Effects of Chronic, Maximal Phosphorodiamidate Morpholino Oligomer (PMO) Dosing on Muscle Function and Dystrophin Restoration in a Mouse Model of Duchenne Muscular Dystrophy
Titel:
Effects of Chronic, Maximal Phosphorodiamidate Morpholino Oligomer (PMO) Dosing on Muscle Function and Dystrophin Restoration in a Mouse Model of Duchenne Muscular Dystrophy
Auteur:
Benny Klimek, Margaret E. Vila, Maria Candida Edwards, Katie Boehler, Jessica Novak, James Zhang, Aiping Van der Meulen, Jack Tatum, Kathleen Quinn, James Fiorillo, Alyson Burki, Umar Straub, Volker Lu, Qi Long Hathout, Yetrib van Den Anker, John Partridge, Terence A. Morales, Melissa Hoffman, Eric Nagaraju, Kanneboyina Jaiswal, Jyoti Nagaraju, Kanneboyina