Editing aberrant splice sites efficiently restores β-globin expression in β-thalassemia
Titel:
Editing aberrant splice sites efficiently restores β-globin expression in β-thalassemia
Auteur:
Xu, Shuqian Luk, Kevin Yao, Qiuming Shen, Anne H. Zeng, Jing Wu, Yuxuan Luo, Hong-Yuan Brendel, Christian Pinello, Luca Chui, David H.K. Wolfe, Scot A. Bauer, Daniel E.