RESTORE: A Prospective Multinational Registry of Patients with Genetically Confirmed Spinal Muscular Atrophy - Rationale and Study Design
Titel:
RESTORE: A Prospective Multinational Registry of Patients with Genetically Confirmed Spinal Muscular Atrophy - Rationale and Study Design
Auteur:
Finkel, Richard S. Day, John W. De Vivo, Darryl C. Kirschner, Janbernd Mercuri, Eugenio Muntoni, Francesco Shieh, Perry B. Tizzano, Eduardo Desguerre, Isabelle Quijano-Roy, Susana Saito, Kayoko Droege, Marcus Dabbous, Omar Khan, Farid Renault, Lydie Anderson, Frederick A. Servais, Laurent