Translational studies of intravenous and intracerebroventricular routes of administration for CNS cellular biodistribution for BMN 250, an enzyme replacement therapy for the treatment of Sanfilippo type B
Titel:
Translational studies of intravenous and intracerebroventricular routes of administration for CNS cellular biodistribution for BMN 250, an enzyme replacement therapy for the treatment of Sanfilippo type B
Auteur:
Grover, Anita Crippen-Harmon, Danielle Nave, Lacey Vincelette, Jon Wait, Jill C. M. Melton, Andrew C. Lawrence, Roger Brown, Jillian R. Webster, Katherine A. Yip, Bryan K. Baridon, Brian Vitelli, Catherine Rigney, Sara Christianson, Terri M. Tiger, Pascale M. N. Lo, Melanie J. Holtzinger, John Shaywitz, Adam J. Crawford, Brett E. Fitzpatrick, Paul A. LeBowitz, Jonathan H. Bullens, Sherry Aoyagi-Scharber, Mika Bunting, Stuart O’Neill, Charles A. Pinkstaff, Jason Bagri, Anil