Safety and efficacy of valoctocogene roxaparvovec with prophylactic glucocorticoids: 1-year results from the phase 3b, single-arm, open-label GENEr8-3 study
Titel:
Safety and efficacy of valoctocogene roxaparvovec with prophylactic glucocorticoids: 1-year results from the phase 3b, single-arm, open-label GENEr8-3 study
Auteur:
Ozelo, Margareth C. Mason, Jane Dunn, Amy L. Villaça, Paula Ribeiro Shen, Ming-Ching Agarwal, Suresh Imtiaz, Urooj Liu, Hai Robinson, Tara M.