Gene transfer into hematopoietic stem cells reduces HLH manifestations in a murine model of Munc13-4 deficiency
Titel:
Gene transfer into hematopoietic stem cells reduces HLH manifestations in a murine model of Munc13-4 deficiency
Auteur:
Soheili, Tayebeh Durand, Amandine Sepulveda, Fernando E. Rivière, Julie Lagresle-Peyrou, Chantal Sadek, Hanem de Saint Basile, Geneviève Martin, Samia Mavilio, Fulvio Cavazzana, Marina André-Schmutz, Isabelle