Clinical Trial and Postmarketing Safety of Onasemnogene Abeparvovec Therapy
Titel:
Clinical Trial and Postmarketing Safety of Onasemnogene Abeparvovec Therapy
Auteur:
Day, John W. Mendell, Jerry R. Mercuri, Eugenio Finkel, Richard S. Strauss, Kevin A. Kleyn, Aaron Tauscher-Wisniewski, Sitra Tukov, Francis Fonyuy Reyna, Sandra P. Chand, Deepa H.