Skeletal improvement in patients with Gaucher disease type 1: a phase 2 trial of oral eliglustat
Titel:
Skeletal improvement in patients with Gaucher disease type 1: a phase 2 trial of oral eliglustat
Auteur:
Kamath, Ravi S. Lukina, Elena Watman, Nora Dragosky, Marta Pastores, Gregory M. Arreguin, Elsa Avila Rosenbaum, Hanna Zimran, Ari Aguzzi, Rasha Puga, Ana Cristina Norfleet, Andrea M. Peterschmitt, M. Judith Rosenthal, Daniel I.