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Evaluation of Children with SMA Type 1 Under Treatment with Nusinersen within the Expanded Access Program in Germany |
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Titel: |
Evaluation of Children with SMA Type 1 Under Treatment with Nusinersen within the Expanded Access Program in Germany |
Auteur: |
Pechmann, Astrid Langer, Thorsten Schorling, David Stein, Sabine Vogt, Sibylle Schara, Ulrike Kölbel, Heike Schwartz, Oliver Hahn, Andreas Giese, Kerstin Johannsen, Jessika Denecke, Jonas Weiß, Claudia Theophil, Manuela Kirschner, Janbernd |
Verschenen in: |
Journal of neuromuscular diseases |
Paginering: |
Jaargang 5 (2018) nr. 2 pagina's 135-143 |
Jaar: |
2018-05-29 |
Inhoud: |
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Uitgever: |
IOS Press, Amsterdam |
Bronbestand: |
Elektronische Wetenschappelijke Tijdschriften |
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