|
Model-Informed Approach Supporting Approval of Nexviazyme (Avalglucosidase Alfa-ngpt) in Pediatric Patients with Late-Onset Pompe Disease |
|
|
|
Titel: |
Model-Informed Approach Supporting Approval of Nexviazyme (Avalglucosidase Alfa-ngpt) in Pediatric Patients with Late-Onset Pompe Disease |
Auteur: |
Li, Ruo-Jing Ma, Lian Drozda, Katarzyna Wang, Jie Punnoose, Ann R. Jeng, Linda J. B. Maynard, Janet W. Zhu, Hao Pacanowski, Michael |
Verschenen in: |
The AAPS journal |
Paginering: |
Jaargang 25 () nr. 1 pagina's xx |
Jaar: |
2023-01-18 |
Inhoud: |
|
Uitgever: |
Springer International Publishing, Cham |
Bronbestand: |
Elektronische Wetenschappelijke Tijdschriften |
|
|
|
|