Full-Length SMN Transcript in Extracellular Vesicles as Biomarker in Individuals with Spinal Muscular Atrophy Type 2 Treated with Nusinersen
Titel:
Full-Length SMN Transcript in Extracellular Vesicles as Biomarker in Individuals with Spinal Muscular Atrophy Type 2 Treated with Nusinersen
Auteur:
Trifunov, Selena Natera-de Benito, Daniel Carrera-García, Laura Codina, Anna Expósito-Escudero, Jesica Ortez, Carlos Medina, Julita Torres Alcala, Soraya Bernal, Sara Alias, Laura Badosa, Carmen Balsells, Sol Alcolea, Daniel Nascimento, Andres Jimenez-Mallebrera, Cecilia