Multi-year enzyme expression in patients with mucopolysaccharidosis type VI after liver-directed gene therapy
Titel:
Multi-year enzyme expression in patients with mucopolysaccharidosis type VI after liver-directed gene therapy
Auteur:
Rossi, Alessandro Romano, Roberta Fecarotta, Simona Dell’Anno, Margherita Pecorella, Valentina Passeggio, Roberta Zancan, Stefano Parenti, Giancarlo Santamaria, Francesca Borgia, Francesco Deodato, Federica Funghini, Silvia Rupar, Charles A. Prasad, Chitra O’Callaghan, Mar Mitchell, John J. Valsecchi, Maria Grazia la Marca, Giancarlo Galimberti, Stefania Auricchio, Alberto Brunetti-Pierri, Nicola