Long-term efficacy and safety of nusinersen in adults with 5q spinal muscular atrophy: a prospective European multinational observational study
Titel:
Long-term efficacy and safety of nusinersen in adults with 5q spinal muscular atrophy: a prospective European multinational observational study
Auteur:
Günther, René Wurster, Claudia Diana Brakemeier, Svenja Osmanovic, Alma Schreiber-Katz, Olivia Petri, Susanne Uzelac, Zeljko Hiebeler, Miriam Thiele, Simone Walter, Maggie C. Weiler, Markus Kessler, Tobias Freigang, Maren Lapp, Hanna Sophie Cordts, Isabell Lingor, Paul Deschauer, Marcus Hahn, Andreas Martakis, Kyriakos Steinbach, Robert Ilse, Benjamin Rödiger, Annekathrin Bellut, Julia Nentwich, Julia Zeller, Daniel Muhandes, Mohamad Tareq Baum, Tobias Christoph Koch, Jan Schrank, Bertold Fischer, Sophie Hermann, Andreas Kamm, Christoph Naegel, Steffen Mensch, Alexander Weber, Markus Neuwirth, Christoph Lehmann, Helmar C. Wunderlich, Gilbert Stadler, Christian Tomforde, Maike George, Annette Groß, Martin Pechmann, Astrid Kirschner, Janbernd Türk, Matthias Schimmel, Mareike Bernert, Günther Martin, Pascal Rauscher, Christian Meyer zu Hörste, Gerd Baum, Petra Löscher, Wolfgang Flotats-Bastardas, Marina Köhler, Cornelia Probst-Schendzielorz, Kristina Goldbach, Susanne Schara-Schmidt, Ulrike Müller-Felber, Wolfgang Lochmüller, Hanns von Velsen, Otgonzul Kleinschnitz, Christoph Ludolph, Albert C. Hagenacker, Tim