Gene therapy for adenosine deaminase–deficient severe combined immune deficiency: clinical comparison of retroviral vectors and treatment plans
Titel:
Gene therapy for adenosine deaminase–deficient severe combined immune deficiency: clinical comparison of retroviral vectors and treatment plans
Auteur:
Candotti, Fabio Shaw, Kit L. Muul, Linda Carbonaro, Denise Sokolic, Robert Choi, Christopher Schurman, Shepherd H. Garabedian, Elizabeth Kesserwan, Chimene Jagadeesh, G. Jayashree Fu, Pei-Yu Gschweng, Eric Cooper, Aaron Tisdale, John F. Weinberg, Kenneth I. Crooks, Gay M. Kapoor, Neena Shah, Ami Abdel-Azim, Hisham Yu, Xiao-Jin Smogorzewska, Monika Wayne, Alan S. Rosenblatt, Howard M. Davis, Carla M. Hanson, Celine Rishi, Radha G. Wang, Xiaoyan Gjertson, David Yang, Otto O. Balamurugan, Arumugam Bauer, Gerhard Ireland, Joanna A. Engel, Barbara C. Podsakoff, Gregory M. Hershfield, Michael S. Blaese, R. Michael Parkman, Robertson Kohn, Donald B.