Prospective characterization of early symptom onset and progression in young pediatric patients with variants in the G LA gene across 5 years: Longitudinal data from the Fabry MOPPet Study
Titel:
Prospective characterization of early symptom onset and progression in young pediatric patients with variants in the G LA gene across 5 years: Longitudinal data from the Fabry MOPPet Study
Auteur:
Laney, D.A. Houde, M.F. Foley, A.L. Peck, D.S. Atherton, A.M. Manwaring, L.P. Grange, D.K. Heese, B.A. Holida, M.D. Quillin, A.L. Vinson, R. Auray-Blais, C. Hopkin, R.J.