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Assessing the Role of Anti rh-GAA in Modulating Response to ERT in a Late-Onset Pompe Disease Cohort from the Italian GSDII Study Group |
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Titel: |
Assessing the Role of Anti rh-GAA in Modulating Response to ERT in a Late-Onset Pompe Disease Cohort from the Italian GSDII Study Group |
Auteur: |
Filosto, Massimiliano Cotti Piccinelli, Stefano Ravaglia, Sabrina Servidei, Serenella Moggio, Maurizio Musumeci, Olimpia Donati, Maria Alice Pegoraro, Elena Di Muzio, Antonio Maggi, Lorenzo Tonin, Paola Marrosu, Gianni Sancricca, Cristina Lerario, Alberto Sacchini, Michele Semplicini, Claudio Bozzoni, Virginia Telese, Roberta Bonanno, Silvia Piras, Rachele Maioli, Maria Antonietta Ricci, Giulia Vercelli, Liliana Galvagni, Anna Gallo Cassarino, Serena Caria, Filomena Mongini, Tiziana Siciliano, Gabriele Padovani, Alessandro Toscano, Antonio |
Verschenen in: |
Advances in therapy |
Paginering: |
Jaargang 36 (2019) nr. 5 pagina's 1177-1189 |
Jaar: |
2019 |
Inhoud: |
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Uitgever: |
Springer Healthcare, Cheshire |
Bronbestand: |
Elektronische Wetenschappelijke Tijdschriften |
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