| no |
title |
author |
magazine |
year |
volume |
issue |
page(s) |
type |
| 1 |
AAV8-mediated Gene Therapy Prevents Induced Biochemical Attacks of Acute Intermittent Porphyria and Improves Neuromotor Function
|
Yasuda, Makiko
|
|
2010
|
18 |
1 |
p. 17-22
6 p.
|
article
|
| 2 |
Activation of Transgene-specific T Cells Following Lentivirus-mediated Gene Delivery to Mouse Lung
|
Limberis, Maria P
|
|
2010
|
18 |
1 |
p. 143-150
8 p.
|
article
|
| 3 |
Adeno-associated Virus Gene Therapy With Cholesterol 24-Hydroxylase Reduces the Amyloid Pathology Before or After the Onset of Amyloid Plaques in Mouse Models of Alzheimer's Disease
|
Hudry, Eloise
|
|
2010
|
18 |
1 |
p. 44-53
10 p.
|
article
|
| 4 |
Adipose Tissue–derived Mesenchymal Stem Cells Expressing Prodrug-converting Enzyme Inhibit Human Prostate Tumor Growth
|
Cavarretta, Ilaria T
|
|
2010
|
18 |
1 |
p. 223-231
9 p.
|
article
|
| 5 |
Characterization of Genome Integrity for Oversized Recombinant AAV Vector
|
Dong, Biao
|
|
2010
|
18 |
1 |
p. 87-92
6 p.
|
article
|
| 6 |
Deficiency of the Housekeeping Gene Hypoxanthine–Guanine Phosphoribosyltransferase (HPRT) Dysregulates Neurogenesis
|
Guibinga, Ghiabe-Henri
|
|
2010
|
18 |
1 |
p. 54-62
9 p.
|
article
|
| 7 |
Design and Evaluation of Doxorubicin-containing Microbubbles for Ultrasound-triggered Doxorubicin Delivery: Cytotoxicity and Mechanisms Involved
|
Lentacker, Ine
|
|
2010
|
18 |
1 |
p. 101-108
8 p.
|
article
|
| 8 |
Dystrophin Delivery to Muscles of mdx Mice Using Lentiviral Vectors Leads to Myogenic Progenitor Targeting and Stable Gene Expression
|
Kimura, En
|
|
2010
|
18 |
1 |
p. 206-213
8 p.
|
article
|
| 9 |
Effect of Genome Size on AAV Vector Packaging
|
Wu, Zhijian
|
|
2010
|
18 |
1 |
p. 80-86
7 p.
|
article
|
| 10 |
Evaluation of Efficacy, Biodistribution, and Inflammation for a Potent siRNA Nanoparticle: Effect of Dexamethasone Co-treatment
|
Abrams, Marc T
|
|
2010
|
18 |
1 |
p. 171-180
10 p.
|
article
|
| 11 |
Evidence for the Failure of Adeno-associated Virus Serotype 5 to Package a Viral Genome ≥8.2 kb
|
Lai, Yi
|
|
2010
|
18 |
1 |
p. 75-79
5 p.
|
article
|
| 12 |
G-rich Oligonucleotides Inhibit HIF-1α and HIF-2α and Block Tumor Growth
|
Guan, Yongli
|
|
2010
|
18 |
1 |
p. 188-197
10 p.
|
article
|
| 13 |
Image-guided, Intravascular Hydrodynamic Gene Delivery to Skeletal Muscle in Pigs
|
Kamimura, Kenya
|
|
2010
|
18 |
1 |
p. 93-100
8 p.
|
article
|
| 14 |
Interesting Times: Molecular Therapy and the Evolving Media of Scientific Publishing
|
Brenner, Malcolm
|
|
2010
|
18 |
1 |
p. 1-2
2 p.
|
article
|
| 15 |
In the Beginning: Reflections on the Genesis of Molecular Therapy
|
Wilson, James M
|
|
2010
|
18 |
1 |
p. 9-10
2 p.
|
article
|
| 16 |
In This Issue
|
|
|
2010
|
18 |
1 |
p. 4-
1 p.
|
article
|
| 17 |
Lack of Immunotoxicity After Regional Intravenous (RI) Delivery of rAAV to Nonhuman Primate Skeletal Muscle
|
Toromanoff, Alice
|
|
2010
|
18 |
1 |
p. 151-160
10 p.
|
article
|
| 18 |
Little Vector, Big Gene Transduction: Fragmented Genome Reassembly of Adeno-associated Virus
|
Hirsch, Matthew L
|
|
2010
|
18 |
1 |
p. 6-8
3 p.
|
article
|
| 19 |
Long-term Rescue of a Lethal Murine Model of Methylmalonic Acidemia Using Adeno associated Viral Gene Therapy
|
Chandler, Randy J
|
|
2010
|
18 |
1 |
p. 11-16
6 p.
|
article
|
| 20 |
Low-level shRNA Cytotoxicity Can Contribute to MYC-induced Hepatocellular Carcinoma in Adult Mice
|
Beer, Shelly
|
|
2010
|
18 |
1 |
p. 161-170
10 p.
|
article
|
| 21 |
Multiple Functions of the 37/67-kd Laminin Receptor Make It a Suitable Target for Novel Cancer Gene Therapy
|
Scheiman, Jonathan
|
|
2010
|
18 |
1 |
p. 63-74
12 p.
|
article
|
| 22 |
Persistent Expression of FLAG-tagged Micro dystrophin in Nonhuman Primates Following Intramuscular and Vascular Delivery
|
Rodino-Klapac, Louise R
|
|
2010
|
18 |
1 |
p. 109-117
9 p.
|
article
|
| 23 |
Polysialic Acid Glycomimetic Promotes Functional Recovery and Plasticity After Spinal Cord Injury in Mice
|
Mehanna, Ali
|
|
2010
|
18 |
1 |
p. 34-43
10 p.
|
article
|
| 24 |
Prevention of Dystrophic Pathology in Severely Affected Dystrophin/Utrophin-deficient Mice by Morpholino-oligomer-mediated Exon-skipping
|
Goyenvalle, Aurélie
|
|
2010
|
18 |
1 |
p. 198-205
8 p.
|
article
|
| 25 |
Proteasome Inhibitors Decrease AAV2 Capsid derived Peptide Epitope Presentation on MHC Class I Following Transduction
|
Finn, Jonathan D
|
|
2010
|
18 |
1 |
p. 135-142
8 p.
|
article
|
| 26 |
Research Highlights
|
|
|
2010
|
18 |
1 |
p. 5-
1 p.
|
article
|
| 27 |
Stem Cell Vaccination Against Cancer: Fighting Fire With Fire?
|
Zwaka, Thomas P
|
|
2010
|
18 |
1 |
p. 8-9
2 p.
|
article
|
| 28 |
Suppression of FVIII Inhibitor Formation in Hemophilic Mice by Delivery of Transgene Modified Apoptotic Fibroblasts
|
Su, Rui-Jun
|
|
2010
|
18 |
1 |
p. 214-222
9 p.
|
article
|
| 29 |
Systematic Evaluation of AAV Vectors for Liver directed Gene Transfer in Murine Models
|
Wang, Lili
|
|
2010
|
18 |
1 |
p. 118-125
8 p.
|
article
|
| 30 |
Systemic Delivery of Synthetic MicroRNA-16 Inhibits the Growth of Metastatic Prostate Tumors via Downregulation of Multiple Cell-cycle Genes
|
Takeshita, Fumitaka
|
|
2010
|
18 |
1 |
p. 181-187
7 p.
|
article
|
| 31 |
The Pharmacological Chaperone 1-Deoxygalactonojirimycin Reduces Tissue Globotriaosylceramide Levels in a Mouse Model of Fabry Disease
|
Khanna, Richie
|
|
2010
|
18 |
1 |
p. 23-33
11 p.
|
article
|
| 32 |
The Pleiotropic Effects of Natural AAV Infections on Liver-directed Gene Transfer in Macaques
|
Wang, Lili
|
|
2010
|
18 |
1 |
p. 126-134
9 p.
|
article
|
Journal description