Increase in Full-Length Dystrophin by Exon Skipping in Duchenne Muscular Dystrophy Patients with Single Exon Duplications: An Open-label Study
Titel:
Increase in Full-Length Dystrophin by Exon Skipping in Duchenne Muscular Dystrophy Patients with Single Exon Duplications: An Open-label Study
Auteur:
Nicolau, Stefan Malhotra, Jyoti Kaler, Maryann Magistrado-Coxen, Pamela Iammarino, Megan A. Reash, Natalie F. Frair, Emma C. Wijeratne, Saranga Kelly, Benjamin J. White, Peter Lowes, Linda P. Waldrop, Megan A. Flanigan, Kevin M.