The role of enzyme replacement therapy in severe Hunter syndrome—an expert panel consensus
Titel:
The role of enzyme replacement therapy in severe Hunter syndrome—an expert panel consensus
Auteur:
Muenzer, Joseph Bodamer, Olaf Burton, Barbara Clarke, Lorne Frenking, Gudrun Schulze Giugliani, Roberto Jones, Simon Rojas, Maria Verónica Muñoz Scarpa, Maurizio Beck, Michael Harmatz, Paul