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Risdiplam in Spinal Muscular Atrophy: Safety Profile and Use Through The Early Access to Medicine Scheme for the Paediatric Cohort in Great Britain |
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Titel: |
Risdiplam in Spinal Muscular Atrophy: Safety Profile and Use Through The Early Access to Medicine Scheme for the Paediatric Cohort in Great Britain |
Auteur: |
Cornell, Nikki Childs, Anne-Marie Wraige, Elizabeth Munot, Pinki Ambegaonkar, Gautam Chow, Gabriel Hughes, Imelda Illingworth, Marjorie Majumdar, Anirban Marini-Bettolo, Chiara Parasuraman, Deepak Spinty, Stefan Willis, Tracey Scoto, Mariacristina Baranello, Giovanni |
Verschenen in: |
Journal of neuromuscular diseases |
Paginering: |
Jaargang 11 () nr. 2 pagina's 361-368 |
Jaar: |
2024-03-05 |
Inhoud: |
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Uitgever: |
IOS Press, Amsterdam |
Bronbestand: |
Elektronische Wetenschappelijke Tijdschriften |
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