Population pharmacokinetic modeling and dosing simulation of avalglucosidase alfa for selecting alternative dosing regimen in pediatric patients with late-onset pompe disease
Titel:
Population pharmacokinetic modeling and dosing simulation of avalglucosidase alfa for selecting alternative dosing regimen in pediatric patients with late-onset pompe disease
Auteur:
Tiraboschi, Gilles Marchionni, David Tuffal, Gilles Fabre, David Martinez, Jean-Marie Haack, Kristina An Miossec, Patrick Kittner, Barbara Daba, Nadia Hurbin, Fabrice