Safety and efficacy of factor IX gene transfer to skeletal muscle in murine and canine hemophilia B models by adeno-associated viral vector serotype 1
Titel:
Safety and efficacy of factor IX gene transfer to skeletal muscle in murine and canine hemophilia B models by adeno-associated viral vector serotype 1
Auteur:
Arruda, Valder R. Schuettrumpf, Joerg Herzog, Roland W. Nichols, Timothy C. Robinson, Nancy Lotfi, Yasmin Mingozzi, Federico Xiao, Weidong Couto, Linda B. High, Katherine A.