polyplexes 2012
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1 p.
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441 522. Isolation and Culture of Neuronal Stem Cells Which Directed into Purkinje Cells To Be Used for Brain Damage and Epilepsy Treatment in Mice 2012
 20 S1 p. S201-S202
2 p.
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442 KEYWORD INDEX 2012
 20 S1 p. S309-S322
14 p.
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443 544. Kinetic Analysis of Oncolytic Virus Spread through Large Lymphoid Tumors after Systemic Administration 2012
 20 S1 p. S210-
1 p.
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444 474. Lanatoside C Enhances the Therapeutic Efficacy of Secreted TRAIL Expressed by Human Neural Stem Cells in an Orthotopic Invasive Primary Glioblastoma Model 2012
 20 S1 p. S184-
1 p.
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445 761. Large-Scale cGMP Manufacture of a Plasmid Vector for Cystic Fibrosis Gene Therapy Clinical Trials 2012
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1 p.
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446 487. Large-Scale Expansion of Functional Regulatory T Cells Using a Gas-Permeable Rapid Expansion Cultureware (G-Rex) 2012
 20 S1 p. S189-
1 p.
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447 386. Large-Scale Library Production Provides New Insight into Zinc Finger Specificity 2012
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1 p.
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448 578. Large-Scale Production of a Maraba-Based Oncolytic Virus 2012
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1 p.
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449 325. Lentiviral Gene Therapy Against HIV-1 Using a Novel TRIM21-Cyclophilin A Fusion Restriction Factor 2012
 20 S1 p. S128-
1 p.
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450 488. Lentiviral Gene Therapy for X-SCID Using HSCs Mobilized by Treatment with G-CSF and AMD 3100 2012
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2 p.
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451 1. Lentiviral Vector-Based Insertional Mutagenesis Identifies New Clinically Relevant Cancer Genes Involved in the Pathogenesis of Hepatocellular Carcinoma 2012
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452 237. Lentiviral Vector Gene Transfer to Porcine Sinus and Pulmonary Airways 2012
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1 p.
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453 223. Lentiviral Vector Mediated Gene Therapy for X-Linked Lymphoproliferative Disease Restores Humoral and Cellular Functions 2012
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2 p.
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454 345. Lentiviral Vectors Targeting Human T Cells for RNAi-Mediated Gene Therapy of HIV Infection 2012
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1 p.
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455 547. Lentiviral Vector Transduced CD34+ Cells for the Treatment of Wiskott-Aldrich Syndrome 2012
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2 p.
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456 500. Light-Inducible Spatiotemporal Gene Regulation Using Engineered Transcription Factors 2012
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2 p.
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457 114. Limitations of Encapsidation of Recombinant scAAV2 Genomes in Different Serotype Capsids and Their Quantitation 2012
 20 S1 p. S47-
1 p.
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458 601. Linearized Oncolytic Adenoviral Plasmid DNA Delivered by Bioreducible Polymers 2012
 20 S1 p. S232-
1 p.
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459 704. Linking Epigenetics and Gene Therapy: Enhanced Replication and Therapeutic Effect of a CRAd by Placing a Nucleosome Positioning Sequence Upstream of a Tumor Specific Promoter 2012
 20 S1 p. S272-
1 p.
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460 151. Liposomal Surface Coatings of Metal Coronary Artery Stents for Efficient Non-Viral Gene Delivery to the Injured Vasculature 2012
 20 S1 p. S60-S61
2 p.
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461 313. Liver-Directed Gene Therapy for Mucopolysaccharidosis Type I (MPS I) 2012
 20 S1 p. S123-S124
2 p.
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462 558. Liver-Directed Gene Transfer for the Induction of Antigen-Specific Tolerance: Mechanism and Potential Therapeutic Applications 2012
 20 S1 p. S216-
1 p.
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463 548. Liver Gene Therapy by Lentiviral Vectors Allows Partial Correction of Two Hemophilia B Dogs and Revert Pre-Existing Anti-Transgene Immunity in Mice 2012
 20 S1 p. S212-
1 p.
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464 138. Liver Gene Therapy for PKU Using Naked DNA/Minicircle Vectors Expressing Phenylalanine Hydroxylase from a Synthetic Minigene 2012
 20 S1 p. S56-
1 p.
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465 38. Local Downregulation of Pre-B Cell Colony-Enhancing Factor (PBEF)/Visfatin Using an AAV5 Vector Encoding a Specific Small Hairpin RNA for PBEF Results in Amelioration of Arthritis 2012
 20 S1 p. S15-S16
2 p.
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466 600. Local Sustained Delivery of Oncolytic Adenovirus with Injectable Alginate Gel for Cancer Virotherapy 2012
 20 S1 p. S232-
1 p.
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467 749. Long-Term Cultured Human Term Placenta-Derived Mesenchymal Stem Cells (MSC) of Maternal Origin Displays Plasticity 2012
 20 S1 p. S289-
1 p.
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468 90. Long-Term Elimination of Human Hepatitis C Virus in Human Hepatocyte Chimeric Mice after Single Administration of Plasmid DNA Expressing Human Interferon-γ 2012
 20 S1 p. S37-
1 p.
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469 652. Long-Term Follow-Up of Hemophilia A Dogs for 2-7 Years Demonstrates Sustained Factor VIII Expression after AAV-Mediated Delivery 2012
 20 S1 p. S252-
1 p.
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470 159. Long-Term Rescue by AAV-Delivered Therapy in Autosomal Dominant Retinitis Pigmentosa (ADRP) Mice 2012
 20 S1 p. S64-
1 p.
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471 40. Long-Term Results of a Double-Blind, Placebo-Controlled, Multicenter Study Evaluating the Safety and Potential Activity of Escalating Doses of hMaxi-K Gene Transfer in Female Participants with Overactive Bladder and Detrusor Overactivity 2012
 20 S1 p. S16-
1 p.
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472 55. Long-Term Transgene Expression and Biological Effect Following IM Administration of AAV1-LPLS447X to LPL Deficient Patients 2012
 20 S1 p. S23-
1 p.
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473 624. Long Term Transgene Expression in Rat Liver Using a Novel Electromotor-Driven Hydrodynamic Gene Injector 2012
 20 S1 p. S240-
1 p.
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474 724. Lung Tumor Metastasis Inhibition with Modified siRNA Targeting Cell Cycle 2012
 20 S1 p. S280-
1 p.
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475 574. Magnetic Colocalization of Viral Vectors and Target Cells Improves Transduction Efficiency in Human Hematopoietic Cells 2012
 20 S1 p. S223-
1 p.
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476 605. Magnetic Nanoparticle Uptake and Gene Delivery for Magnetically Guided Endothelial Cell Delivery 2012
 20 S1 p. S233-S234
2 p.
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477 235. Manipulation of Airway Epithelia To Improve siRNA Delivery and RNAi Efficacy 2012
 20 S1 p. S92-S93
2 p.
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478 571. Manufacture of Clinical-Grade Lentiviral Vectors for Ex Vivo Use 2012
 20 S1 p. S222-
1 p.
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479 17. Mass Spectrometry Identification of Proteins That Bind to Trafficking Plasmids during Transfection 2012
 20 S1 p. S7-
1 p.
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480 688. Matrix Metalloproteinase Responsive, Proximity-Activated Targeting Polymeric Nanoparticles for siRNA Delivery to Tumor Metastases 2012
 20 S1 p. S266-
1 p.
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481 592. Mechanism of Transduction of Human Hematopoietic Cells by Recombinant AAV6 Vectors 2012
 20 S1 p. S229-S230
2 p.
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482 565. Mechanisms of Stem Cell Therapy in Cystinosis Treatment 2012
 20 S1 p. S219-
1 p.
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483 546. Mesenchymal Stromal Cells Are Promising Candidates as Delivery Vehicles for Systemic Oncolytic Measles Virotherapy in Models of Acute Lymphoblastic Leukaemia 2012
 20 S1 p. S211-
1 p.
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484 12. Microfluidic Live-Neuron Tracking of AAV9 Axonal Transport within the Endosomal System 2012
 20 S1 p. S5-
1 p.
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485 41. microRNA 126 Is a New Regulator of Hematopoietic Stem Cells Homeostasis 2012
 20 S1 p. S17-
1 p.
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486 106. microRNA Regulated Cardiotropic AAV Vectors with Skeletal Muscle and Liver Specific Suppression of Transgene Expression 2012
 20 S1 p. S44-
1 p.
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487 206. microRNA-Sensitive and Armed Oncolytic Measles Virus for Therapy of Pancreatic Cancer 2012
 20 S1 p. S81-
1 p.
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488 210. Midkine Promoter-Driven Oncolytic Adenovirus with Ad35 Fiber Modification Achieves Enhanced Transduction of Human Malignant Mesothelioma Cells In Vitro and In Vivo 2012
 20 S1 p. S82-
1 p.
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489 563. miR-126 Controls Hematopoietic Stem Cell Proliferation by Regulating PI3K/AKT Signaling 2012
 20 S1 p. S218-
1 p.
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490 414. Mobilization of Hematopoietic Stem Cells with Plerixafor or Plerixafor+G-CSF for Human Gene Therapy of Thalassemia 2012
 20 S1 p. S161-S162
2 p.
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491 670. Modeling Pre-Existing Immunity to Adenovirus in Rodents: Immunological Requirements for Successful Development of an Ad5-Based Ebola Vaccine 2012
 20 S1 p. S258-S259
2 p.
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492 20. Modified HK siRNA Polyplexes with Improved Pharmacokinetics Enhance Tumor Inhibition 2012
 20 S1 p. S8-
1 p.
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493 689. Modulating Cancer Progression with Zymogen Protein C in a Murine Model 2012
 20 S1 p. S266-S267
2 p.
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494 445. Modulating Myoblast Differentiation for Improved Engraftment Potential 2012
 20 S1 p. S173-
1 p.
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495 208. Modulation of Complement System for Enhancing Oncolytic Vaccinia Virus-Mediated Cancer Therapy 2012
 20 S1 p. S81-S82
2 p.
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496 705. Molecular and Immunological Complementation between Oncolytic Adeno- and Vaccinia Virus: Paving the Way for Next Generation Cancer Therapy 2012
 20 S1 p. S273-
1 p.
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497 93. Molecular Cardiac Surgery Mediated ssAAV1-SERCA2a Gene Therapy Restores Global and Regional Contractility in Ovine Ischemic Cardiomyopathy 2012
 20 S1 p. S38-S39
2 p.
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498 27. More Pleiades MiniPromoters for the Brain and Eye 2012
 20 S1 p. S11-
1 p.
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499 723. Multifunctional Lipid-Polymer Nanoparticles for Enhanced Serum Stability and Intracellular Delivery of Oligonucleotides 2012
 20 S1 p. S279-
1 p.
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500 692. Multi-Optimization and Image-Aided In Vivo Evaluation of Adenovirus Containing Multi-Targeting Devices for Hepatocellular Carcinoma 2012
 20 S1 p. S268-
1 p.
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501 477. Multipotent VΔ2-Negative γΔT-Cells after CMV-Reactivation in Allogeneic Stem Cell Transplantation 2012
 20 S1 p. S185-
1 p.
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502 172. Muscle Force Improvement by Long-Term Systemic Expression of an AAV9 Minidystrophin after Delivery in Young Adult GRMD Dogs without Immune Suppression 2012
 20 S1 p. S69-
1 p.
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503 673. Myeloid Derived Suppressor Cells in Glioma Differentiate towards an Antigen Presenting Cell Phenotype upon Interleukin-12 Vector Based Immunotherapy 2012
 20 S1 p. S260-
1 p.
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504 186. Myogenic Transduction and Cell Surface Marker Selection of DMD Fibroblasts Enable Stable Dystrophin mRNA Expression for Exon Skipping Assay 2012
 20 S1 p. S74-
1 p.
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505 192. Naive-Derived Memory Stem T Cells: A Novel Promising Platform for Cancer Immune-Gene Therapy 2012
 20 S1 p. S76-
1 p.
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506 261. Nanoparticles as Delivery Systems for Antisense Oligoribonucleotides Aimed at Exon Skipping: Results in the Dystrophinopathic mdx Animal Model by Intraperitoneal Ad Oral Administration Routes 2012
 20 S1 p. S102-S103
2 p.
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507 265. Nanoparticles with Triplex-Forming Oligonucleotides for Site-Specific Editing of the Human Cystic Fibrosis Transmembrane Receptor Gene 2012
 20 S1 p. S104-
1 p.
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508 165. Natural Killer Cells for Therapy of Neural Tumors 2012
 20 S1 p. S66-S67
2 p.
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509 103. Nectin-4 Is the Measles Virus Host Exit Receptor: Implications for Other Respiratory Infections and for Oncolysis 2012
 20 S1 p. S43-
1 p.
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510 596. Negative Regulation-Resistant p53 Variant Enhances Oncolytic Adenoviral Gene Therapy 2012
 20 S1 p. S231-
1 p.
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511 137. Neonatal Gene Therapy for OTC Deficiency 2012
 20 S1 p. S56-
1 p.
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512 155. Neutralizing Antibodies Against AAV Serotypes 1, 2, 6 and 9 in Sera of Commonly Used Animal Models and Their Significance for In Vivo Experiments 2012
 20 S1 p. S62-
1 p.
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513 342. New Approaches for Targeted Delivery of Dicer-Substrate siRNA 2012
 20 S1 p. S134-
1 p.
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514 327. New Safety and Efficacy Data of a Phase 1-2 Study in Patients with Advanced Renal Cell Carcinoma, Following Vaccination with Fourfold Gene-Modified, Allogeneic Tumor Cells Combined with a DNA-Based Immunomodulator 2012
 20 S1 p. S129-
1 p.
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515 735. nNOS Short Hairpin RNA Expression Vector To Reduce the Glioma Cells Viability 2012
 20 S1 p. S283-
1 p.
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516 734. nNOS shRNA Expression Vector in Combination with Interferon Gamma To Reduce the Viability of Human Glioma Cell Lines 2012
 20 S1 p. S283-
1 p.
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517 721. Non-Contact Helium Based Plasma for the Efficient Delivery of DNA Vaccines 2012
 20 S1 p. S278-S279
2 p.
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518 390. Non-Integrating Lentiviral Vectors for Efficient and Transient Delivery of Zinc Finger Nucleases and Donor Constructs for Site-Specific Gene Correction 2012
 20 S1 p. S152-S153
2 p.
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519 417. Non-Invasive Monitoring of Insulin-Producing Cells In Vivo with Viral Vectors 2012
 20 S1 p. S163-
1 p.
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520 627. Non-Invasive, Multimodal Imaging of Microvesicles with Metabolically Biotinylated, Membrane-Bound Gaussia Luciferase 2012
 20 S1 p. S241-
1 p.
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521 29. Noninvasive, Quantitative Imaging of Vector-Mediated D2R80A Reporter Gene Expression in the Living Animal Brain 2012
 20 S1 p. S12-
1 p.
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522 32. Normalized Survival and Permanent Restoration of NAGLU Activity in the CNS, PNS and Somatic Tissues in MPS IIIB Mice after a Single Intravenous rAAV9-hNAGLU Gene Delivery 2012
 20 S1 p. S13-
1 p.
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523 125. Novel Antitumor Strategy by Transfection of Plasmids Encoding Pathogenic Antigen- and Cytokine-Genes 2012
 20 S1 p. S51-
1 p.
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524 298. Novel CpG-Rich Oncolytic Adenovirus Backbone To Stimulate Tumor-Specific Immune Response and Block the Suppression of Myeloid-Derived Suppressive Cells 2012
 20 S1 p. S118-
1 p.
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525 660. Novel GNE Mutations in Patients with Autosomal Recessive Hereditary Inclusion Body Myopathy 2012
 20 S1 p. S255-
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526 412. Novel Nanoparticles To Encapsulate microRNA for the Treatment of Stroke 2012
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2 p.
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527 202. Novel Oncolytic HSV-1 for the Treatment of Prostate Carcinoma with Improved Efficacy Independent of Tumor Growth Rate 2012
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2 p.
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528 359. Novel, Shuffled, Human-Specific rAAV Vectors 2012
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2 p.
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529 714. Novel Strategies To Modulate Pre-Existing Anti-Factor VIII Immune Responses in Hemophilia A Inhibitor Mice Treated with Factor VIII Plasmid-Mediated Gene Therapy 2012
 20 S1 p. S275-S276
2 p.
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2 p.
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532 604. Oncolytic Herpes Simplex Virus Shows Synergistic Effects with Rapamycin Against Triple-Negative Breast Cancer 2012
 20 S1 p. S233-
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533 540. Oncolytic Properties of a Vesicular Stomatitis/Measles Virus Hybrid 2012
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534 706. Oncolytic Vaccinia Virus Armed with GM-CSF: Studies on Safety, Efficacy, Anti-Viral and Anti-Tumor Immune Response in Immunocompetent and Immunodeficient Rodents 2012
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535 708. Oncolytic Vaccinia Viruses Deleted in the Gene Encoding the Small Subunit of Ribonucleotide Reductase for the Treatment of Bladder Cancer 2012
 20 S1 p. S274-
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536 696. Oncolytic Vaccinia Virus Infection of Tumor Vasculature in a Window-Chamber Tumor Model 2012
 20 S1 p. S269-
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537 630. Optimal Electrogene Transfer Method for Human Mesenchymal Stem Cells 2012
 20 S1 p. S242-S243
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538 656. Optimisation and Validation of Protocols for Vector Detection in Circulation 2012
 20 S1 p. S253-
1 p.
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539 608. Optimisation of the ‘FMDV’ 2A Co-Expression System for Gene Therapies 2012
 20 S1 p. S234-S235
2 p.
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540 496. Optimised Factor VIII Vectors for Gene Therapy of Haemophilia A 2012
 20 S1 p. S192-
1 p.
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541 631. Optimization of Electroporation-Enhanced Intradermal Delivery of DNA Vaccine Using a Minimally Invasive Device 2012
 20 S1 p. S243-
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542 370. Optimization of Kidney-Targeted Gene Delivery for Cystinosis Using AAV 2012
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1 p.
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543 584. Optimization of rAAV for Anti-Glioma Therapy 2012
 20 S1 p. S226-S227
2 p.
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544 344. Optimization of the MCM7 miRNA Cluster as a Novel Platform to Multiplex Small Interfering and Nucleolar RNAs for Combinational HIV-1 Gene Therapy 2012
 20 S1 p. S135-
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545 641. Optimizing Gene Delivery Properties of PEGylated Polyacridine Peptides through Sequence Specific Structure Activity Relationships 2012
 20 S1 p. S247-
1 p.
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546 575. Optimizing the Manufacture of CAR-T Cells for Clinical Applications 2012
 20 S1 p. S223-
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547 150. Osteopontin Treated Circulating Angiogenic Cells Enhance Functional Recovery in a SCID Model of Hindlimb Ischemia 2012
 20 S1 p. S60-
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548 82. Overcoming Tumor Immune Escape Using Bi-Specific CAR T Cells 2012
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549 693. Over-Expression of miR-145 Enhances the Effectiveness of HSVtk Gene Therapy for Malignant Glioma 2012
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550 78. Overexpression of Non-Aggregatable Alpha-Synuclein Protects Against Human Wildtype Alpha-Synuclein Mediated Toxicity 2012
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551 79. Overexpression of the NDUFA6 Subunit of Complex I Ameliorates Neurodegeneration in Experimental Optic Neuritis 2012
 20 S1 p. S32-S33
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552 70. Pancreatic Gene Delivery for Diabetes Therapy 2012
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553 440. Pathogenesis of Lumbar Spine Disease in Mucopolysaccaridosis and Response to Neonatal Gene Therapy 2012
 20 S1 p. S171-
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554 524. Patterns of scAAV Vector Genome Insertion Associated with Oncogenic Events in a Mouse Model for Genotoxicity 2012
 20 S1 p. S202-
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555 410. pDMAEMA-Based Polyplexes as Vectors for Retinal Gene Therapy 2012
 20 S1 p. S160-
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556 763. Peak Supply: Implications of Serum and Consumable Availability for Clinicians, Researchers, and Commercial Translation 2012
 20 S1 p. S293-S294
2 p.
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557 632. PEG Length and Linkage Dramatically Influence PEGylated Polyacridine Peptide DNA Polyplex Pharmacokinetics and Hydrodynamically-Stimulated Gene Expression 2012
 20 S1 p. S243-
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558 216. PEGylation of Vesicular Stomititis Virus (VSV) Extends Virus Persistence in Blood in the Presence of Neutralizing Antibodies 2012
 20 S1 p. S85-
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559 405. Pendant Polymer:Amino-β-Cyclodextin Guest:Host Complexes as Safe and Efficient Vectors for Nucleic Acid Delivery 2012
 20 S1 p. S158-
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560 13. Peri-Nuclear Accumulation of Adeno-Associated Virus: A Novel Barrier Limiting AAV Transduction? 2012
 20 S1 p. S5-S6
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561 110. Persistent Transgene Expression from AAVHSC15 in Mice Pre-Treated with High Dose Human IVIG 2012
 20 S1 p. S46-
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562 752. Pharmacokinetic-Guided Delivery of Mesenchymal Stem Cells 2012
 20 S1 p. S290-
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563 556. Pharmacological Modulation of Humoral Immunity in a Non-Human Primate Model of AAV Gene Transfer for Hemophilia B 2012
 20 S1 p. S215-
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564 143. Pharmacological Read-Through of Nonsense ARSB Mutations as a Potential Therapeutic Approach for Mucopolysaccharidosis VI 2012
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565 711. Phase II 2:1 Randomized Adjuvant Study of the “Triad” Autologous (FANG™) Vaccine, Incorporating Bifunctional shRNAfurin and GMCSF Transgene Expression, in Stage IIIc Ovarian Epithelial Carcinoma: Preliminary Data 2012
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566 336. Phase II Study of FANG™ (Autologous Tumor Cell — GMCSF/pbi-shRNA™ Furin DNA Plasmid) Vaccine in Advanced Melanoma 2012
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567 264. Phase I Study of pbi-shRNA™ STMN1 Bilamellar Invaginated Vesicle (BIV) Lipoplex (LP) Via Intratumoral Injection in Advanced Cancer 2012
 20 S1 p. S104-
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568 331. Phase I Study of the “Triad” Autologous (FANG™) Vaccine, Incorporating Bifunctional shRNAfurin and GMCSF Transgene Expression, in Advanced Cancer Patients 2012
 20 S1 p. S130-S131
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569 319. Phase I Study To Improve Virus-Specific Immune Reconstitution after Cord Blood Transplantation Using Cord Blood-Derived Virus-Specific T Cells 2012
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570 717. Phase I Trial of Escalating Doses of SGT-53 Infusion in Combination with Taxotere in Advanced Solid Tumor Patients 2012
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571 212. Phase I Trial of Intratumoral (IT) Administration of HF10, a Replication-Competent Herpes Simplex Virus Type 1, in Patients with Refractory Superficial Cancer 2012
 20 S1 p. S83-
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572 543. Phase 1 Study of CG0070, a GM-CSF Expressing Oncolytic Adenovirus, in Non-Muscle Invasive Bladder Cancer 2012
 20 S1 p. S210-
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573 559. Phase 1 Study of HSVTK-CD34 Modified T Cells Therapy Following Haematopoietic Stem Cell Transplantation (HSCT) without Serotherapy 2012
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574 645. Phosphonium-Containing Macromolecules for Nonviral Gene Delivery 2012
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2 p.
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575 407. Physical and Transfection Properties of Non-Viral Gemini Surfactant-Phospholipid Nanoparticles 2012
 20 S1 p. S159-
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576 505. Physiological Regulation of Transgene Expression by a Lentiviral Vector Containing the A2UCOE Linked to a Myeloid Promoter 2012
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577 457. P140K-Mediated In Vivo Selection Strategies Combining AMD3100 with O6-Benzylguanine and BCNU Significantly Enhances Selection of Gene-Modified T Lymphocytes 2012
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578 426. Placental Growth Factor-2 Gene Transfer by Electroporation Improves Diabetic Sensory Neuropathy in Mice 2012
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579 24. Pluronic Block Copolymer as a Potential Gene Delivery Candidate 2012
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580 404. Polyacridine Octreotide Peptides for Targeted Gene Delivery 2012
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583 262. Preclinical Biodistribution, Toxicology and Survival Assessments for the Administration of pbi-shRNA™ STMN1 Lipoplex 2012
 20 S1 p. S103-
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584 215. Preclinical Development of ORCA-010, a Novel Potency-Enhanced Oncolytic Adenovirus 2012
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585 609. Preclinical Evaluation of Bifunctional Short Hairpin RNAs (shRNA) Against Steroid Receptor Coactivator-3/Amplified in Breast Cancer 1 (SRC-3) and Steroid Receptor Coactivator-1 (SRC-1) in Breast Cancers 2012
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586 117. Pre-Existing Neutralizing Antibodies to AAV2 and AAV5 in the Serum and Synovial Fluid of 20 Horses 2012
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587 679. Preliminary Safety Results from the IMPACT Study — A Phase 2-3 Clinical Study in Patients with Advanced Colorectal Carcincoma with the Immunomodulator MGN1703 2012
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588 30. Presymptomatic Gene Therapy Cures Feline GM1 Gangliosidosis 2012
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589 259. Prevalence and Correlation of Neutralizing Antibodies Against AAV2, 7, 8, 9 and RH32.33 in the Human Sera from Southern China 2012
 20 S1 p. S102-
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590 132. Prevention of Hepatocellular Adenoma and Correction of Metabolic Abnormalities in Murine Glycogen Storage Disease Type Ia by Gene Therapy 2012
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591 740. Prevention of Radiation-Induced Lung Injury by Administration of Gene-Modified Mesenchymal Stem Cells 2012
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592 590. Primary Human Keratinocyte-Selective AAV Targeting Vectors 2012
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593 149. Process Development for Manufacture of hES Cell-Derived Cardiomyocytes 2012
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594 483. Production and Evaluation of Lenti-hWASP-Vectors for Wiscott Aldrich Syndrome 2012
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595 157. Progeny of Pronuclear Injections of Mutant Human Mitochondrial Genes 2012
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596 127. PROGNOSE: An Online Tool for Predicting and Analyzing the Off-Target Site Effects of Designer Nucleases 2012
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597 743. Proliferation and Multilineage Differentiation Potential of Adipose-Derived Stem Cells Isolated from Dystrophin and Utrophin Knockout Mice 2012
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598 653. Proliferative Endothelial Progenitors as a Therapeutic Vehicle for the Treatment of Hemophilia 2012
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599 214. Prolonged Survival of Mice in an Orthotopic Glioblastoma Stem Cell Mouse Model after Treatment with an Y-Box Binding Protein 1 (YB-1) Dependent Oncolytic Adenovirus 2012
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601 675. Prostate Cancer Immunotherapy by Direct Lentivirus Vector Injection: Murine and Rhesus Macaque Models 2012
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602 270. Protamine Containing Chitosan:shRNA Complexes for Silencing of VEGF Expression 2012
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603 296. Protease-Activated Receptor 2 Cooperates with Toll-Like Receptor 4 in Sensing of Adenovirus-Coagulation Factor X Complex and Activating Innate Immune and Inflammatory Responses 2012
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604 516. Protein Kinase C Activators Enhance Zinc Finger Nuclease-Driven Genome Editing in Hematopoietic Stem/Progenitor Cells 2012
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605 454. Pushing the Limits of Expression: Highly Optimized Next Generation Molecular Adjuvants for Mucosa-Targeting DNA Vaccines 2012
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606 384. Quantification of Mature shRNA from Rat Tissues in a Biodistribution Study of pbi-shRNA™ STMN1 Lipoplex 2012
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608 233. rAAV9 Airway Delivery Results in Effective Knockdown of Mutant alpha 1-Antitrypsin in the Liver While Upregulating Wildtype alpha 1-Antitrypsin in the Lung 2012
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610 528. rAAV8/9-Mediated Muscle Transduction with Tacrolimus in Non-Human Primate 2012
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611 518. Radiation and Temozolomide Chemotherapy Do Not Inhibit the Oncolytic Adenovirus Loaded Carrier Cells to Effectively Deliver Their Payload 2012
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612 187. Randomized Phase II Trial of Post-Operative Adjuvant Chemotherapy ±FANG™ Autologous Tumor Cell Vaccine in Colorectal Carcinoma with Liver Metastases 2012
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614 281. Rapid Generation of Induced Pluripotent Stem Cells (iPSCs) from the Urine of a Patient with Duchenne Muscular Dystrophy 2012
 20 S1 p. S111-
1 p.
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 20 S1 p. S64-S65
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616 577. Ratios of Full to Empty Virions of AAV8 Vector Preparations Negatively Impact on Transduction Efficiency and Liver Toxicity in the Liver-Directed Gene Transfer 2012
 20 S1 p. S224-
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617 398. Recent Advances Using Small Molecule Targeting for Bilamellar Invaginated Vesicle (BIV) Delivery 2012
 20 S1 p. S155-S156
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 20 S1 p. S287-S288
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 20 S1 p. S174-
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620 329. Redirection of TH17 Cells with a Car Containing the ICOS Costimulatory Domain Enhances Function, Antitumor Activity and Persistence of TH17 Cells 2012
 20 S1 p. S130-
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 20 S1 p. S278-
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622 629. Refined Ultrasound-Mediated Gene Delivery Using Customized Microbubbles In Vitro 2012
 20 S1 p. S242-
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 20 S1 p. S140-
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624 171. Repair of Spinal Cord Injury (SCI) Using Monocytes Transfected with Adenoviral Vector Expressing Decorin in a Rat SCI Model 2012
 20 S1 p. S68-S69
2 p.
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625 588. Reproducible and Scalable Production Processes of Recombinant Adeno-Associated Virus Compatible with Current Good Manufacturing Practice 2012
 20 S1 p. S228-
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626 26. Rescue of Lethal Phenotype in Aspartoacylase Knockout Mouse by Single Intravenous Delivery of Therapeutic Vector That Also Improves Neuropathology, Nephropathy, Motor Function and Visual Acuity 2012
 20 S1 p. S11-
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627 245. Respiratory Tract Tropism Difference of FIV and VEV Vectors Pseudotyped with GP64 Envelope Glycoprotein 2012
 20 S1 p. S97-
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628 231. Response of Hematopoietic Cells to the Activation of Evi1 2012
 20 S1 p. S91-
1 p.
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 20 S1 p. S28-S29
2 p.
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630 51. Results of a Phase I Trial of SGT-53: A Systemically Administered, Tumor-Targeting Immunoliposome Nanocomplex Incorporating a Plasmid Encoding wtp53 2012
 20 S1 p. S21-
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 20 S1 p. S67-
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632 276. RNAi-Based Therapeutics Targeting nNOS for Prevention of Neuroblastoma Cell Apoptosis 2012
 20 S1 p. S109-
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633 173. RNA Interference Inhibits DUX4-Induced Muscle Toxicity In Vivo: Implications for a Targeted FSHD Therapy 2012
 20 S1 p. S69-
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634 736. RNA Interference on nNOS in Combination with Neomycin To Reduce the Viability of Human Glioma Cell Lines 2012
 20 S1 p. S283-S284
2 p.
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635 35. RNAi Therapy for Dominant Limb Girdle Muscular Dystrophy Type 1A 2012
 20 S1 p. S14-
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636 47. Robust Differentiation of Hematopoietic Progenitor Cells from Pigtail Macaque Induced Pluripotent Stem Cells toward Modeling Human Disease and Stem Cell Therapies In Vivo 2012
 20 S1 p. S19-S20
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 20 S1 p. S7-
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638 468. Role of STAT3 Signaling in Dendritic Cell Based Immunotherapy 2012
 20 S1 p. S182-
1 p.
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639 335. Safe and Durable Hepatic Expression of Anti-HCV shRNA in a Non-Human Primate Model 2012
 20 S1 p. S132-
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640 501. Safe and Efficient In Vivo Selection of Hematopoietic Cells Gene-Modified with Chemotherapy Inducible Methylguanine Methyltransferase P140K 2012
 20 S1 p. S194-
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641 130. Safe Harbor Locus Preservation with Zinc-Finger Nuclease Mediated Gene Addition in Mouse Primary Fibroblasts 2012
 20 S1 p. S52-S53
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642 135. Safety of Liver-Directed AAV2/8-Mediated Gene Transfer in a Large Animal Model of Lysosomal Storage Disease 2012
 20 S1 p. S55-
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643 594. Scalable Single-Step Affinity Purification of rAAV Vector Using AVB-Sepharose Yields High Purity and High Titer Vector 2012
 20 S1 p. S230-
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644 374. Scavenger Receptor A (SR-A) and Scavenger Receptor Expressed on Endothelial Cells I (SREC-I) Are Receptors of Helper-Dependent Adenoviral Vectors 2012
 20 S1 p. S146-S147
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645 108. Selection and Isolation of Patient Specific AAV Nab Escape Mutants 2012
 20 S1 p. S45-
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646 366. Selection of an Optimal AAV Serotype for Gene Therapy in ALS 2012
 20 S1 p. S143-S144
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647 539. Selective Targeting and Disruption of Tumor-Associated Vasculature in Humans with an Engineered Oncolytic Poxvirus 2012
 20 S1 p. S208-
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648 249. Self-Complementary AAV Vectors Delivered Intramuscularly Induce an Enhanced Immune Response to Factor IX 2012
 20 S1 p. S98-
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649 703. Serotype Chimeric Oncolytic Adenovirus Coding for Granulocyte-Macrophage Colony-Stimulating Factor (GMCSF) for Treatment of Soft Tissue Sarcoma in Rodents and Humans 2012
 20 S1 p. S272-
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650 140. Sex-Dependent Expression of Very Long Chain acyl-CoA Dehydrogenase (VLCAD) Transgene and the Role of the Liver in Biochemical and Phenotypic Correction of VLCAD Deficiency 2012
 20 S1 p. S57-
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 20 S1 p. S261-
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652 234. shRNA for Thymic Stromal Lymphopoietin as an Novel Antagonist for Pulmonary Fibrosis 2012
 20 S1 p. S92-
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653 61. Single Nucleotide Mismatches Decrease the Frequency of Gene Targeting 2012
 20 S1 p. S25-
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654 332. Sipuleucel-T in Metastatic Castrate-Resistant Prostate Cancer (mCRPC): Clinical Evidence of the Immunologic Mechanism of Action (MOA) 2012
 20 S1 p. S131-
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655 728. siRNA-miRNA Chimera Initiation Both siRNA-Induced and miRNA-Induced RNAi 2012
 20 S1 p. S281-
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656 116. Site-Directed Mutagenesis of Surface-Exposed Tyrosine, Serine, and Threonine Residues Leads to High-Efficiency Transduction by Recombinant Adeno-Associated Virus 2 Vectors 2012
 20 S1 p. S48-
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657 309. Site-Specific Gene Correction of β-Globin Using Zinc Finger Nucleases 2012
 20 S1 p. S122-
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658 121. Sleeping Beauty Transposon-Based Integration System Analysis in Human Epithelial Cells 2012
 20 S1 p. S49-S50
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659 71. Small Molecule Inhibitor of FAH Enzyme Allows for Selection of Genetically Resistant Donor Hepatocytes in Wildtype Settings In Vivo 2012
 20 S1 p. S29-
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660 85. SNS01-T, an eIF5A-Based Gene Therapy Nanoparticle Designed for the Treatment of Multiple Myeloma, Has Anti-Tumoral Activity in Lymphoma 2012
 20 S1 p. S35-
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661 285. SOX2 Is a Possible Target for the Treatment of Tumors Emerged in the Process of Reprogramming for iPSC Generation 2012
 20 S1 p. S113-
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662 731. Specific RNA Cleavage by Oligodeoxyribozyme Suppresses Proliferation of Drug-Resistant Leukemia Cells 2012
 20 S1 p. S282-
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663 750. Spectral Karyotyping of Multipotent Stromal Cells during In Vitro Expansion 2012
 20 S1 p. S289-S290
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664 647. Stabilized Quaternary Nanoparticles for Targeted Delivery of siRNA 2012
 20 S1 p. S249-S250
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665 418. Stable New Insulated Lentivectors towards Gene Therapy in Fanconi's Anemia 2012
 20 S1 p. S163-
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666 129. Stimulation of Homologous Recombination-Mediated Genome Editing through Donor DNA Processing 2012
 20 S1 p. S52-
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667 585. Strategy for rAAV-Mediated Transduction of Common Marmoset Skeletal Muscle To Generate NHP DMD Model 2012
 20 S1 p. S227-
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668 299. Strengthening of Antitumor Immune Memory and Prevention of Thymic Atrophy Mediated by Adenovirus Expressing IL-12 and GM-CSF 2012
 20 S1 p. S118-
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669 649. Structure-Activity Relationships in a Series of Pyridinium Gemini Surfactants for Gene Delivery Bearing Hydrophilic Linkers 2012
 20 S1 p. S250-S251
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670 382. Studies on the Biodistribution Evaluation of Gene Therapy Products Using the Real Time-PCR 2012
 20 S1 p. S150-
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671 397. Successful Gene Delivery with Polyamidoamine Dendrimers Targeted to the α Vβ3 Receptor Is Dependent on Caveolar Trafficking 2012
 20 S1 p. S155-
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672 198. Survey of Gene Therapy Researchers’ Perceptions and Assessment of Risks in Clinical Trials 2012
 20 S1 p. S78-
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673 133. Survival with Normal Neurological Development of the Juvenile Lethal Urea Cycle Defect Arginase Deficient Mouse with AAV Gene Therapy 2012
 20 S1 p. S54-
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674 373. Sustained and Safe Inhibition of Hepatitis B Virus Replication In Vivo Using Helper-Dependent Adenovirus Vectors To Deliver Antiviral RNAi Expression Cassettes 2012
 20 S1 p. S146-
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675 681. Syngeneic Hematopoietic Stem Cell Transplantation Enhances the Antitumor Immunity of Intratumoral Type I Interferon Gene Transfer for Sarcoma 2012
 20 S1 p. S263-
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676 244. Synthetic DNA Vaccine Against Avian Influenza A Virus 2012
 20 S1 p. S96-
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677 272. Synthetic Double-Stranded siRNA-Based Therapeutics Targeting nNOS for Prevention of 6-OHDA Neurotoxicity in Neuroblastoma Cells 2012
 20 S1 p. S107-
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678 273. Synthetic Double-Stranded siRNAs Can Silence the Expression of Neuronal Nitric Oxide Synthase Enzyme (nNOS) from Neuroblastoma Cells in a Temporal and Dose Dependent Manner 2012
 20 S1 p. S107-S108
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679 508. Synthetic Promoter Design of Cell Type-Specific Adeno-Associated Viral Vectors in the Retina 2012
 20 S1 p. S196-
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680 288. Systematic Development and Qualification of Assays for the Characterization of Human Embryonic Stem Cells and Their Differentiated Progeny 2012
 20 S1 p. S114-
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681 131. Systematic Identification of Bi-Functional Short-Hairpin RNA (shRNA) Specific for Single-Nucleotide KRAS Mutations 2012
 20 S1 p. S53-
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682 684. Systemic Administration of Platelet Vector Containing Inactivated Sendai Virus Particle Eradicates Melanoma in Mice 2012
 20 S1 p. S264-
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683 201. Systemic Cancer Virotherapy with MDVV, a Combined miRNA-Regulated and Thymidine Kinase-Deleted Oncolytic Vaccinia Virus 2012
 20 S1 p. S79-
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684 597. Systemic Delivery of Chitosan-PEG-FA-Conjuatged Oncolytic Adenovirus Nanocomplexes for Folate Receptor-Overexpressing Cancer Therapy 2012
 20 S1 p. S231-
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685 179. Systemic Delivery of nNOS-Recruiting Mini-Dystrophin AAV Vectors Ameliorated Muscular Dystrophy in a Mouse DMD Model 2012
 20 S1 p. S72-
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686 300. Systemic Delivery of Oncolytic Adenoviruses Targeting Transforming Growth Factor Beta Inhibits Established Bone Metastasis in a Prostate Cancer Mouse Model 2012
 20 S1 p. S118-S119
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687 28. Systemic Delivery of rAAV9-hNAGLU in Adult Non-Human Primates: Efficient CNS and Somatic Transduction with No Detectable Toxicity 2012
 20 S1 p. S11-S12
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688 371. Systemic Gene Expression after Intravenous Injection of Adeno-Associated Virus 2/9 to Fetal and Neonatal Mice 2012
 20 S1 p. S145-S146
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689 667. Systemic Immunization with Mucosal Chemokine Molecular Adjuvant TECK/CCL25 Targets Antigen Specific Immune Responses in the Mucosa-Associated Lymphoid Tissue 2012
 20 S1 p. S257-
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690 67. Targeted Integration in Human Epidermal Stem Cells by Zinc-Finger Nuclease-Mediated Homologous Recombination 2012
 20 S1 p. S28-
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691 372. Targeted Mutagenesis of Ubiquitin-Binding Lysine Residues on the Adeno-Associated Virus (AAV)2 Capsid Improves Its Transduction Efficiency 2012
 20 S1 p. S146-
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 20 S1 p. S243-S244
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693 607. Targeting 2A-Fusions to Endogenous Genes 2012
 20 S1 p. S234-
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694 730. Targeting Androgen Receptors in Hormone-Dependent and Castration Resistant Prostate Cancer 2012
 20 S1 p. S281-S282
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695 81. Targeting Castration Resistant Prostate Cancer (CRPC) with Autologous PSMA-Directed Chimeric Antigen Receptor T Cells 2012
 20 S1 p. S33-
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696 476. Targeting Gene Transfer in Pancreatic Adenocarcinoma with Cell Surface Antigens 2012
 20 S1 p. S185-
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697 533. Targeting Intracellular Antigens Using Chimeric Antigen Receptors 2012
 20 S1 p. S206-
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698 722. Targeting siRNA Toxicity to HER2+ Tumors: Multi-Pronged Attack and Implications for Drug-Resistance 2012
 20 S1 p. S279-
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699 207. Tat-PTD-Modified Oncolytic Adenovirus Driven by the SCG3 Promoter and ASH1 Enhancer for Neuroblastoma Therapy 2012
 20 S1 p. S81-
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700 535. T Cells Redirected Against HER2 for Adoptive Immunotherapy for HER2-Positive Osteosarcoma 2012
 20 S1 p. S206-S207
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701 84. T-Cell Targeting an Ancient Retrovirus Expressed in Melanoma Cells 2012
 20 S1 p. S34-S35
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 20 S1 p. S205-
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703 534. TGF-β as a Modifier of Response to Adoptive Cell Therapy for Melanoma: Enhanced Tumor Treatment in Animal Models and a Highly Significant Correlation between Clinical Response and TGF-β Genotypes 2012
 20 S1 p. S206-
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704 448. TGF-b1 Transduced Human Chondrocytes (TG-C) Formulated in Fibrin Glue Regenerated Cartilage in the Pig Cartilage Defect Model 2012
 20 S1 p. S174-
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705 340. The Anti-Gene Oligonucleotide “Zorro-LNA”, Delivered by a Cationic Lipid, DownRegulates Huntingtin Gene Expression in Mammalian Cells 2012
 20 S1 p. S133-S134
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706 284. The Application of A9 Dopaminergic Neurons Derived from Human Parthenogenetic Stem Cells for the Treatment of Parkinson's Disease 2012
 20 S1 p. S112-
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707 425. The Aurora A Kinase Inhibitor MLN8237 Significantly Enhances the Antitumor Activity of Oncolytic Measles Virus Derivatives in the Treatment of Glioblastoma 2012
 20 S1 p. S166-
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708 437. The Brain Specific microRNA Regulates Neuronal Injury in Rat Intracerebral Hemorrhage Model 2012
 20 S1 p. S170-
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 20 S1 p. S129-
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710 428. The Development of Non-Viral Vectors for Choroideremia 2012
 20 S1 p. S167-
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 20 S1 p. S5-
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 20 S1 p. S61-
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 20 S1 p. S265-S266
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714 513. The Immunosuppressant Drug Rapamycin Relieves Lentiviral Transduction Resistance in Human Hematopoietic Stem Cells 2012
 20 S1 p. S198-
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 20 S1 p. S138-S139
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 20 S1 p. S41-S42
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 20 S1 p. S207-S208
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 20 S1 p. S9-
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 20 S1 p. S62-
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720 33. Therapeutic Applications of Sleeping Beauty System and iPS technology To Treat Duchenne Muscular Dystrophy 2012
 20 S1 p. S13-S14
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 20 S1 p. S238-
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 20 S1 p. S112-
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 20 S1 p. S270-
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725 275. Time-Dependent siRNA Effects on nNOS Message in Glioma Cells in Culture 2012
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726 742. Tissue Factor-Triggered Procoagulant Activity of Murine/Human Mesenchymal Stem Cells 2012
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727 383. Tissue Specific piggyBac Gene Therapy Vectors 2012
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729 581. Toxicology and Liver Transduction Efficacy Evaluation of a Recombinant Adeno-Associated Viral Vector in Non Human Primates as a Potential Treatment for Acute Intermittent Porphyria 2012
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730 219. Tracking the Fate and Activity of Individual HSC and Memory Stem T Cell Clones in GT Patients through Insertional Tagging 2012
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732 507. Transcriptional Repression of the Rhodopsin Gene Via Zinc-Finger Technology for the Treatment of the Dominant Retinal Degenerations 2012
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740 716. Transient Transgene Repression Post-Gene Delivery Improves Long-Term Expression In Vivo 2012
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744 330. Tumor Pericytes: A Novel Target for Immunotherapy in Renal Cell Carcinoma 2012
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745 369. Two Complementary Methods To Identify AAVS1 Integrants 2012
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751 499. Upregulation of the Pluripotency-Associated miRNA 302-367 Cluster Using Engineered Transcription Activator-Like Effector (TALE) Activators 2012
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752 209. Use of Helicobacter pyroli Neutrophil Activating Protein (NAP) as an Immune-Modulatory Agent To Enhance the Efficacy of Oncolytic Adenovirus Therapy for Cancer 2012
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753 486. Use of the In Vitro Immortalization Assay To Quantify the Impact of Vector Design and Integration Pattern on Insertional Mutagenesis 2012
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754 305. Using Homologous Recombination To Stack Genetic Resistance to HIV 2012
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755 400. Vaccines Based on Disrupted Ad5 Against Small Molecule Drugs Are Efficacious in the Presence of Preexisting Ad5 Immunity 2012
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756 495. Validation of Cellular Function and Imaging Capability of CD34+ Stem Cells Labeled with a 19F MRI Contrast Agent 2012
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757 229. Vectofusin-1 Augments Lentiviral Transduction of Human Hematopoietic Cells by Enhancing Adhesion and Fusion of Particles to CD34+ Cells 2012
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758 350. Vector Design-Dependent Modulation of Viral-Cellular Chimeric Fusion Transcripts Derived from Self-Inactivating (SIN) Lentiviral Vectors 2012
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759 523. Vector Genome Length and Self-Complementarity Affect AAV Capsid Uncoating 2012
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760 745. Viral-Based Dual-Color Imaging for Cell Division and Fusion In Vitro 2012
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761 301. Viral Genome DNA/Lipoplexes Elicit In Situ Oncolytic Viral Replication and Potent Antitumor Efficacy Via Systemic Delivery 2012
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762 709. Virological and Immunological Data in Cancer Patients Treated with a Fully Serotype 3 Oncolytic Adenovirus Ad3-hTERT-E1A 2012
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763 674. VSV-Expressed cDNA Libraries Cure Established Melanoma and Identify Repertoires of Antigens Which Co-Operate To Stimulate Protective Tumor Immunity 2012
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 20 S1 p. S18-
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765 308. Zinc-Finger Nuclease-Mediated Correction of RS-SCID 2012
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766 568. Zinc-Finger Nuclease Mediated Correction of α-Thalassemia in iPS 2012
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