P171: Developing an approach to screening rare genetic diagnoses for amenability to bespoke genetic therapy development
Title:
P171: Developing an approach to screening rare genetic diagnoses for amenability to bespoke genetic therapy development
Author:
Cheerie, David Lauffer, Marlen Beijer, Danique Synofzik, Matthis Aartsma-Rus, Annemieke Szego, Michael Amburgey, Kimberly Kalish, Brian Dowling, James Costain, Gregory