AAV8 gene therapy for mitochondrial neurogastrointestinal encephalomyopathy (MNGIE) in a patient's liver maintained ex situ for 9 days
Titel:
AAV8 gene therapy for mitochondrial neurogastrointestinal encephalomyopathy (MNGIE) in a patient's liver maintained ex situ for 9 days
Auteur:
Brevini, Teresa Swift, Lisa Reynolds, Helen Ong, John Stopforth, Richard Malam, Yogeshkumar Spiers, Harry AnnaPaterson, Duckworth, Adam Kaser, Arthur Kosmoliaptsis, Vassillis Marti, Ramon van den Ameele, Jelle Webb, Gwilym Watson, Christopher Butler, Andrew Sampaziotis, Fotios