DEVOTE Study Exploring Higher Dose of Nusinersen in Spinal Muscular Atrophy: Study Design and Part A Results
Titel:
DEVOTE Study Exploring Higher Dose of Nusinersen in Spinal Muscular Atrophy: Study Design and Part A Results
Auteur:
Finkel, Richard S. Day, John W. Pascual Pascual, Samuel Ignacio Ryan, Monique M. Mercuri, Eugenio De Vivo, Darryl C. Montes, Jacqueline Gurgel-Giannetti, Juliana Monine, Michael Gambino, Giulia Makepeace, Corinne Foster, Richard Berger, Zdenek