Corticosteroid use to mitigate transaminitis-associated decline in FVIII levels following valoctocogene roxaparvovec gene therapy: clinical practice guidance
Titel:
Corticosteroid use to mitigate transaminitis-associated decline in FVIII levels following valoctocogene roxaparvovec gene therapy: clinical practice guidance
Auteur:
Konkle, Barbara A. Peyvandi, Flora Foster, Graham R. Hermans, Cedric La Mura, Vincenzo Leavitt, Andrew D. Lillicrap, David Mahlangu, Johnny Ozelo, Margareth C. Pipe, Steven Recht, Michael Srivastava, Alok Young, Guy Miesbach, Wolfgang